MedPath

Ambrisentan for the Improvement in Right Ventricular Strain in Scleroderma Associated Pulmonary Arterial Hypertension

Not Applicable
Terminated
Conditions
Pre-Pulmonary Atrial Hypertension
Interventions
Registration Number
NCT02169752
Lead Sponsor
National Jewish Health
Brief Summary

This research study is looking at the use of the drug ambrisentan and if it can improve right ventricle function in people with systemic sclerosis-associated pre-pulmonary arterial hypertension. It is also looking at using right ventricle function changes as a marker of disease severity.

Detailed Description

This research study is looking at the use of the drug ambrisentan and if it can improve right ventricle function in people with systemic sclerosis-associated pre-pulmonary arterial hypertension. It is also looking at using right ventricle function changes as a marker of disease severity.

Pre-pulmonary arterial hypertension is a borderline elevation in blood pressure in the lungs. Pre-pulmonary arterial hypertension is not currently treated with the drug therapies that are used for pulmonary arterial hypertension. It represents a group of patients that are at risk for developing pulmonary arterial hypertension.

The administration of ambrisentan is the experimental part of this study. Ambrisentan has not been approved by the FDA for use of improving right ventricle function in people with pre-pulmonary arterial hypertension. You will still receive your normal clinical care.

The purpose of this study is to learn more about ambrisentan and its role in treating systemic sclerosis-associated pre-pulmonary arterial hypertension. Ambrisentan is already approved for use in people with systemic sclerosis-associated pulmonary arterial hypertension, but this study wants to research its role in people with pre-pulmonary arterial hypertension.

Recruitment & Eligibility

Status
TERMINATED
Sex
All
Target Recruitment
7
Inclusion Criteria
  • Age >18 years, < 80 years

  • Systemic sclerosis with any of the following features:

    1. Duration of Raynaud's phenomena >8 years
    2. Anticentromere antibody positivity
    3. isolated nucleolar-pattern ANA positivity
    4. Extensive telangiectasias
    5. DLCO < 60% in the absence of extensive ILD
    6. FVC%/DLCO% >1.6
    7. Unexplained dyspnea
  • Right heart catheterization-proven pre PAH (mean PAP 20-25 mmHg and pulmonary capillary wedge pressure <15 mmHg)

  • Systolic blood pressure >100 mmHg

  • Reliable contraception for women of childbearing age

  • Informed consent

Exclusion Criteria
  • < 18 years or > 80 years
  • Left ventricular ejection fraction < 55%
  • Systolic or diastolic left ventricular congestive heart failure
  • Liver disease (abnormal AST/ALT, chronic hepatitis, or cirrhosis)
  • Extensive ILD or FVC< 60%
  • Pregnant
  • Breast-feeding women
  • Cyclosporine use

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
PlaceboAmbrisentanSubjects will be randomly assigned in a 1:1 ration according to the computer generated random numbers to receive either placebo (sugar pill) or ambrisentan.
AmbrisentanAmbrisentanSubjects will be randomly assigned in a 1:1 ration according to the computer generated random numbers to receive either placebo (sugar pill) or ambrisentan.
Primary Outcome Measures
NameTimeMethod
Improvement in right ventricular (RV) myocardio strain > 2%1, 3 and 6 months

Assess for tolerance, gas exchange, and therapeutic benefit, resting oximetry, six minute walk with oximetry, pulmonary function testing with diffusion capacity (DLCO), and functional class will be assessed prior to ambrisentan initiation, and 1,3, and 6 months.

Secondary Outcome Measures
NameTimeMethod

Trial Locations

Locations (1)

National Jewish Health

🇺🇸

Denver, Colorado, United States

© Copyright 2025. All Rights Reserved by MedPath