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A Double-Blind Pharmacokinetic Interaction Study Evaluating the Effect of a Single IV Infusion of GGF2 or Placebo on Midazolam Pharmacokinetics in Patients With Heart Failure

Phase 1
Completed
Conditions
Heart Failure
Interventions
Registration Number
NCT01944683
Lead Sponsor
Acorda Therapeutics
Brief Summary

The study will examine midazolam pharmacokinetics following single dose administration of 3 planned dose levels of GGF2 .

Detailed Description

This drug-drug interaction (DDI) study evaluates the potential effect of intravenously administered GGF2 on the elimination kinetics of midazolam.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
22
Inclusion Criteria
  • If female, must be at least 2 years post-menopausal or have bilateral oophorectomy, hysterectomy or documented sterility
  • If male, must have documented sterility (by verbal report or previous vasectomy), or if non-sterile, must agree to use barrier contraception for the entire duration of the trial and until 3 months after the last dose of investigational product. Must also agree not to donate sperm during the study and up to 3 months after the last dose of investigational product
  • Stable coronary disease without unstable angina or acute coronary syndrome in the last 6 months
  • All cardiac medications, specifically beta-blockers, renin-angiotensin system inhibitors, aldosterone antagonists, hydralazine and nitrates are at a stable dose (at least 4 weeks) prior to Day 1
Exclusion Criteria
  • Any previous exposure to GGF2 or other neuregulins
  • Initiation or change of a prescription medication within the 2 weeks prior to Day 1, and/or concomitant medication regimen is expected to change during the course of the study
  • Known allergic reaction to midazolam, or any of the components of midazolam syrup (including cherry flavoring), or components of GGF2 diluent
  • Known specific hepatic disease; total bilirubin >2 mg/dL, AST > 100 IU
  • History of hepatic impairment (hepatitis B and C)
  • Type I Diabetes
  • Documented stroke or transient ischemic attack (TIA) within 2 months of study enrollment

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
PlaceboPlaceboPatients will be randomized to receive GGF2 or Placebo and on study day 3 administered a single IV infusion. Each patient will receive 5 oral doses of Midazolam syrup on study day 1 and days 4 through 7 respectively.
GGF2MidazolamPatients will be randomized to receive GGF2 or Placebo and on study day 3 administered a single IV infusion. Each patient will receive 5 oral doses of Midazolam syrup on study day 1 and days 4 through 7 respectively.
PlaceboMidazolamPatients will be randomized to receive GGF2 or Placebo and on study day 3 administered a single IV infusion. Each patient will receive 5 oral doses of Midazolam syrup on study day 1 and days 4 through 7 respectively.
GGF2GGF2Patients will be randomized to receive GGF2 or Placebo and on study day 3 administered a single IV infusion. Each patient will receive 5 oral doses of Midazolam syrup on study day 1 and days 4 through 7 respectively.
Primary Outcome Measures
NameTimeMethod
Safety and tolerability of GGF2 IV infusion in patients with heart failure assessed by review of Treatment Emergent Adverse Events (TEAE)90 days (± 3 days)
Pharmacokinetic (PK) parameter Area Under the Curve (AUC) of a single dose of midazolam when administered prior to and following a single IV infusion of GGF2 or PlaceboDay 1 to Day 7
Secondary Outcome Measures
NameTimeMethod
Change from baseline of 2D-Echocardiogram (2D-ECHO) or ECHO with contrastVisit 1 (day-14 to day-1) and visits 2-5 (day 8 through day 90 ± 3 days)
Change from baseline of the Six-Minute Walk Test (6MWT)Visit 1 (day-14 to day-1) and visits 3-5 (day 14 through day 90 ± 3 days)
Change from baseline of metabolic testing measuring maximum capacity of body to transport and use oxygen during incremental exercise (VCO2 and VO2 max)Visit 1 (day-14 to day-1) and visits 3-5 (day 14 through day 90 ± 3 days)
Change from baseline of the M.D. Anderson Symptom Inventory (MDASI) scoreVisit 1 (day-14 to day-1) and visits 3-5 (day 14 through day 90 ± 3 days)

MDASI is a questionnaire asking patients about the severity of their heart disease symptoms and impact of the symptoms on daily functioning during the past 24 hours.

Scale ranges from 0 (sympton has not been present) to 10 (the symptom was as bad as you can imagine it could be).

Trial Locations

Locations (8)

Orange County Research Center

🇺🇸

Tustin, California, United States

Tulane University School of Medicine

🇺🇸

New Orleans, Louisiana, United States

Sentara Cardiovascular Research Institute

🇺🇸

Norfolk, Virginia, United States

UCSD Medical Center

🇺🇸

La Jolla, California, United States

Duke Clinical Research Unit

🇺🇸

Durham, North Carolina, United States

Vanderbilt University Medical Center

🇺🇸

Nashville, Tennessee, United States

New Orleans Center for Clinical Research (NOCCR)

🇺🇸

Knoxville, Tennessee, United States

Jacksonville Center for Clinical Research

🇺🇸

Jacksonville, Florida, United States

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