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Expanded Access Protocol to Provide Lumasiran to Patients With Primary Hyperoxaluria Type 1

Conditions
Primary Hyperoxaluria
Registration Number
NCT04125472
Lead Sponsor
Alnylam Pharmaceuticals
Brief Summary

The purpose of this study is to provide expanded access to lumasiran for adults and pediatric patients with Primary Hyperoxaluria Type 1 (PH1),

Detailed Description

Choosing to participate in an expanded access program is an important personal decision. Talk with your doctor and family members or friends about deciding to join a research study. To learn more about this study, please have your doctor contact the study research staff using the Contacts provided. For general information, see the link provided in More Information.

Recruitment & Eligibility

Status
APPROVED_FOR_MARKETING
Sex
All
Target Recruitment
Not specified
Inclusion Criteria
  • Documented diagnosis of Primary Hyperoxaluria Type 1
Exclusion Criteria
  • Clinically significant health concerns (with the exception of PH1)
  • Received an investigational agent within 30 days before the first dose of lumasiran or are in follow-up of another clinical study
  • Previously or currently participating in lumasiran clinical study
  • History of liver transplant

Study & Design

Study Type
EXPANDED_ACCESS
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Secondary Outcome Measures
NameTimeMethod
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