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Mast Cells in Male Pelvic Pain and and Lower Urinary Tract Dysfunction

Early Phase 1
Completed
Conditions
Chronic Prostatitis With Chronic Pelvic Pain Syndrome
Interventions
Registration Number
NCT03167216
Lead Sponsor
Northwestern University
Brief Summary

The objective of this study is to evaluate inhibition of mast cells and the histamine 1 receptor (H1R) for treatment of chronic prostatitis (CP) and chronic pelvic pain syndrome (CPPS).

Detailed Description

Chronic pelvic pain is a hallmark of patients with CPPS, a non-bacterial category of prostatitis that is a significant source of morbidity in men. The cause of CPPS is unknown and there is a lack of biomarkers for diagnosis of this syndrome. Research in animal models of CP/CPPS have pointed to a role for mast cells and their degranulation constituents including mast cell tryptase in the development of pelvic pain and lower urinary tract symptoms. This study aims to evaluate the ability of FDA approved and marketed drugs to inhibit the release of mast cell tryptase and to ameliorate symptoms in patients with CP/CPPS.

This is an open label study to evaluate the efficacy of Cromolyn Sodium Oral Solution and Cetirizine hydrochloride (tablet) in men with CP/CPPS to reduce mast cell tryptase levels in expressed prostatic fluids and to show improvement in symptoms of CP/CPPS. There is no control group for the study. The difference between pre- and post-treatment levels across individuals will be assessed.

The study will consist of 3 periods: the Screening Period (Days -7 to -1), the Treatment Period (Days 1 to 21), and the Follow-up Period (7 days) after the last dose at Day 21.

During screening, subjects will be admitted to the clinic, undergo specimen (Expressed prostatic secretions (EPS), urine and blood) collection and recording of their baseline questionnaire responses Subjects will provide a basic health history, including current general health, adverse events, medications or treatments within the past 5 years. A physical examination including vital heart rate, breathing rate, blood pressure, temperature, height, weight and body mass will be taken. Subsequently, EPS from eligible subjects will be collected by the clinical team and assayed for the levels of mast cell tryptase within 24 hours of sample collection at the screening visit. 20 subjects with elevated mast cell tryptase will be identified and will be eligible for receiving the study medication from the Investigational pharmacy at Northwestern University.

Eligible subjects will be required to take medication for days 1-21 (Week 1-3), record their symptom scores weekly using the NIH-CPSI, and record all safety related symptoms.

Subjects will return to the clinic after the completion of three weeks of treatment. Expressed prostatic secretions (EPS), blood as well as a voided bladder 1, 2 and 3 (VB1-3) urine specimens will be collected as at baseline and after the last dose at day 21 for evaluating mast cell tryptase levels. A review subject's general health, adverse events, and any medications that have changed since the last visit will be collected. Vital signs (heart rate, breathing rate, blood pressure, temperature, weight and BMI will be collected.

Treated subjects will be contacted by phone 7 days after treatment by the study coordinator to follow up on any study related adverse effects or changes in symptoms.

Recruitment & Eligibility

Status
COMPLETED
Sex
Male
Target Recruitment
20
Inclusion Criteria
  • Male ages 21-80 years old
  • Diagnosed with Category III Chronic Pelvic Pain Syndrome
  • Patients reporting pain or discomfort in any of the 8 domains of the NIH_ Chronic Prostatitis Symptom Index (NIH-CPSI).
  • CP/CPPS symptoms must have been present for the majority of the time during any 3 months in the previous 6 months.
  • Mast cell tryptase levels in EPS above a control threshold of 25ng/ml based on healthy men.
Exclusion Criteria
  • Females
  • Males <21 and >80 years old
  • Patients with a known hypersensitivity to cromolyn sodium or cetirizine hydrochloride
  • Patients with impaired renal or hepatic function.
  • Mast cell tryptase levels in EPS equal to or below a control threshold of 25ng/ml based on healthy men.

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
Treatment armCetirizine HydrochlorideTreated arm with cromolyn sodium and cetirizine hydrochloride
Treatment armCromolyn SodiumTreated arm with cromolyn sodium and cetirizine hydrochloride
Primary Outcome Measures
NameTimeMethod
Mast cell tryptase levels in expressed prostatic secretions3 weeks

Changes in Mast cell tryptase at the end of treatment compared to levels observed before administration of the study drug.

Secondary Outcome Measures
NameTimeMethod
NIH-CPSI score3 weeks

Change in pelvic pain, urinary symptoms and quality of life after treatment

AUA-SI score3 weeks

Change in symptoms of lower urinary tract dysfunction after treatment

Trial Locations

Locations (1)

Northwestern Medical Faculty Foundation

🇺🇸

Chicago, Illinois, United States

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