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A Trial to Investigate Long Term Efficacy and Safety of Lonapegsomatropin in Adults With Growth Hormone Deficiency

Phase 3
Completed
Conditions
Endocrine System Diseases
Hormone Deficiency
Adult Growth Hormone Deficiency
Interventions
Registration Number
NCT05171855
Lead Sponsor
Ascendis Pharma Endocrinology Division A/S
Brief Summary

This is a phase 3 open-label multicenter extension study designed to evaluate the long-term safety and efficacy of Lonapegsomatropin administered once-weekly. The study participants are adults (males and females) with confirmed growth hormone deficiency (GHD) having completed the treatment period in study TCH-306 (foresiGHt).

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
233
Inclusion Criteria
  • Signing of the trial specific informed consent
  • Completion of the treatment period and Visit 7 assessments of trial TCH-306, including collection and upload of Visit 7 DXA scan
  • Fundoscopy at Visit 7 in trial TCH-306 without signs/symptoms of intracranial hypertension or diabetic retinopathy stage 2 / moderate or above
Exclusion Criteria
  • Diabetes mellitus if any of the following are met:

    1. Poorly controlled diabetes, defined as HbA1C higher than 7.5% according to central laboratory at Visit 6 in trial TCH-306
    2. Use of diabetes mellitus drugs other than metformin and/or dipeptidyl peptidase-4 (DPP-4) inhibitors
  • Active malignant disease or history of malignancy. Exceptions are:

    1. Resection of in situ carcinoma of the cervix uteri
    2. Complete eradication of squamous cell or basal cell carcinoma of the skin
  • Known history of hypersensitivity and/or idiosyncrasy to the investigational product (somatropin or excipients)

  • Female who is pregnant, plans to become pregnant, or is breastfeeding

  • Female participant of childbearing potential (i.e., fertile, following menarche and until becoming post-menopausal unless permanently sterile) not willing throughout the trial to use contraceptives as required by local law or practice. Details included in Appendix 4/section 10.4 of the protocol

  • Male participant not willing throughout the trial to use contraceptives as required by local law or practice. Details included in Appendix 4/ section 10.4 of the protocol

  • Any disease or condition that, in the judgement of the investigator, may make the participant unlikely to comply with the requirements of the protocol or any condition that presents undue risk from the investigational product or trial procedures

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
LonapegsomatropinLonapegsomatropinLonapegsomatropin administered once-weekly by subcutaneous injection
Primary Outcome Measures
NameTimeMethod
Incidence of Treatment-Emergent Adverse EventsThroughout the 52 week treatment period

To evaluate the safety and tolerability of once-weekly lonapegsomatropin in adults with growth hormone deficiency

Secondary Outcome Measures
NameTimeMethod
Change from Baseline in Total Body Lean MassWeek 52

Change from baseline in total body lean mass (as assessed by dual-energy x ray absorptiometry \[DXA\]) at Week 52

Change from Baseline in Trunk Fat MassWeek 52

Change from baseline in trunk fat mass (as assessed by dual-energy x ray absorptiometry \[DXA\]) at Week 52

Evaluate serum IGF-1 and IGF-1 SDSWeek 52

To evaluate the pharmacodynamics (PD) of once-weekly lonapegsomatropin in adults with growth hormone deficiency

Change from Baseline in Trunk Percent FatWeek 52

Change from baseline in trunk percent fat (as assessed by dual-energy x ray absorptiometry \[DXA\]) at Week 52

Evaluate serum hGH, lonapegsomatropin, and mPEG levelsWeek 52

To evaluate the pharmacokinetics (PK) of once-weekly lonapegsomatropin in adults with growth hormone deficiency

Trial Locations

Locations (1)

Ascendis Pharma Investigational Site

🇬🇧

Leeds, United Kingdom

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