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Preclinical Studies of Omalizumab in Chronic Rhinosinusitis With Nasal Polyposis

Early Phase 1
Completed
Conditions
Nasal Polyps
Chronic Rhinosinusitis With Nasal Polyps
Interventions
Biological: Omalizumab
Registration Number
NCT04583501
Lead Sponsor
Johns Hopkins University
Brief Summary

The goal of this study is to examine the mechanism of action of omalizumab in ex vivo tissue culture of whole human nasal polyps from patients with chronic rhino sinusitis with nasal polyposis (CRSwNP), such that specific molecular markers of inflammation can be identified.

Detailed Description

Objectives:

Aim 1. The investigation will identify the specific tissue compartment distribution of immunoglobulin E (IgE) expression within human nasal polyps. Colocalization studies will examine functional interaction of IgE with effector cells.

Aim 2. The investigation will examine the direct effect of omalizumab on expression of Type 2, 1, and 3 inflammatory pathways in human nasal polyp tissue from phenotypically characterized chronic rhinosinusitis with nasal polyposis (CRSwNP) patients.

Study Rationale: Human nasal polyps express high local tissue IgE. However, the tissue distribution, cellular location and functional consequence of IgE accumulation within the polyp tissue is not known. Phase 3 studies of omalizumab demonstrated efficacy, with responders. However, the reason for non-responder outcomes in a subset of CRSwNP patients was not understood. Therefore, the goal of this study is to examine the mechanism of action of omalizumab in CRSwNP, such that specific responders for this treatment can be identified and therapy can be optimally directed.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
21
Inclusion Criteria
  • Sinonasal inflammation for greater than 12 weeks which include at least 2 of the following symptoms: nasal obstruction/congestion, nasal discharge (anterior or posterior), facial pressure/pain, reduction of sense of smell
  • Confirmation of the clinical symptoms by (2a) CT scan evidence of paranasal sinus mucosal inflammation, and/or (2b) endoscopic exam evidence of purulence from the sinuses or ostiomeatal complex
  • Presence of nasal polyps seen on endoscopic exam or sinus CT scan
  • Adults from age of 18-100 will be eligible
  • All potential participants will be required to sign an Institutional Review Board (IRB) approved research consent form.
Exclusion Criteria
  • Children under the age of 18 will be excluded
  • No pregnant or lactating females, prisoners, mentally disabled, or persons unable to give informed consent will be contemplated for inclusion.
  • The subject groups will also exclude those with disease secondary to a clearly defined anatomic process, such as facial trauma, and obstruction due to sinonasal neoplasm.
  • To eliminate confounding variables in our ex vivo experimental studies, any subject with a history of exposure to oral or systemic IV glucocorticoids within 2 weeks of surgery or any immunomodulatory biologics will be excluded. These include, but are not limited to systemic treatment with biologics omalizumab, dupilumab, mepolizumab, benralizumab, reslizumab, or rituximab.

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
OmalizumabOmalizumabEx vivo exposure of excised human surgical polyp tissue to omalizumab.
Primary Outcome Measures
NameTimeMethod
IgE tissue compartment distribution in nasal polyps as assessed by quantitative IgE expression1 year

Quantitative IgE Expression within these cellular compartments will be measured by immunohistochemistry.

Messenger ribonucleic acid (mRNA) expression1 year

mRNA expression will be analyzed using high throughput RNA sequencing to determine the pattern of inflammatory gene expression.

Secondary Outcome Measures
NameTimeMethod

Trial Locations

Locations (2)

Johns Hopkins Bayview Medical Center

🇺🇸

Baltimore, Maryland, United States

Johns Hopkins Hospital

🇺🇸

Baltimore, Maryland, United States

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