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Systemic and local diffusion of ethanol after administration of ethanol 96% formulated in a gel (L0122 Gel) and ethanol 98% solution (absolute ethanol) by the percutaneous route, in patients with congenital venous malformations (CVM): pharmacokinetic, pharmacodynamic and clinical study.

Phase 1
Conditions
patients with congenital venous malformations (CVM)
Registration Number
EUCTR2009-011276-29-FR
Lead Sponsor
ORFAGE
Brief Summary

Not available

Detailed Description

Not available

Recruitment & Eligibility

Status
ot Recruiting
Sex
All
Target Recruitment
31
Inclusion Criteria

-Patients of both sexes, of at least 12 years of age,
-For women of childbearing potential, negative pregnancy test at baseline,
-Patients with one clinically and radiologically (MRI) documented lesion diagnosed as CVM (pure or predominant),
-Patients for which an embolosclerotherapy by the percutaneous route is indicated as first line therapy of the test lesion, or for which previous treatments (i.e. surgery, embolosclerotherapy, laser) have been unsuccessful or insufficient,
-Patients with CVM lesional size of at least 12 cm3 (maximum craniocaudal dimension X mean dimension of 3 transverse equispaced measurements X mean dimension of 3 deepness equispaced measurements dimension) at MRI,
-Patients with focal or multifocal CVM lesion, i.e. with one or several well-interconnecting venous spaces and well-defined margins,
-Patients or parents able to follow study instructions and attend study visits,
-Written informed consent from the patients or parents.

Are the trial subjects under 18? yes
Number of subjects for this age range:
F.1.2 Adults (18-64 years) yes
F.1.2.1 Number of subjects for this age range
F.1.3 Elderly (>=65 years) yes
F.1.3.1 Number of subjects for this age range

Exclusion Criteria

-Patients under 12 years of age,
-Pregnant women, nursing mothers and women of childbearing potential with no reliable contraception from more than 2 months,
-Women of childbearing potential with a positive pregnancy test at baseline,
-Patients with CVM of non venous predominance,
-Patients with CVM that are not reachable by the percutaneous route,
-Patients with extensive superficial skin CVM (i.e. with high risk of skin necrosis),
-Patients with a test lesion adjacent to major nerves (e.g. facial nerve in the parotid region, intramuscular regions adjacent to major nerves),
-Patients with facial CVM or bone involvement,
-Patients with small CVM lesion (<12 cm3 at MRI),
-Patients requiring more than 1 ml/Kg body weight (b.w.) in USA or more than 0.5 ml/Kg b.w. in france, or more than 30 mL of absolute ethanol to infuse,
-Patients with a known allergy to one of the components of the test products,
-Patients with a suspected allergy to iodinated products,
-Patients with abnormal clotting parameters (platelets, partial thromboplastin, prothrombin time),
-Patients with an active inflammatory episode of the test lesion (i.e. acute or subacute swelling of the test lesion),
-Patients with complex malformations (e.g. Klippel-Trenaunay syndrome, Blue Rubber Bled Nevus syndrome, Muco-cutaneous familial venous malformations, Mafucci’s syndrome),
-Patients in which a surgery, laser therapy or embolosclerotherapy of the test lesion has been performed within the last 12 weeks prior to study entry,
-Asthmatic patients who require daily medications,
-Patients with a non treated or non stabilized cardiac disease,
-Patients with a suspected right-left shunt,
-Patients with an intercurrent condition or a concomitant treatment which may interfere with a good conduct or the evaluation parameters of the study,
-Patients who participated in a study within the 12 weeks prior to study entry,
-Patients or parents who are not able or willing to follow the study instructions,
-Patients or parents who refuse to give written informed consent.

Study & Design

Study Type
Interventional clinical trial of medicinal product
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Secondary Outcome Measures
NameTimeMethod
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