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HIT-CF Organoid Study: Stratifying Cystic Fibrosis Patients Based on Intestinal Organoid Response To Different CFTR-modulators

Recruiting
Conditions
Cystic Fibrosis CF
Registration Number
NL-OMON24027
Lead Sponsor
niversity Medical Center Utrecht
Brief Summary

Not available

Detailed Description

Not available

Recruitment & Eligibility

Status
Recruiting
Sex
Not specified
Target Recruitment
500
Inclusion Criteria

–Male or female with confirmed diagnosis of CF

–Adult age on the date of informed consent

Exclusion Criteria

–Subject has at least one of the following CFTR-mutations:

•F508del, G551D, G1244E, G1349D, G178R, G551S, S1251N, S1255P, S549N, S549R, R117H, A455E, 3849+10kbC>T

Study & Design

Study Type
Interventional
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Intestinal organoid response of 500 subjects to three drug products of <br>different pharmaceutical companies, ranked by best response per drug product.
Secondary Outcome Measures
NameTimeMethod
ot applicable
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