A study on the safety and efficacy of cyclodextrin intrathecal administration in Niemann-Pick disease type C
Not Applicable
- Conditions
- iemann-Pick disease type C
- Registration Number
- JPRN-UMIN000023094
- Lead Sponsor
- ara Medical University
- Brief Summary
Not available
- Detailed Description
Not available
Recruitment & Eligibility
- Status
- Complete: follow-up continuing
- Sex
- All
- Target Recruitment
- 1
Inclusion Criteria
Not provided
Exclusion Criteria
1)CNS or systemic infection 2)Without neurological involvement
Study & Design
- Study Type
- Interventional
- Study Design
- Not specified
- Primary Outcome Measures
Name Time Method
- Secondary Outcome Measures
Name Time Method