MedPath

Second-line Treatment of Primary Autoimmune Hemolytic Anemia

Phase 3
Recruiting
Conditions
Primary Autoimmune Hemolytic Anemia
Interventions
Registration Number
NCT05057468
Lead Sponsor
Assiut University
Brief Summary

the cyclosporine showed efficacy in many immune cytopenic diseases in the light of numerous case reports and retrospective data. This study compares cyclosporin versus rituximab in steroid-refractory anemia.

Detailed Description

Auto-immune hemolytic anemia (AIHA) is a heterogeneous syndrome in adults. This disease is associated with significant morbidity-mortality. First-line treatment with prolonged corticosteroid is well identified but there is not enough data about cyclosporine treatment in case of resistance or dependence on steroids.

the cyclosporine showed efficacy in many immune cytopenic diseases in the light of numerous case reports and retrospective data. This drug is cheap, licensed in immunologic diseases, and does not expose to major infections. So, we compare cyclosporin versus rituximab in steroid-refractory anemia.

Recruitment & Eligibility

Status
RECRUITING
Sex
All
Target Recruitment
30
Inclusion Criteria
  • Patients aged more than 18 years old from any sex with a diagnosis of primary warm autoimmune hemolytic anemia (AIHA) based on the presence of hemolytic anemia and serological evidence of anti-erythrocyte antibodies, detectable by the direct antiglobulin test who have disease progression or failure after treatment with steroid therapy, or who are intolerant to treatment, or who refuse standard treatment.
  • No evidence of a lymphoproliferative malignancy or other autoimmune-related underlying conditions.
Exclusion Criteria
  • any contraindications to the drugs of the study.
  • any identified secondary cause of the AIHA.
  • pregnant or lactating women.

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
RituximabRituximab375 mg/ m2 weekly dose for a maximum of 4 weeks.
CyclosporineCyclosporine2.5-5mg/kg of cyclosporine daily for 3 months
Primary Outcome Measures
NameTimeMethod
the proportion of partial response3months

(Hb ≥10 g/dL or at least 2 g/dL increase in Hb, and no transfusion requirement

the proportion of complete response3months

Hb ≥12 g/dL and normalization of all hemolytic markers

Secondary Outcome Measures
NameTimeMethod
rate of adverse events3months

according to Common Terminology Criteria for Adverse Events Version 5

Trial Locations

Locations (1)

Assiut university hospital

🇪🇬

Assiut, Egypt

© Copyright 2025. All Rights Reserved by MedPath