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Short Stature Related Distress

Phase 4
Completed
Conditions
Self Image
Idiopathic Short Stature
Interventions
Drug: GH treatment (Genotropin)
Drug: 1 year treatment with placebo followed by optional 3 years of GH treatment
Registration Number
NCT01246219
Lead Sponsor
Rabin Medical Center
Brief Summary

The research aims to provide data on gender-related psychological impact of GH (Growth Hormone)treatment. Implicit measurable psychological metrics of the therapy outcome on males are to be evaluated in a Prospective Randomized Controlled Trial. As a secondary axis of the study, the investigators aim to provide descriptive documentation of the unique distress signal manifestation implicitly shown by Idiopathic Short Stature (ISS) boys and suggest methods of early detection and measurement of such manifestations that can be used to cement guidelines for the treatment in GH.

Detailed Description

Study Design:

A prospective randomized, double blind, placebo controlled trial design, comparing four research groups, with 4 repeated psychological measures (before treatment, after 3 months,after 1 year, and at the end of treatment, after 4 years).

The study will be divided into two segments:

Segment 1:double blind, placebo controlled, will include the first 60 ISS (Idiopathic Short Stature)recruited patients. Patients in this segment will be randomized to one of the growth hormone treatment groups in a ratio of 2:1. 40 patients will be treated 4 years with GH and 20 patients will be treated with placebo at the first year of the study and will have the option to start GH treatment after one year, for a duration of 3 years.

Segment 2:after the enrollment to segment 1 will end, enrollment to segment 2 will begin.Participants in segment 2 (patients with ISS and short stature) will serve as control groups and therefore will not be treated with growth hormone. Patients in Segment 2 will be evaluated only once.

The 4 repeated psychological evaluations (before treatment,after 3 months, after 1 year, and at the end of treatment, after 4 years)will include the following:

1. Implicit Association Test

2. Masculine Self Image

3. Pictures Projective Test

4. The Rosenberg Self Esteem Scale-a self report measure of explicit self- esteem

5. Quality of Life Questionnaire

6. Silhouette Apperception Technique (SAT)- a self report measure assessing children's and adolescent's perception of their own body size compared with that of their age-related peers

7. Child Behavior Checklist

Recruitment & Eligibility

Status
COMPLETED
Sex
Male
Target Recruitment
60
Inclusion Criteria

1 Segment 1 :Boys at the age range of 8-13 years 2. Segment 2: Boys at the age range of 12-17 years 3. Tanner stage 1 (segment 1 only) 4. more than 2 SD's (standard deviation) below the average height

Exclusion Criteria
  1. Mental retardation,
  2. Psychiatric illness,
  3. Lack of informed consent\assent.
  4. Health status that required chronic treatment with steroids

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
GH treatmentGH treatment (Genotropin)4 years of GH treatment
Placebo1 year treatment with placebo followed by optional 3 years of GH treatment1 year treatment with placebo followed by optional 3 years of GH treatment
Primary Outcome Measures
NameTimeMethod
Psychological Distress scoreAfter 4 years of treatment

short stature related distress score as measured by Silhouette Apperception Technique questionnaire

Secondary Outcome Measures
NameTimeMethod
Perceived self image scoreAfter 4 years of treatment

Perceived self image score as measured through the Masculine Self Image questionnaire

Trial Locations

Locations (1)

Schneider Children's Medical center

🇮🇱

Petach-Tikva, Israel

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