MedPath

PHASE III STUDY OF EMICIZUMAB IN PATIENTS WITH ACQUIRED HEMOPHILIA A (AGEHA)

Phase 3
Completed
Conditions
Acquired hemophilia A
Registration Number
JPRN-jRCT2080225056
Lead Sponsor
Chugai Pharmaceutical Co., Ltd.
Brief Summary

These results in this study suggest that emicizumab prophylaxis with the modified dosing regimen and completion criteria for AHA has a favorable benefit-risk profile in patients with AHA.

Detailed Description

Not available

Recruitment & Eligibility

Status
completed
Sex
All
Target Recruitment
14
Inclusion Criteria

(1) At least 18 years of age at time of informed consent.
(2) Diagnosed with acquired hemophilia A.
(3) FVIII activity < 50 IU/dL and FVIII inhibitors >= 0.6 BU/mL in the last test within 7 days before enrollment .
(4) History of bleeds and/or bleeding symptoms related to acquired hemophilia A and have available records of bleeding episodes and treatment with coagulation factor products in the 24 weeks before enrollment.

Exclusion Criteria

(1) Have bleeding disorders other than acquired hemophilia A.
(2) Have had treatment for thromboembolic disease within the last 12 months (except for prophylactic treatment).
(3) History of clinically significant hypersensitivity associated with monoclonal antibody therapies or administration of globulin products.
(4) At high risk for TMA, e.g., a previous medical or family history of TMA (thrombotic thrombocytopenic purpura [TTP], atypical hemolytic uremic syndrome, etc.), in the judgment of the investigator/subinvestigator.
(5) Planned surgery (excluding minor procedures such as tooth extraction or incision and drainage) during the study.
(6) Pregnancy and lactation.

Study & Design

Study Type
Interventional
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
safety<br>Observation, Laboratory tests
Secondary Outcome Measures
NameTimeMethod
efficacy<br>pharmacokinetics<br>pharmacodynamics<br>Observation, Laboratory tests
© Copyright 2025. All Rights Reserved by MedPath