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BPA vs. PEA in CTEPH

Not Applicable
Recruiting
Conditions
Chronic Thromboembolic Pulmonary Hypertension
Interventions
Procedure: Pulmonary endarterectomy
Procedure: Balloon pulmonary angioplasty
Registration Number
NCT05110066
Lead Sponsor
University of Aarhus
Brief Summary

Chronic thromboembolic pulmonary hypertension (CTEPH) is a rare and potentially life-threatening progressive disease that evolves from unresolved pulmonary embolism. Gold standard treatment for CTEPH is pulmonary endarterectomy (PEA) performed by skilled cardio-thoracic surgeons.

Some patients may not be surgical candidates due to co-morbidities or because the vascular lesions are too distal making them technically inoperable. In these patients, balloon pulmonary angioplasty (BPA) has emerged as an effective treatment. In a subgroup of patients, the distribution of vascular lesions makes it possible to perform either BPA or PEA. There has never been a head-to head comparison of BPA with PEA. The aim of this study is therefore, to evaluate if BPA is non-inferior to PEA in patients with (CTEPH) who are eligible for both treatments.

Detailed Description

An investigator-initiated multicenter, prospective, randomized, controlled, open label, non-inferiority trial. The study will randomize (1:1) 152 patients with CTEPH who are eligible for both PEA and BPA. Patients will be screened for study inclusion at the local CTEPH multidisciplinary team conference and eligibility for both PEA and BPA will be confirmed by a central adjudication committee.

PEA or BPA will be completed within 6 months from randomization. Follow-up visit with right heart catheterization will be completed at 4 months and 12 months after PEA or last BPA session.

Primary end-point is change in pulmonary vascular resistance from baseline to 4 months and 12 months after PEA or the last BPA session.

Recruitment & Eligibility

Status
RECRUITING
Sex
All
Target Recruitment
139
Inclusion Criteria
  • Diagnosed with chronic thromboembolic pulmonary hypertension according to current European society of cardiology/European Respiratory Society guidelines and eligible for both pulmonary endarterectomy and ballon pulmonary angioplasty by decision at the local multidisciplinary team conference and central adjudication committee
  • Written informed consent from the patient
  • Patient age >17 and <80 years
  • Able to understand and follow instructions and to participate in the entire study period
Exclusion Criteria
  • Life expectancy <12 months
  • Co morbidities evaluated at the multidisciplinary team conference, that contributes significantly to the patients pulmonary hypertension
  • Not possible to perform balloon pulmonary angioplasty or pulmonary endarterectomy within 4 months after randomization.
  • Evaluated at multidisciplinary team conference that changes in pulmonary artery hypertension targeted therapy between baseline and 4 months follow-up is inevitable*
  • Known pregnancy or positive urine Human chorionic gonadotropin screening test in fertile women
  • Previous balloon pulmonary angioplasty or pulmonary endarterectomy

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
PEA groupPulmonary endarterectomyPatients randomized to PEA will undergo surgery within 4 months after randomization and optional run-in phase. Distality of the dissection plane is at the discretion of the operating physicians.
BPA groupBalloon pulmonary angioplastyBalloon pulmonary angioplasty. Typically 4-8 sessions are needed to treat the patient. The specific pre-planning protocol, choice of wires and balloons, the number of vessels treated per session, and the decision that no further BPA sessions are needed is at the discretion of the treating physician.
Primary Outcome Measures
NameTimeMethod
Change in pulmonary vascular resistance4 months and 12 months

Change in pulmonary vascular resistance from baseline to 4-months and 12-months after the procedure(s). Patients on medical treatments at baseline will remain on medical treatments until the assessment of the primary endpoint, and be taken off if hemodynamics permit

Secondary Outcome Measures
NameTimeMethod
Six minutes walking distance4 months and 12 months

Six minutes walking distance

Cardiac index4 months and 12 months

Cardiac index measured by right heart catheterization

Mean right atrial pressure4 months and 12 months

Right atrial pressure measured by right heart catheterization

Time to clinical worsening4 months and 12 months

Clinical worsening includes all-cause mortality, nonelective hospitalization for pulmonary artery hypertension, and disease progression (disease progression is defined as a reduction from baseline in the six minutes walking distance by 15% plus worsening functional class (except for patients already in Orld health organization functional class IV).)

Quality of life evaluated by the "Living with pulmonary hypertension questionnaire"4 months and 12 months

Measured by the use of Living with pulmonary hypertension questionnaire (21 questions scored 0-5. Minimum score is 0 and maximum score is 105. Low score means high quality of life and a high score means a low quality of life).

Mean pulmonary artery pressure4 months and 12 months

Mean pulmonary artery pressure measured by right heart catheterization

N-terminal pro B-type natriuretic peptide4 months and 12 months

N-terminal pro B-type natriuretic peptide

Trial Locations

Locations (2)

Aarhus University Hospital

🇩🇰

Aarhus, Denmark

Royal Ppworth

🇬🇧

Cambridge, United Kingdom

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