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International Registry for Severe Chronic Neutropenia

Conditions
Neutropenia
Registration Number
NCT00004342
Lead Sponsor
National Center for Research Resources (NCRR)
Brief Summary

OBJECTIVES: I. Document the clinical course of severe chronic neutropenia (SCN).

II. Monitor and assess long term safety of primary treatment in SCN patients in the United States, Canada, Europe, and Australia.

III. Study the incidence and outcome of adverse events such as osteoporosis, splenomegaly, cytogenetic abnormalities, myelodysplastic syndrome, and leukemia.

IV. Evaluate growth and development and hematologic parameters. V. Monitor for clinically significant changes in primary treatment response over time.

VI. Establish a physician network to increase the understanding of SCN. VII. Establish a demographic database to allow for future research.

Detailed Description

PROTOCOL OUTLINE:

Patients are treated by the referring physician as medically indicated. Clinical data are collected at baseline and then every 6 months.

Recruitment & Eligibility

Status
UNKNOWN
Sex
All
Target Recruitment
1000
Inclusion Criteria

Not provided

Exclusion Criteria

Not provided

Study & Design

Study Type
OBSERVATIONAL
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Secondary Outcome Measures
NameTimeMethod

Trial Locations

Locations (10)

Dana-Farber/Boston Children¹s Cancer and Blood Disorders Center

🇺🇸

Boston, Massachusetts, United States

Hospital for Sick Children

🇨🇦

Toronto, Ontario, Canada

Leeds Teaching Hospitals, Yorkshire Regional Centre for Paediatric Oncology & Haematology

🇬🇧

Leeds, England, United Kingdom

University of Massachusetts

🇺🇸

Worcester, Massachusetts, United States

Monash University

🇦🇺

Melbourne, Victoria, Australia

St. Joseph's Children's Hospital

🇺🇸

Paterson, New Jersey, United States

Medizinische Hochschule Hannover

🇩🇪

Hannover, Germany

University of Michigan

🇺🇸

Ann Arbor, Michigan, United States

University of Washington School of Medicine

🇺🇸

Seattle, Washington, United States

CancerCare Manitoba

🇨🇦

Winnipeg, Manitoba, Canada

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