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Bioenergetics and Muscle Function Improvement With AMAZ-02 in Elderly Skeletal Muscle (ENERGIZE Trial)

Not Applicable
Completed
Conditions
Mitochondrial Function, Bioenergetics
Muscle Function
Aging
Interventions
Dietary Supplement: Placebo
Dietary Supplement: Mitopure
Registration Number
NCT03283462
Lead Sponsor
Amazentis SA
Brief Summary

This is a randomized, double-blind, single-center, placebo-controlled Phase 2 trial enrolling 66 healthy elderly subjects (33 placebo and 33 AMAZ-02 administration) who are ≥65 and ≤ 90 years of age with evidence of low mitochondrial function. AMAZ-02 or placebo will be orally administered for 4 months.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
66
Inclusion Criteria
  1. Adults ≥65 and ≤90 years of age
  2. Able to travel to and from the University of Washington and Fred Hutch Cancer Research Center (FHCRC)
  3. Informed consent obtained
  4. 6 minute walk distance of <550 meters
  5. ATP max < 1mM /sec (in the hand FDI muscle)
Exclusion Criteria
  1. Subjects who have significant disease(s) or condition(s) which, in the opinion of the investigator, may put the subject at risk because of their participation in the trial or may influence either the results of the trial or the subject's ability to participate in the trial
  2. Hospitalization within 3 months for major atherosclerotic events (defined as combined incidence of myocardial infarction, urgent target-vessel revascularization, coronary bypass surgery and stroke) and for any hospitalization within 2 months.
  3. Have any metal implants in the right limbs, including non-MRI compatible metal stents, titanium pins/markers, etc.
  4. Have an implanted cardiac pacemaker or other implanted non-MRI compatible cardiac device
  5. Chronic, uncontrolled hypertension as judged by the Investigator (i.e., Baseline SBP >150 mm Hg, DBP >90 mm Hg) or a SBP > 150 mm Hg or DBP > 95 mm Hg at the time of screening or baseline. If the initial BP reading is above these values, the reading may be repeated one time within 20 minutes of the initial reading.
  6. Body mass index <18 or >32 kg/m2
  7. Severe chronic kidney disease requiring treatment with hemodialysis or peritoneal dialysis.
  8. Additional laboratory abnormalities determined as clinically significant by the Investigator.
  9. Clinically significant abnormalities on physical examination (as judged by the Investigator)
  10. Clinically significant and chronic uncontrolled renal, hepatic, pulmonary, endocrine, neurologic disorders, bone, or gastrointestinal system dysfunction
  11. History of seizures or epilepsy
  12. History of serious mental illness as judged by the Investigator
  13. Oral temperature >37.5°C at the time of the physical
  14. Suspicion, or recent history, of alcohol or substance abuse or tobacco use
  15. Subjects who in the opinion of the Investigator have a clinically significant abnormal 12-lead ECG during the screening period. Presence of atrial fibrillation, varying degrees of AV block, existence of a left bundle branch block, or evidence of previous myocardial infarction.
  16. Subjects who are either unwilling to agree to refrain from using or are found to be using supplementary antioxidant vitamins (e.g., Coenzyme Q10, resveratrol, L-carnitine) from 7 days prior to dosing and throughout the treatment period
  17. Subjects who are either unwilling to agree to refrain from using or are found to be using the following dietary restrictions (pomegranate juice, walnuts, pecans, strawberry, raspberry blackberry) from 7 days prior to dosing and throughout the treatment period
  18. Are currently enrolled in a clinical trial involving an investigational product or non-approved use of a drug or device or concurrently enrolled in any other type of medical research judged not to be scientifically or medically compatible with this study
  19. Have participated, within the last 30 days from a clinical trial involving an investigational product. If the previous investigational product has a long half life, 3 months or 5 half-lives (whichever is longer) should have passed

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
PlaceboPlacebo-
MitopureMitopure-
Primary Outcome Measures
NameTimeMethod
Change in 6 minute walking distance (6MWD) at the end of study intervention compared to baseline4 months
Percent change from baseline in ATP max (maximal ATP synthesis rate) in hand skeletal muscle (via Magnetic Resonance Spectroscopy)2, 4 months
Secondary Outcome Measures
NameTimeMethod
Percent change from baseline in contraction number during a hand muscle fatigue test2, 4 months
Percent change from baseline in ATP max (maximum ATP synthesis rate) in leg skeletal muscle (via MRS)4 months
Percent change from baseline in contraction number during a leg muscle fatigue test4 months
Change in Short Physical Performance Battery (SPPB) scores at the end of study intervention compared to baseline4 months
Change in exercise tolerance compared to baseline (via cycle ergometry)4 months
Change in hand grip strength at the end of study intervention compared to baseline4 months
Change in leg muscle strength (1-RM and 10-RM) at the end of study intervention compared to baseline4 months
Change in muscle size (cross-sectional area of the muscles) at the end of study intervention compared to baseline4 months
Change in mitochondrial function on muscle biopsy samples at the end of study intervention compared to baseline (via respirometry)4 months
Effect of AMAZ-02 on mitochondrial gene and protein expression in muscle tissue4 months
Effect of AMAZ-02 on plasma acylcarnitines4 months
Effect of AMAZ-02 on quality of life questionnaire (SF36)4 months
Change from baseline in plasma lipid profile4 months
Change from baseline in plasma for circulating biomarkers (myostatin, follistatin)4 months

Trial Locations

Locations (1)

University of Washington Medical Center

🇺🇸

Seattle, Washington, United States

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