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Reversing Epigenetic & Other Markers of Senescence by Transfusing Young Plasma To Older Human Subjects

Phase 1
Conditions
Aging
Interventions
Biological: Plasma Transfusion
Registration Number
NCT03353597
Lead Sponsor
Chandra Duggirala
Brief Summary

This trial is designed to study the effects of monthly transfusions of young healthy male donor plasma on biological age as assessed by DNA methylation levels, and changes in cognitive, renal, and pulmonary function, muscle strength, telomere length, testosterone, estrogen, DHEAS, IGF-1, high resolution C-Reactive protein, and expression of P16INK4a in peripheral blood T lymphocytes and skin biopsies.

Detailed Description

Aging is a process for which there is no cure. Plasma transfusions, based on extensive animal studies, have the potential to reverse many, systemic age-related changes in the human body as well as age related chronic diseases. This is a non-randomized, uncontrolled phase I/II study to study the effects of monthly transfusions of young healthy male donor plasma on biological age as assessed by DNA methylation levels, and changes in cognitive, renal, and pulmonary function, muscle strength, telomere length, testosterone, estrogen, DHEAS, IGF-1, high resolution C-Reactive protein, and expression of p16INK4a in peripheral blood T lymphocytes and skin biopsies. To determine the safety and tolerability of monthly, 2-unit transfusions of young (\<25 years of age) healthy male donor plasma for 6 months in patients older then 40 years of age.

Recruitment & Eligibility

Status
UNKNOWN
Sex
All
Target Recruitment
2120
Inclusion Criteria
  • Age > 40.
  • Stable medications for 2 months prior to Screening.
  • Signed and dated written informed consent obtained from the subject in accordance with local Institutional Review Board regulations.
  • Males and all Women of Child Bearing Potential agree to abstain from sex or use an adequate method of contraception for the duration of the study and for 30 days after the last dose of study drug. Adequate contraceptive methods include those with a low failure rate, i.e., less than 1% per year, when used consistently and correctly), and , a woman who has been surgically sterilized or who has been in a state of amenorrhea.
Exclusion Criteria
  • Dementia of any etiology.
  • Any medical condition other than dementia that could account for cognitive deficits (e.g., active seizure disorder, stroke, Central Nervous System diseases);
  • History of significant cardiovascular, hematologic, renal, or advanced hepatic disease (or laboratory evidence thereof);
  • History of major psychiatric illness or untreated depression;
  • Neutrophil count <1,500/mm3, platelets <100,000/mm3, serum creatinine >1.5x upper limit of normal (ULN), total bilirubin >1.5 x ULN, Alanine Transaminase >3 x ULN, Aspartate Transaminase >3 x ULN, or International Normalized Ratio (INR) >1.2 at Screening evaluations;
  • Evidence of any clinically significant findings on Screening or baseline evaluations which, in the opinion of the Investigator would pose a safety risk or interfere with appropriate interpretation of study data;
  • Current or recent history (within four weeks prior to Screening) of a clinically significant bacterial, fungal, or mycobacterial infection;
  • Current clinically significant viral infection;
  • Major surgery within four weeks prior to Screening;
  • Any contraindication to monthly plasma transfusions, including but not limited to:
  • History of significant transfusion complications;
  • Compatible plasma units not available;
  • Prior intolerance to intravenous (IV) fluids;
  • Immunoglobulin A deficiency by history or laboratory evidence at Screening;
  • Bleeding;
  • Any concurrent use of an anti-coagulant therapy.
  • Daily administration of Aspirin 81mg will be allowed as long as the dose is stable for 30 days prior to Screening. Anti-platelet drugs are acceptable.
  • Treatment with another investigational drug or participation in another interventional clinical trial within 3 months of Screening;
  • Treatment with any human blood product, including IV immunoglobulin, during the 6 months prior to Screening or during the trial;
  • Pregnant or lactating;
  • Positive pregnancy test at Screening or Baseline (Day 1);
  • Cancer within 5 years of Screening, except for nonmetastatic skin cancer or non-metastatic prostate cancer not expected to cause significant morbidity or mortality within one year of Baseline.
  • AB blood type.

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
Plasma TransfusionPlasma TransfusionPlasma Transfusions with 2 units of plasma per dose, for a total of 6 doses
Primary Outcome Measures
NameTimeMethod
Biological age as assessed by DNA methylation levels, to calculate the Epigenetic age.Baseline to end of Month 9.

The "epigenetic clock," as assessed by DNA methylation levels, which has been shown to be highly correlated with biologic age, longevity and is an independent predictor of mortality.

Secondary Outcome Measures
NameTimeMethod
TestosteroneBaseline and Month 9

Serum free and total Testosterone levels

EstrogenBaseline and Month 9

Serum Estrogen levels

Mental (Cognitive) FunctionBaseline and Month 9

Executive functioning, as measured by the California Stroop test

Lung (Pulmonary) FunctionBaseline and Month 9

FEV1 (Forced Expiratory Volume during the first second), and Peak Expiratory Flow

Kidney (Renal) FunctionBaseline and Month 9

Twenty-four hour urine collections will be performed by patients at Baseline and at Month 9. Creatinine Clearance, a measure of Renal function will be determined by calculating the glomerular filtration rate (GFR), which is the sum of filtration rates in all functioning nephrons.

Muscle StrengthBaseline and Month 9

Unilateral Maximal Voluntary Isometric and Concentric Strength

Telomere LengthBaseline and Month 9

A telomere is a region of repetitive nucleotide sequences at each end of a chromosome, which protects the end of the chromosome from deterioration or from fusion with neighboring chromosomes.

Telomere shortening is associated with aging, mortality and aging-related diseases. Average telomere length will be measured in white blood cells by real time PCR technique.

DHEASBaseline and Month 9

Dehydroepiandrosterone is an endogenous steroid hormone that has a role in the synthesis of sex steroids (androgens and estrogens), as well as neurotrophic and other effects

IGF-1Baseline and Month 9

Insulin Like Growth Factor -1(IGF-1) declines continuously with aging in adults, and has been shown to mediate a number of pathways that are associated with longevity.

High Sensitivity C-Reactive ProteinBaseline and Month 9

C-Reactive Protein is a blood protein that is a marker of inflammation. Studies have suggested that a persistent level of inflammation plays a major role in cardiovascular and other degenerative and aging related diseases.

P16INK4a (A marker of cellular aging)Baseline and Month 9

The cyclin- dependent kinase inhibitor CDKN2A, commonly referred to as p16INK4a or p16, has been established as a general marker of cellular senescence or aging. The expression of p16INK4a has been shown to increase exponentially with chronologic age. P16-INK4a is performed on a small specimen of blood drawn from the subjects, as well as from skin biopsy samples.

Trial Locations

Locations (1)

The Infusion Center & Clinic

🇺🇸

San Mateo, California, United States

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