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Endothelial Activation Hemostasis Disturbances and Severe Bleeding Events in Hyperleukocytic Acute Myeloid Leukemia

Conditions
Leukemia, Myeloid, Acute
Registration Number
NCT04133220
Lead Sponsor
Assistance Publique - Hôpitaux de Paris
Brief Summary

Hyper-leukocytosis \> 50.109/L is observed in 15% of acute myeloid leukemia (AML).

Level of hyper-leukocytosis is linearly associated with the incidence of life threatening complications that lead to the early death in 25% of these patients.

The HEAL project is a prospective, uni-centric, observational study that plans to include a cohort of 50 patients presenting de novo AML with hyper-leukocytosis (HL) (\> 50.109/L) and 10 controls. The aim of the study is to describe the relative proportion of various hemostasis components disturbances, endothelium alterations, platelet dysfunction and to calculate cumulative incidence of hemorrhagic and thrombotic complications as well as overall survival of patients presenting with HL AML.

Detailed Description

Not available

Recruitment & Eligibility

Status
UNKNOWN
Sex
All
Target Recruitment
60
Inclusion Criteria
  • De novo AML
  • GB counts > 50 G/L
  • Eligible for intensive chemotherapy
  • no previous AML treatment
Exclusion Criteria
  • secondary AML
  • relapse of AML
  • Acute promyelocytic leukemia
  • Previous antiplatelet or anticoagulant treatment

Study & Design

Study Type
OBSERVATIONAL
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Hemostasis / platelet and endothelial dysfunction assessed by plasma concentration of PAI-1 Ag12hours after chemotherapy initiation

plasma concentration of PAI-1 Ag

Hemostasis / platelet and endothelial dysfunction assessed by plasma concentration of Factor X12hours after chemotherapy initiation

plasma concentration of Factor X

Hemostasis / platelet and endothelial dysfunction parameter assessed by plasma concentration of Syndecan-112hours after chemotherapy initiation

plasma concentration of Syndecan-1

Hemostasis / platelet and endothelial dysfunction assessed by plasma concentration of Fragments thrombin 1+212hours after chemotherapy initiation

plasma concentration of Fragments thrombin 1+2

Hemostasis / platelet and endothelial dysfunction assessed by plasma concentration of vWF:CB12hours after chemotherapy initiation

plasma concentration of vWF:CB

Hemostasis / platelet and endothelial dysfunction parameter assessed by plasma concentration of vWF Ag12hours after chemotherapy initiation

plasma concentration of vWF Ag

Hemostasis / platelet and endothelial dysfunction assessed by vWF activity12hours after chemotherapy initiation

vWF activity

Hemostasis / platelet and endothelial dysfunction assessed by plasma concentration of u-PA12hours after chemotherapy initiation

plasma concentration of u-PA

Hemostasis / platelet and endothelial dysfunction assessed by plasma concentration of sCD40L12hours after chemotherapy initiation

plasma concentration of sCD40L

Hemostasis / platelet and endothelial dysfunction parameter assessed by plasma concentration of IL612hours after chemotherapy initiation

plasma concentration of IL6

Hemostasis / platelet and endothelial dysfunction assessed by plasma concentration of PAI-1 activity12hours after chemotherapy initiation

plasma concentration of PAI-1 activity

Hemostasis / platelet and endothelial dysfunction assessed by plasma concentration of t-PA-PAI-1 complex12hours after chemotherapy initiation

plasma concentration of t-PA-PAI-1 complex

Hemostasis / platelet and endothelial dysfunction assessed by plasma concentration of Fibrin monomers12hours after chemotherapy initiation

plasma concentration of Fibrin monomers

Hemostasis / platelet and endothelial dysfunction assessed by plasma concentration of ADAMTS13 Ag12hours after chemotherapy initiation

plasma concentration of ADAMTS13 Ag

Hemostasis / platelet and endothelial dysfunction assessed by ADAMTS13 activity12hours after chemotherapy initiation

ADAMTS13 activity

Hemostasis / platelet and endothelial dysfunction assessed by plasma concentration of Factor II12hours after chemotherapy initiation

plasma concentration of Factor II

Hemostasis / platelet and endothelial dysfunction assessed by plasma concentration of ICAM-12hours after chemotherapy initiation

plasma concentration of ICAM-

Hemostasis / platelet and endothelial dysfunction assessed by plasma concentration of Fg12hours after chemotherapy initiation

plasma concentration of Fg

Hemostasis / platelet and endothelial dysfunction assessed by plasma concentration of t-PA12hours after chemotherapy initiation

plasma concentration of t-PA

Hemostasis / platelet and endothelial dysfunction assessed by plasma concentration of e-Selectin12hours after chemotherapy initiation

plasma concentration of e-Selectin

Hemostasis / platelet and endothelial dysfunction assessed by plasma concentration of AT12hours after chemotherapy initiation

plasma concentration of AT

Hemostasis / platelet and endothelial dysfunction assessed by plasma concentration of TAT complex12hours after chemotherapy initiation

plasma concentration of TAT complex

Hemostasis / platelet and endothelial dysfunction assessed by plasma concentration of plasmin-antiplasmin complex12hours after chemotherapy initiation

plasma concentration of plasmin-antiplasmin complex

Hemostasis / platelet and endothelial dysfunction assessed by Prothrombine Time12hours after chemotherapy initiation

Prothrombine Time

Hemostasis / platelet and endothelial dysfunction assessed by plasma concentration of Factor VIII12hours after chemotherapy initiation

plasma concentration of Factor VIII

Hemostasis / platelet and endothelial dysfunction assessed by plasma concentration of Factor XII12hours after chemotherapy initiation

plasma concentration of Factor XII

Hemostasis / platelet and endothelial dysfunction assessed by Activated Partial Thromboplastin Time [APTT]12hours after chemotherapy initiation

Activated Partial Thromboplastin Time \[APTT\]

Hemostasis / platelet and endothelial dysfunction assessed by plasma concentration of Factor IX12hours after chemotherapy initiation

plasma concentration of Factor IX

Secondary Outcome Measures
NameTimeMethod
Overall survival1 month

Time from inclusion to death of any cause

Cumulative incidence of serious bleeding events1 month

Time from inclusion to first serious bleeding event

ICU length of stay1 month

duration of stay in ICU within the first month

Cumulative incidence of thrombotic events1 month

Time from inclusion to first thrombotic event

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