Eculizumab in patients with classic PNH: A cost effectivity study.
- Conditions
- Patient satisfaction, cost effectiveness, Qualtity of life, home-based treatment
- Registration Number
- NL-OMON29026
- Lead Sponsor
- Radboud University Nijmegen Medical Centre (RUNMC)
- Brief Summary
/A
- Detailed Description
Not available
Recruitment & Eligibility
- Status
- Pending
- Sex
- Not specified
- Target Recruitment
- 25
Inclusion Criteria
1. PNH patients treated with eculizumab;
2. Aged >= 18 years;
Exclusion Criteria
No informed consent.
Study & Design
- Study Type
- Observational non invasive
- Study Design
- Not specified
- Primary Outcome Measures
Name Time Method Satisfaction of patients (home care versus intramural administration) determined by a treatment satisfaction questionnaire.
- Secondary Outcome Measures
Name Time Method 1. Quality of life (EORTC and Facit Fatigue scale);<br /><br>2. Resource utilisation;<br /><br>3. Indirect costs (productivity losses);<br /><br>4. Utility assessments (EQ-5D);<br /><br>5. Clinical outcomes: safety and sustained reduction of hemolysis;<br /><br>6. Quality control.