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Observational Study of Real World Effectiveness Data and Safety in Patients Receiving Pazopanib With Advanced or Metastatic Renal Cell Carcinoma

Completed
Conditions
Carcinoma, Renal Cell
Interventions
Registration Number
NCT01649778
Lead Sponsor
Novartis Pharmaceuticals
Brief Summary

This is a global, multi-centre, long-term, prospective, observational study to evaluate treatment patterns and clinical outcomes in patients with advanced or metastatic RCC treated for the first time with pazopanib. The study is designed to enroll approximately 700-1000 patients in over the course of an enrollment period of approximately 18 months.There are no protocol-mandated visits or procedures associated with the study. Each patient is expected to participate for a maximum of 30 months or until premature discontinuation (i.e., due to death, withdrawal of consent, lost to follow-up or study termination).

Detailed Description

This is a global, multi-centre, long-term, prospective, observational study to evaluate treatment patterns and clinical outcomes in patients with advanced or metastatic RCC treated for the first time with pazopanib. The study is designed to enroll approximately 700-1000 patients in over the course of an enrollment period of approximately 18 months. Sites will be contacted and qualified by the estimated number of advanced or metastatic RCC patients available for enrollment annually. To the extent possible, consecutive patients meeting inclusion/exclusion criteria will be enrolled. Sites will be required to maintain a patient enrolment log of eligible patients at their treatment centres. This log will document how patients came to be included or excluded from the study, in order to assess the representativeness of the study population. The overall number of patients and sites may be adjusted during the study to meet enrollment goals, if needed. Eligible patients will be enrolled by medical oncologists and potentially by urologists experienced in the management of patients with RCC, if consistent with local practice. There are no protocol-mandated visits or procedures associated with the study. Each patient is expected to participate for a maximum of 30 months or until premature discontinuation (i.e., due to death, withdrawal of consent, lost to follow-up or study termination). Follow-up information will be collected approximately every 3 months (a window of ± 4 weeks around the date of the suggested data collection will be allowed). If the patient is not seen for a regularly scheduled visit at that time, the site may contact the patient by telephone to solicit information regarding the events of interest and to limit loss to follow up. It is anticipated that frequency of patient assessment and imaging will differ according to local standard practice; therefore the quarterly data collection time points are intended to collect all assessments (with the date of assessment) since the previous visit date.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
662
Inclusion Criteria
  • Patients eligible for enrolment in the study must meet all of the following criteria:

    • Age ≥ 18 years at enrollment
    • Documented diagnosis of advanced and/or metastatic clear cell or predominantly clear cell RCC
    • Clinical decision made to initiate treatment with pazopanib prior to enrollment in the study, but within 30 days of enrollment
    • Willing and able to provide written informed consent
Exclusion Criteria
  • Patients meeting any of the following criteria must not be enrolled in the study:

    • Patients currently participating in any interventional clinical trials in which treatment regimen and/or monitoring is dictated by a protocol
    • Previous exposure to an investigational or licensed multi-kinase inhibitor or an anti- VEGF angiogenesis inhibitor for advanced or metastatic disease
    • Life expectancy < 12 weeks

Study & Design

Study Type
OBSERVATIONAL
Study Design
Not specified
Arm && Interventions
GroupInterventionDescription
PazopanibPazopanibProspective Observational study collecting real world data on Pazopanib in patients with advanced or metastatic Renal Cell Carcinoma. Study is considered non-interventional, no drug will be provided. No study visits or procedures are mandated per protocol.
Primary Outcome Measures
NameTimeMethod
EfficacyApproximately 30 months

To evaluate overall survival (OS), progression-free survival (PFS) and the overall response rate (ORR) in patients treated with pazopanib

Relative Dose Intensity(RDI)Approximately 30 months

To characterize the relative dose intensity (RDI) and its observed effect on treatment outcomes

Characterise the RCC patient population treatedApproximately 30 months

To characterise the RCC patient population treated with pazopanib (e.g., by demographics, disease characteristics, previous RCC treatment history) in comparison to a selected clinical trial population

Evaluate SafetyFrom first treatment with pazopanib till 30 days after last dose of pazopanib treatment

To evaluate the frequency of serious adverse events(SAEs) and adverse events of special interest (AESIs) in patients treated with pazopanib. Endpoint: Any adverse event that results in a pazopanib dose modification or discontinuation. Evidence of liver toxicity (e.g., increased ALT and/or AST, liver failure). New onset or worsened hypertension. Cardiac dysfunction (e.g., decreased left ventricular function, congestive heart failure). Thyroid dysfunction.

Evaluate the change in health-related quality of life (HRQoL)Approximately 30 months from baseline

To evaluate the change in health-related quality of life (HRQoL) relative to baseline in patients treated with pazopanib

Secondary Outcome Measures
NameTimeMethod
Evaluate efficacy and safety comparable to VEG105192Approximately 30 months

To evaluate clinical effectiveness, safety and RDI in those patients with comparable baseline characteristics to those included in the Phase III clinical trial \[VEG105192\]. Endpoints: Same as primary effectiveness, safety and RDI objectives

Evaluate efficacy, safety, RDI, and HRQoLApproximately 30 months

To evaluate clinical effectiveness, safety, RDI and HRQoL in relevant subgroups treated with pazopanib

Trial Locations

Locations (1)

Novartis Investigative Site

🇬🇧

Shrewsbury, United Kingdom

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