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Diagnostic and Prognostic Biomarkers of Idiopathic Intracranial Hypertension

Recruiting
Conditions
Benign Intracranial Hypertension
Interventions
Other: Standard treatment
Registration Number
NCT04032379
Lead Sponsor
Danish Headache Center
Brief Summary

Idiopathic intracranial hypertension (IIH) is a condition of unknown etiology, primarily affecting overweight females of childbearing age. Typically, patients experience headache and visual symptoms due to increased intracranial pressure (ICP) and papilledema. The diagnosis is difficult, and outcomes vary from no sequelae to blindness or chronic headaches. No clear prognostic indicators exist. Treatment consists of medication, weight loss, and possibly surgical intervention.There is an unmet need of defining biomarkers with prognostic or diagnostic value and defining predictors of a poor outcome.

This project is a prospective, population-based cohort study including clinical data and a biobank (blood samples and cerebrospinal fluid).

The investigator's primary aim is to identify biomarkers of diagnostic or prognostic value and to create a clinical IIH database. The clinical database will answer questions about patient characteristics at baseline and during follow-up, identify predictors of outcome, and help create a standardized programme for follow-up and

Detailed Description

This study is a multicenter, prospective, population-based cohort study with consecutive inclusion of patients in which the diagnosis of IIH is suspected. This study is carried out in collaboration between the Danish Headache Center, Rigshospitalet-Glostrup, and the Neurological Department at Odense University Hospital.

Patients are eligible for inclusion into the study if:

1. IIH is suspected

2. \> 18 years old and able to provide written informed consent.

At baseline included patients will have:

A.) Medical history B.) Neurological, ophthalmological and general medical examination C.) Relevant neuro-imaging D.) Blood samples and lumbar puncture F.) Evaluation by other specialist, including neuro-psychologists, if appropriate.

Subsequently patients are divided into three sub-groups according to revised Friedmann criteria:

1. Certain IIH or IIH-WOP

2. Suspected, but unconfirmed, IIH

3. IIH ruled out

Patients are followed at a headache center and by neuro-ophthalmologist according to standard clinical practice.

Recruitment & Eligibility

Status
RECRUITING
Sex
All
Target Recruitment
300
Inclusion Criteria
  1. Able to and willing to provide informed consent
  2. More than 18 years of age
  3. Suspicion of IIH (based on clinical evaluation by neurologist or opthalmologist)
Exclusion Criteria

1.) Unable to consent (e.g. language, mental retardation).

Study & Design

Study Type
OBSERVATIONAL
Study Design
Not specified
Arm && Interventions
GroupInterventionDescription
Certain IIH or IIH-WOPStandard treatmentAccording to revised diagnostic criteria, Friedmann, 2013.
IIH ruled outStandard treatmentPatients in whom another diagnosis is made.
Suspected IIHStandard treatmentIIH is suspected, does not fulfill diagnostic criteria.
Primary Outcome Measures
NameTimeMethod
Biomarkers of IIH (diagnostic and prognostic)2 years

Analyses of CSF and blood for markers of metabolism (method: Metabolomics)

Headache status at conclusion of study2 years

Prevalence of chronic headache (\>=15 headache days per month)

Visual status at conclusion of study2 years

Assessment of visual acuity

Secondary Outcome Measures
NameTimeMethod
Baseline characteristics related to IIH diagnosis2 years

Evaluation of disease presentation in the different sub-groups focusing on headache phenotype, visual disturbances and pulsatile tinnitus.

Development of IIH or IIHWOP in patients with borderline elevated ICP not fulfilling diagnostic criteria at baseline2 years

ICP is measured by lumbar puncture, borderline elevated ICP is considered \>20-30 mmH2O

Baseline characteristics related to poor outcome1 year

Poor outcome is defined as either a.) Persistent visual field defects, decreased visual acuity after 12 months and or b.) Headache \>= 15 days per month after 12 months

Results of neuropsychological evaluations1 year

Standard neuro-psychological tests

Clinical markers related to disease activity2 years

Clinical markers of relevance: Headache phenotype, pulsatile tinnitus, visual disturbances, weight changes.

Treatment and follow-up3 years

Length and type of treatment and follow-up

Weight change in a standard care program2 years

Unit of measurement is BMI

Diagnostic criteria and their use in the clinical setting2 years

Revised Friedmann criteria of 2013

Trial Locations

Locations (2)

The Danish Headache Center, Department of Neurology, Rigshospitalet-Glostrup

🇩🇰

Copenhagen, Glostrup, Denmark

Odense University Hospital, Department of Neurology

🇩🇰

Odense, Region Syddanmark, Denmark

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