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The Brigance Assessment Of Individual Neurodevelopment In Young Children With Sickle Cell Disease- 2

Completed
Conditions
Sickle Cell Disease
Interventions
Other: Brigance Preschool Screen -II
Registration Number
NCT01123863
Lead Sponsor
St. Jude Children's Research Hospital
Brief Summary

A preliminary study was conducted involving 88 three-year-old children with sickle cell disease (SCD) who were followed at the St. Jude Children's Research Hospital Sickle Cell Center. They were offered developmental screening with the Brigance Preschool Screen-II test during their regular clinic visits from January 2006 to August 2008. Data from this work showed that 50% of 3 year old children with SCD had low developmental screening scores. In addition, the low scores were found to be associated with less parental education and with speech deficits. However they were not associated with sickle cell genotype and hemoglobin level.

The primary goal of this study is to prospectively administer Brigance Preschool Screen -II to 3 year old children with SCD and 3 year old children without SCD who come from similar socioeconomic backgrounds and compare the results between the two groups.

Detailed Description

The primary objective of this study is to compare development in 3 year old children with SCD who are not on any treatment to age matched healthy controls using pass/fail rate for the Brigance Preschool Screen II.

Secondary objectives:

1. To compare the raw scores of the Brigance Preschool Screen II between SCD and control groups.

2. To compare the pass/fail rate and the raw scores between SCD patients who are not on any treatment and those who are being treated with hydroxyurea.

3. To compare the pass/fail rate and the raw scores between SCD patients on hydroxyurea treatment and the healthy controls

4. To assess the influence of medical factors on the Brigance Preschool Screen II performance in children with SCD.

5. To assess the influence of socioeconomic factors on the Brigance Preschool II results in children with SCD and controls.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
248
Inclusion Criteria

Not provided

Exclusion Criteria

Not provided

Study & Design

Study Type
OBSERVATIONAL
Study Design
Not specified
Arm && Interventions
GroupInterventionDescription
control groupBrigance Preschool Screen -IIThe control group will consist of 3-year-old children attending day care in the Memphis area and serve as a population that come from a similar socioeconomic background as the SCD patient population. Intervention: Brigance Preschool Screen -II
Patient GroupBrigance Preschool Screen -IIThis study will administer Brigance Preschool Screen -II to 3 year old children with SCD followed at St. Jude Children's Research Hospital Intervention: Brigance Preschool Screen -II
Primary Outcome Measures
NameTimeMethod
Compare development in 3 year old children with SCD who are not on treatment to age matched controls using pass/fail rate for the Brigance Preschool Screen II.4 years
Secondary Outcome Measures
NameTimeMethod
Assess the influence of socioeconomic factors on the Brigance Preschool II results in children with SCD and controls.4 years
Compare the raw scores of the Brigance Preschool Screen II between SCD and control groups.4 years
Compare the pass/fail rate and the raw scores between SCD patients on hydroxyurea treatment and the healthy controls4 years
Assess the influence of medical factors on the Brigance Preschool Screen II performance in children with SCD.4 years
Compare the pass/fail rate and the raw scores between SCD patients who are not on any treatment and those who are being treated with hydroxyurea.4 years

Trial Locations

Locations (1)

St. Jude Children's Research Hospital

🇺🇸

Memphis, Tennessee, United States

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