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B-cell differentiation defects and clinical complications in antibody deficiency syndromes with a focus on Common Variable Immunodeficiency

Completed
Conditions
Disorder of antibody production
humoral immunodeficiency
10021429
10003816
10019815
Registration Number
NL-OMON31550
Lead Sponsor
Erasmus MC, Universitair Medisch Centrum Rotterdam
Brief Summary

Not available

Detailed Description

Not available

Recruitment & Eligibility

Status
Completed
Sex
Not specified
Target Recruitment
130
Inclusion Criteria

Patients with antibody deficiency syndromes and patients with clinical complications that can be the result of antibody deficency syndromes like bronchiectasis of unknown origin or repeated severe ENT infections without known cause despite extensive examinations.

Exclusion Criteria

Cystic fibrosis, anatomical abnormalities of the respiratory tract, primairy ciliary dyskinesia. Age below 2 years of age.

Study & Design

Study Type
Observational non invasive
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
<p>Primairy parameters:<br /><br>B-cell differentiation and maturation defects.<br /><br><br /><br>Immunological outcome: in vivo vaccination response (adults). History of<br /><br>response to vaccination (children).<br /><br><br /><br>Clinical outcome:<br /><br>The presence of auto-immune disease and the appearance or progression (if<br /><br>already present at the moment of diagnosis) of permanent pulmonary damage.</p><br>
Secondary Outcome Measures
NameTimeMethod
<p>Frequency of pneumonia after diagnosis<br /><br>Number of pneumonias with hospital admission before diagnosis<br /><br>Bronchiectasis before diagnosis<br /><br>Presence or appearance of malignacies<br /><br>Quality of life<br /><br>Nasopharyngeal carriage of bacteria<br /><br>Carriage of abdominal parasites</p><br>
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