MedPath

Double-Blind, Randomized, Placebo-Controlled, Multi-Center Phase 3 Study to Evaluate the Efficacy and Safety of Fostamatinib in COVID-19 Subjects

Phase 3
Completed
Conditions
SARS Pneumonia
Pneumonia
SARS (Severe Acute Respiratory Syndrome)
Pneumonia, Viral
SARS-Associated Coronavirus as Cause of Disease Classified Elsewhere
Covid19
Interventions
Drug: Placebo
Registration Number
NCT04629703
Lead Sponsor
Rigel Pharmaceuticals
Brief Summary

The study is a double-blind, randomized, placebo-controlled, multi-center, Phase 3 study to evaluate the efficacy and safety of fostamatinib in COVID-19 subjects.

Detailed Description

The primary objective of this study is:

To evaluate the efficacy of fostamatinib when used in combination with standard of care (SOC) in subjects hospitalized with COVID- 19 and requiring oxygen supplementation, as measured by days on oxygen.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
280
Inclusion Criteria
  • ≥18 years of age at screening.
  • The subject or a legally authorized representative has provided written informed consent.
  • Hospitalized COVID-19 subjects without respiratory failure who are either not receiving any oxygen therapy or are receiving supplemental oxygen via mask or nasal prongs.
  • Male or non-pregnant, non-lactating female subjects with SARS-CoV-2 infection documented by a hospital approved diagnostic test (eg, a Food and Drug Administration authorized test in the US) within 7 days prior to randomization.
Exclusion Criteria
  • Pregnant or lactating female of childbearing potential.
  • Use of extracorporeal membrane oxygenation (ECMO).
  • Uncontrolled hypertension (systolic blood pressure [BP] ≥160 mmHg and/or diastolic BP ≥100 mmHg), unstable angina, congestive heart failure of New York Heart Association classification III or IV, serious cardiac arrhythmia requiring treatment at screening.
  • History of myocardial infarction within 1 month prior to screening.

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Placebo (twice daily for 14 days) + Standard of CarePlaceboPlacebo (twice daily for 14 days) + Standard of Care
Fostamatinib (150 mg twice daily for 14 days) + Standard of CareFostamatinibFostamatinib (150 mg twice daily for 14 days) + Standard of Care
Primary Outcome Measures
NameTimeMethod
Number of days on oxygen from randomization on Day 1 to Day 2929 days

Number of days on oxygen from randomization on Day 1 to Day 29

Secondary Outcome Measures
NameTimeMethod
Proportion of subjects alive by Day 60 and oxygen free on Day 2960 days

Proportion of subjects alive by Day 60 and oxygen free on Day 29

Number of days in the ICU from randomization on Day 1 to Day 2929 days

Number of days in the ICU from randomization on Day 1 to Day 29

Mean change from baseline over time in clinical status score using the 8-point ordinal scale, to the average from Day 5 through Day 15.10 days

Mean change from baseline over time in clinical status score using the 8-point ordinal

All-cause mortality by Day 29.29 days

All-cause mortality by Day 29.

Time to first sustained hospital discharge by Day 29. (A discharge is defined as sustained when no readmission occurs by Day 29 after the discharge).29 days

Time to first sustained hospital discharge by Day 29. (A discharge is defined as sustained when no readmission occurs by Day 29 after the discharge).

All-cause mortality by Day 6060 days

All-cause mortality by Day 60

Proportion of subjects alive by Day 29 and oxygen free on Day 29.29 days

Proportion of subjects alive by Day 29 and oxygen free on Day 29.

Trial Locations

Locations (45)

Hospital Luxenburgo-Associação Mário Penna

🇧🇷

Belo Horizonte, Minas Gerais, Brazil

Irmandade da Santa Casa de Misericórdia de Porto Alegre - ISCMPA

🇧🇷

Porto Alegre, Rio Grande Do Sul, Brazil

Alternative Research Associates, LLC

🇺🇸

Miami, Florida, United States

Henry Ford

🇺🇸

Detroit, Michigan, United States

Harvard Medical School- Bringham and Women's Hospital

🇺🇸

Boston, Massachusetts, United States

Houston Methodist Research Institute

🇺🇸

Houston, Texas, United States

Sanatorio Mayo Privado

🇦🇷

Córdoba, Argentina

Hospital San Roque

🇦🇷

Córdoba, Argentina

Icaro Investigaciones en Medicina

🇲🇽

Chihuahua, Mexico

Hospital Ángeles Roma

🇲🇽

Mexico, Mexico

George Washington University Hospital

🇺🇸

Washington, District of Columbia, United States

Clinica Chutro

🇦🇷

Cordoba, CP, Argentina

Corporacion Medica de General San Martin

🇦🇷

San Martin, Provincia De Buenos Aires, Argentina

Hospital Del Bicentenario - Dr. Luis Federico Leloir

🇦🇷

Buenos Aires, Argentina

Hospital Lencinas

🇦🇷

Godoy Cruz, Mendoza, Argentina

The American British Cowdray Medical Center I.A.P.

🇲🇽

Mexico City, Mexico

Nuevo Hospital Civil de Guadalajara

🇲🇽

Guadalajara, Mexico

Hospital Civil de Culiacan

🇲🇽

Sinaloa, Mexico

University of California Irvine

🇺🇸

Orange, California, United States

Ascension Medical Group- St. John Clinic Infectious Disease

🇺🇸

Tulsa, Oklahoma, United States

Hospital de Alta Complejidad Cuenta Alta

🇦🇷

Buenos Aires, Argentina

Sanatorio Guemes

🇦🇷

Buenos Aires, Argentina

Clinica Zabala

🇦🇷

Buenos Aires, Argentina

Clinica Adventista Belgrano

🇦🇷

Buenos Aires, Argentina

Clinica Monte Grande

🇦🇷

Buenos Aires, Argentina

Hospital de Infecciosas Dr.Francisco Javier Muñiz

🇦🇷

Buenos Aires, Argentina

Hospital das Clínicas da Universidade Federal de Goiás (HC/UFG)

🇧🇷

Goiânia, Goiás, Brazil

Hospital Universitario de Maringa

🇧🇷

Maringá, Parana, Brazil

Sanatorio Sagrado Corazon

🇦🇷

Buenos Aires, Argentina

Hosp. Angelina Caron

🇧🇷

Campina Grande do Sul, Paraná, Brazil

Hospital des clinicas de porto alegre - Centro de pequisas clinicas

🇧🇷

Porto Alegre,, RS, Brazil

Complexo de Prevenção, Diagnóstico, Terapia e Reabilitação Respiratória LTDA

🇧🇷

Blumenau, Santa Catarina, Brazil

Clinica de Alergia Martti Antila S/S Ltda

🇧🇷

Sorocaba, Sao Paulo, Brazil

Pontificia Universidade Catolica de Campinas (PUC-CAMP) - Hospital e Maternidade Celso Pierro (HMCP)

🇧🇷

Campinas, Sao Paolo, Brazil

Hospital Universitário São Francisco na Providência de Deus

🇧🇷

Braganca Paulista, Sao Paulo, Brazil

Unidad Medica para la Salud Integral (UMSI)

🇲🇽

Monterrey, Nuevo Leon, Mexico

Hospital Bandeirantes (LeForte)

🇧🇷

Liberdade, Sao Paolo, Brazil

Fundação Faculdade Reg. de Med de SJRP

🇧🇷

São José Do Rio Preto, Sao Paulo, Brazil

Hospital Alemão Oswaldo Cruz (HAOC)

🇧🇷

Bela Vista, Sao Paolo, Brazil

Star Medica Vivo Bicentenario

🇲🇽

Nezahualcóyotl, Mex, Mexico

Köhler & Milstein Research

🇲🇽

Mérida, Yucatán, Mexico

Hospital Cardiologica Aguascalientes

🇲🇽

Aguascalientes, Mexico

Centro Medico Issemym Toluca

🇲🇽

Metepec, Mexico

CEPREP Centro de Prevención y Rehabilitación de Enfermedades Pulmonares Crónicas

🇲🇽

Nuevo León, Mexico

Loyola University Medical School

🇺🇸

Maywood, Illinois, United States

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