MedPath

To Evaluate Safety and Tolerability of the Fixed- Dose Combination of Obeticholic Acid and Bezafibrate

Phase 3
Conditions
Primary Biliary Cholangitis
Interventions
Drug: FDC tablet (OCA 5 mg + BZF 400 mg SR)
Registration Number
NCT06488911
Lead Sponsor
Intercept Pharmaceuticals
Brief Summary

An Open Label Long-Term Study to Evaluate the Safety and Tolerability of the Fixed-Dose Combination (FDC) of Obeticholic Acid (OCA) and Bezafibrate (BZF) tablet in Subjects with Primary Biliary Cholangitis (PBC).

Detailed Description

Not available

Recruitment & Eligibility

Status
ENROLLING_BY_INVITATION
Sex
All
Target Recruitment
133
Inclusion Criteria
  • All subjects with PBC who participated and are actively taking investigational product in Study 747-213 or Study 747-214 are eligible to enroll in this study (977-311).
Exclusion Criteria
  • History or presence of other concomitant liver diseases
  • Clinical complications of PBC
  • History or presence of hepatic decompensating events
  • Current or history of gallbladder disease
  • If female, known pregnancy, or has a positive urine pregnancy test (confirmed by a positive serum pregnancy test), or lactating.

Note: Other protocol defined Inclusion/Exclusion criteria may apply.

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
OCA 5 mg + BZF 400 mg SRFDC tablet (OCA 5 mg + BZF 400 mg SR)Participants will be administered with OCA 5 mg + BZF 400 mg SR once daily.
Primary Outcome Measures
NameTimeMethod
Number of participants reporting adverse events (AE) and serious adverse event (SAE)Up to 60 months
Secondary Outcome Measures
NameTimeMethod
Number of participants with 50 percent (%) reduction of pruritus determined by visual analogue scale (VAS) scoreUp to 60 months

The Visual Analogue Scale (VAS) measures pain intensity. The VAS consists of a 10-centimeter (cm) line, with two end points representing 0 ('no pain') and 10 ('pain as bad as it could possibly be').

Number of participants with Adjudicated Liver Related Clinical Outcomes - Progression to hepatic decompensationUp to 60 months
Number of participants reporting all-cause mortalityUp to 60 months
Number of participants with Adjudicated Liver Related Clinical Outcomes - Liver transplantUp to 60 months
Number of participants with Adjudicated Liver Related Clinical Outcomes - Model for End-Stage Liver Disease (MELD) Score โ‰ฅ15Up to 60 months

MELD is a scoring system for assessing the severity of chronic liver disease and to assess prognosis and suitability for liver transplantation. It uses the participant's values for total bilirubin, serum creatinine, and the international normalized ratio (INR) for prothrombin time to predict survival. MELD score ranges from 6 (less ill) to 40 (gravely ill) with scores and mortality probability being: Score 40=71.3% mortality; Scores 30-39=52.6% mortality; Scores 20-29=19.6% mortality; Scores 10-19=6.0% mortality; Score 9 or less=1.9% mortality. Higher scores indicated greater disease severity. Adjudication was performed under the review of HSAC of all available data for each identified participant to determine liver injury status.

Trial Locations

Locations (53)

Hopital de la Pitie Salpetriere

๐Ÿ‡ซ๐Ÿ‡ท

Paris, France

Medizinische Hochschule Hannover

๐Ÿ‡ฉ๐Ÿ‡ช

Hanover, Germany

University Hospital of Larissa

๐Ÿ‡ฌ๐Ÿ‡ท

Larissa, Greece

DEOEC II. sz. Belgygyszati Klinika

๐Ÿ‡ญ๐Ÿ‡บ

Debrecen, Hungary

Hadassah Ein-Karem Medical Center - Liver unit

๐Ÿ‡ฎ๐Ÿ‡ฑ

Jerusalem, Israel

Azienda Ospedaliero-Universitaria di Bologna Policlinico S. Orsola-Malpighi

๐Ÿ‡ฎ๐Ÿ‡น

Bologna, Italy

Hospital ClinicUniversity of Barcelona

๐Ÿ‡ช๐Ÿ‡ธ

Barcelona, Spain

Hacettepe University, Faculty of Medicine, Adult Hospital Gastroenterology

๐Ÿ‡น๐Ÿ‡ท

Ankara, Turkey

Harran University Hospital, Gastroenterology

๐Ÿ‡น๐Ÿ‡ท

ลžanlฤฑurfa, Turkey

CHU Paris Est - Hopital Saint Antoine

๐Ÿ‡ซ๐Ÿ‡ท

Paris, France

University of Alabama at Birmingham

๐Ÿ‡บ๐Ÿ‡ธ

Birmingham, Alabama, United States

Southern California Research Center

๐Ÿ‡บ๐Ÿ‡ธ

Coronado, California, United States

University of Miami/Schiff Center for Liver Diseases

๐Ÿ‡บ๐Ÿ‡ธ

Miami, Florida, United States

Tampa General Medical Group

๐Ÿ‡บ๐Ÿ‡ธ

Tampa, Florida, United States

Piedmont Atlanta Hospital

๐Ÿ‡บ๐Ÿ‡ธ

Atlanta, Georgia, United States

Ochsner Clinic Foundation

๐Ÿ‡บ๐Ÿ‡ธ

New Orleans, Louisiana, United States

Beth Israel Deaconess Medical Center

๐Ÿ‡บ๐Ÿ‡ธ

Boston, Massachusetts, United States

NYU Langone Health

๐Ÿ‡บ๐Ÿ‡ธ

New York, New York, United States

Carolina's GI Research, LLC

๐Ÿ‡บ๐Ÿ‡ธ

Raleigh, North Carolina, United States

University Hospitals Cleveland Medical Center

๐Ÿ‡บ๐Ÿ‡ธ

Cleveland, Ohio, United States

Gastro One

๐Ÿ‡บ๐Ÿ‡ธ

Germantown, Tennessee, United States

East Tennessee Research Institute

๐Ÿ‡บ๐Ÿ‡ธ

Johnson City, Tennessee, United States

The Liver Institute at Methodist Dallas Medical Center

๐Ÿ‡บ๐Ÿ‡ธ

Dallas, Texas, United States

American Research Corporation

๐Ÿ‡บ๐Ÿ‡ธ

San Antonio, Texas, United States

DIM Clinica Privada

๐Ÿ‡ฆ๐Ÿ‡ท

Buenos Aires, Argentina

Hospital Italiano de Buenos Aires

๐Ÿ‡ฆ๐Ÿ‡ท

Buenos Aires, Argentina

Hospital Italiano de La Plata

๐Ÿ‡ฆ๐Ÿ‡ท

Buenos Aires, Argentina

Hospital Universitario Austral

๐Ÿ‡ฆ๐Ÿ‡ท

Buenos Aires, Argentina

Hospital Provincial del Centenario

๐Ÿ‡ฆ๐Ÿ‡ท

Santa Fe, Argentina

Houston Methodist Hospital

๐Ÿ‡บ๐Ÿ‡ธ

Houston, Texas, United States

Royal Adelaide Hospital

๐Ÿ‡ฆ๐Ÿ‡บ

Adelaide, Australia

Flinders Medical Centre

๐Ÿ‡ฆ๐Ÿ‡บ

Bedford Park, Australia

UZ Leuven

๐Ÿ‡ง๐Ÿ‡ช

Leuven, Belgium

University of Alberta Division of Gastroenterology Zeidler Ledcor Centre

๐Ÿ‡จ๐Ÿ‡ฆ

Edmonton, Alberta, Canada

Pacific Gastroenterology Associates GI Research Institute

๐Ÿ‡จ๐Ÿ‡ฆ

Vancouver, British Columbia, Canada

Universityl Hospital Dubrava

๐Ÿ‡ญ๐Ÿ‡ท

Zagreb, Croatia

Hepato-Gastroenterologie HK, s.r.o.

๐Ÿ‡จ๐Ÿ‡ฟ

Hradec Krรกlovรฉ, Czechia

Artroscan s.r.o. Gastroenterologicka

๐Ÿ‡จ๐Ÿ‡ฟ

Ostrava, Czechia

Research Site SRO

๐Ÿ‡จ๐Ÿ‡ฟ

Plzen, Czechia

Tartu University Hospital

๐Ÿ‡ช๐Ÿ‡ช

Tartu, Estonia

Hopital Henri Mondor

๐Ÿ‡ซ๐Ÿ‡ท

Crรฉteil, France

CHRU de Lille

๐Ÿ‡ซ๐Ÿ‡ท

Lille, France

Kyungpook National University Hospital

๐Ÿ‡ฐ๐Ÿ‡ท

Daegu, Korea, Republic of

Seoul National University Bundang Hospital

๐Ÿ‡ฐ๐Ÿ‡ท

Seongnam-si, Korea, Republic of

University Hopital Santaros klinikos

๐Ÿ‡ฑ๐Ÿ‡น

Vilnius, Lithuania

Academisch Medisch Centrum

๐Ÿ‡ณ๐Ÿ‡ฑ

Amsterdam, Netherlands

Akershus University Hospital

๐Ÿ‡ณ๐Ÿ‡ด

Lรธrenskog, Norway

Consorcio Hospital General Universitario

๐Ÿ‡ช๐Ÿ‡ธ

Valencia, Spain

John Radcliffe Hospital

๐Ÿ‡ฌ๐Ÿ‡ง

Oxford, United Kingdom

Ege University, Faculty of Medicine, Gastroenterology

๐Ÿ‡น๐Ÿ‡ท

Bornova, Turkey

Istanbul University, Capa Faculty of Medicine, Gastroenterology

๐Ÿ‡น๐Ÿ‡ท

Istanbul, Turkey

Institute of Cellular Medicine Newcastle University

๐Ÿ‡ฌ๐Ÿ‡ง

Newcastle Upon Tyne, United Kingdom

Hull University Teaching Hospitals NHS Trust

๐Ÿ‡ฌ๐Ÿ‡ง

Hull, United Kingdom

ยฉ Copyright 2025. All Rights Reserved by MedPath