MedPath

Trial of Nilotinib and Adriamycin as Treatment in Liposarcomas and Leiomyosarcomas of Retroperitoneum

Phase 1
Conditions
Chondrosarcoma
Retroperitoneal Liposarcoma
Retroperitoneal Leiomyosarcoma
Interventions
Drug: Nilotinib-adriamycin
Registration Number
NCT02587169
Lead Sponsor
Broto, Javier Martín, M.D.
Brief Summary

Phase I/II multicenter and prospective trial of nilotinib and adriamycin as neoadjuvant treatment in liposarcomas and leiomyosarcomas of retroperitoneum.

The main objective of this study is to improve relapse-free survival (RFS)and overall survival (OS) decreasing from 50% to 30% the relapse percentage at 5 years in patients with resected sarcoma of retroperitoneum.

Secondary objectives include the analysis of antitumoral activity through response rate (RECIST and tissular changes), the assessment of positive correlation between biomarkers and clinical results, the study of long term overall survival, and the analysis of the safety profile of the nilotinib-adriamycin combination.

The trial hypothesis is that the nilotinib-adriamycin combination is synergistic and therefore better response results are expected (from 20% as P0 to 40% as P1). The study seeks to find a positive correlation between biomarkers and clinical results in retroperitoneal liposarcoma and leiomyosarcoma treated with the mentioned combination.

The study involves the participation of 20 hospitals of the Spanish Sarcoma Group (GEIS). The treatment consists of 4 neoadjuvant cycles of nilotinib-adriamycin on patients with resectable retroperitoneal sarcoma. The research comprises a robust translational study as well as histological and radiological reviews.

Detailed Description

The nilotinib-adriamycin combination will be given in 4 cycles of 21 days. In each cycle, nilotinib will be administered at fixed dose of 400 mg/12h orally during 6 consecutive days (1-6) and endovenous adriamycin (20 minutes) on day 5 at three levels (in phase I, dosage of 60 mg/m2, 65 mg/m2, and 75 mg/m2 will be tested to determine the recommended dose for phase II).

Phase I includes patients with retroperitoneal liposarcoma, retroperitoneal leiomyosarcoma and chondrosarcoma. Phase II is focused on retroperitoneal liposarcoma and leiomyosarcoma only.

Recruitment & Eligibility

Status
UNKNOWN
Sex
All
Target Recruitment
40
Inclusion Criteria
  • Patients with histological diagnosis of well differentiated liposarcoma, dedifferentiated liposarcoma or primary leiomyosarcoma of retroperitoneum and resectable. In phase I the study will recruit patients with high-grade chondrosarcoma of non-mesenchymal type.
  • Age: 18-70 years.
  • Measurable disease, according to RECIST criteria.
  • Functional status: 0-1 (ECOG).
  • Baseline medullar function (hemoglobin > 10 g/dL, leukocytes ≥ 3.000/mm3, RAN≥ 1,5 x 109 /l, granulocytes ≥ 1.500/mm3, platelets ≥ 100.000/mm3). Patients with alteration of transaminases ≤ 2.5 times the normal limits, bilirubin total ≤ LSN, CPK≤ 2.5 times the normal limits, alkaline phosphatase ≤ 2.5 times more the normal limits or creatinine values ≤ 1.6 mg/dL, are accepted.
  • Cardiac function (LVEF) normal, considering the normal ranges of the institution.
  • The patient must voluntarily sign the informed consent before any trial test, knowing that he/she can leave the trial at any time, without any consequence for his/her posterior medical attention.
  • Patients in fertile age (both male and female) must use an effective contraceptive method before the entry in the study and during the trial. Moreover, women must maintain contraceptive measures up to 5 months after the treatment. Pregnancy must be ruled out though urine test (negative pregnancy test) for study enrolment.
Exclusion Criteria
  • Patients having received previous chemotherapy.
  • Patient having been irradiated on the tumoral disease.
  • Functional status > 1 (ECOG).
  • Metastasis in any location.
  • Bilirubin values over the normal level. Creatinine over 1.6 mg/dL.
  • History of another oncological disease except basalioma or in situ cervical carcinoma adequately treated.
  • Serious cardiovascular diseases (dyspnea >= 2 NYHA, ie.)
  • Systemic pathologies limiting survival to less than 2 years, limiting patient availability, or those that, by clinical judgement, may interfere significantly with treatment toxicity.
  • Bacterial, viral, or uncontrolled mycotic infectious diseases.
  • Pregnant or lactating patients.
  • Psychological, family, sociological or geographical situations not allowing protocol fulfilment or informed consent signature.
  • Patients currently involved in other clinical trials receiving any other agent under investigation.
  • Patient having participated in a clinical trial and/or having received an agent under investigation in the 30 days prior to enrolment.
  • Patients requiring treatments with prolongation of QT interval as amiodarone, disopyramide, procainamide, quinidine, and sotalol.

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
Nilotinib-adriamycinNilotinib-adriamycinThe nilotinib-adriamycin combination will be given in 4 cycles of 21 days. In each cycle, nilotinib will be administered at fixed dose of 400 mg/12h orally during 6 consecutive days (1-6) and endovenous adriamycin (20 minutes) on day 5 at three levels (in phase I, dosage of 60 mg/m2, 65 mg/m2, and 75 mg/m2 will be tested to determine the recommended dose for phase II).
Primary Outcome Measures
NameTimeMethod
Relapse-free survival (RFS) at 5 years5 years

The main goal of the study is to improve relapse-free survival (RFS) and overall survival (OS) decreasing from 50% to 30% the percentage of relapse at 5 years in patients with resected retroperitoneal sarcoma.

Secondary Outcome Measures
NameTimeMethod
Overall survival (OS)100 months

Overall survival measured from treatment start date until date of death, whichever the cause, assessed up to 100 months

Number of adverse events4 months

Number and type of adverse events according to CTCAE 4.0

Objective response rate (ORR) (confirmed complete response [CR] and partial response [PR])Baseline and at 4 months

To determine the objective response rate (ORR) (confirmed complete response \[CR\] and partial response \[PR\]) using RECIST 1.1 criteria

Trial Locations

Locations (20)

Hospital Puerta de Hierro

🇪🇸

Madrid, Spain

Hospital Universitari Germans Trials i Pujol

🇪🇸

Badalona, Spain

Hospital Universitario La Paz

🇪🇸

Madrid, Spain

Hospital Clínico Universitario de Santiago

🇪🇸

Santiago de Compostela, Spain

Hospital Universitario Ramón y Cajal

🇪🇸

Madrid, Spain

Hospital Marqués de Valdecilla

🇪🇸

Santander, Spain

Hospital Virgen del Rocío

🇪🇸

Sevilla, Spain

Hospital Xeral Cies

🇪🇸

Vigo, Spain

Hospital Infanta Cristina

🇪🇸

Badajoz, Spain

Hospital Universitari Son Espases

🇪🇸

Palma de Mallorca, Balearic Islands, Spain

Hospital de la Santa Creu i Sant Pau

🇪🇸

Barcelona, Spain

Complejo Asistencial Universitario de León

🇪🇸

León, Spain

Hospital Universitari Vall d'Hebron

🇪🇸

Barcelona, Spain

Hospital Provincial de Castellón

🇪🇸

Castellón, Spain

Complejo Hospitalario de Navarra

🇪🇸

Pamplona, Spain

Hospital Virgen de la Salud

🇪🇸

Toledo, Spain

Instituto Valenciano de Oncología

🇪🇸

Valencia, Spain

Hospital Universitario de Canarias

🇪🇸

La Laguna, Spain

Hospital Universitario Miguel Servet

🇪🇸

Zaragoza, Spain

Hospital Universitario Virgen de la Arrixaca

🇪🇸

Murcia, Spain

© Copyright 2025. All Rights Reserved by MedPath