MedPath

Temozolomide and Radiation Therapy With or Without Cediranib Maleate in Treating Patients With Newly Diagnosed Glioblastoma

Phase 2
Completed
Conditions
Adult Glioblastoma
Adult Gliosarcoma
Interventions
Radiation: 3-Dimensional Conformal Radiation Therapy
Radiation: Intensity-Modulated Radiation Therapy
Drug: Cediranib Maleate
Other: Laboratory Biomarker Analysis
Other: Placebo Administration
Drug: Temozolomide
Registration Number
NCT01062425
Lead Sponsor
National Cancer Institute (NCI)
Brief Summary

This randomized phase II trial studies temozolomide, radiation therapy, and cediranib maleate to see how well they work compared with temozolomide, radiation therapy, and a placebo in treating patients with newly diagnosed glioblastoma (a type of brain tumor). Drugs used in chemotherapy, such as temozolomide, work in different ways to stop the growth of tumor cells, either by killing the cells or by stopping them from dividing. Radiation therapy uses high energy x-rays to kill tumor cells. Cediranib maleate may stop the growth of tumor cells by blocking some of the enzymes needed for cell growth and by blocking blood flow to the tumor. It is not yet known whether temozolomide and radiation therapy are more effective when given with or without cediranib maleate in treating glioblastoma.

Detailed Description

PRIMARY OBJECTIVES:

I. To determine if the addition of cediranib (cediranib maleate) to chemoradiation treatment enhances treatment efficacy as measured by the 6-month progression-free survival rate.

SECONDARY OBJECTIVES:

I. To determine if the addition of cediranib to chemoradiation treatment enhances treatment efficacy as measured by overall survival.

II. To determine if the addition of cediranib to chemoradiation treatment enhances treatment efficacy as measured by progression-free survival.

III. To determine if there is an association between tumor O6-methylguanine-deoxyribonucleic acid (DNA) methyltransferase (MGMT) gene methylation status and treatment response and outcome.

IV. To compare and record the toxicities of the cediranib + chemoradiation arm versus the chemoradiation arm.

V. To evaluate whether 6-month progression-free survival is associated with overall survival.

OUTLINE: Patients are randomized to 1 of 2 treatment arms.

ARM I: Patients receive cediranib maleate orally (PO) once daily (QD) for 3 days. Patients then undergo radiation therapy (intensity-modulated radiation therapy or 3-dimensional conformal radiation therapy) QD, 5 days a week, for 6 weeks and receive temozolomide PO QD and cediranib maleate PO QD for 6 weeks. Patients then receive temozolomide PO QD alone on days 1-5. Treatment with temozolomide repeats every 28 days for up to 12 courses in the absence of disease progression or unacceptable toxicity.

ARM II: Patients receive placebo PO QD for 3 days. Patients then undergo radiation therapy (intensity-modulated radiation therapy or 3-dimensional conformal radiation therapy) QD, 5 days a week, for 6 weeks and receive temozolomide PO QD and placebo PO QD for 6 weeks. Patients then receive temozolomide PO QD alone on days 1-5. Treatment with temozolomide repeats every 28 days for up to 12 courses in the absence of disease progression or unacceptable toxicity.

After completion of study treatment, patients are followed up every 3 months for 1 year, every 4 months for 1 year, and then every 6 months thereafter.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
261
Inclusion Criteria
  • Histologically proven diagnosis of glioblastoma or gliosarcoma (World Health Organization [WHO] grade IV) confirmed by central review prior to step 2 registration

  • Tumor tissue that is determined by central pathology review prior to step 2 registration to be of sufficient size for analysis of MGMT status

    • Patients must have at least 1 block of tumor tissue; submission of 2 blocks is strongly encouraged
    • Cavitron ultrasonic aspirator (CUSA)-derived material is not allowed; fresh frozen tumor tissue acquisition is encouraged
    • Diagnosis must be made by surgical excision, either partial or complete; stereotactic biopsy is not allowed because it will not provide sufficient tissue for MGMT analysis
    • The tumor tissue must be sent as soon as possible to maximize the likelihood of eligibility; tumor tissue may not be submitted later than 28 days after the surgical procedure, because tissue analysis will not be able to be performed in time for treatment to commence by the mandatory 6-week post-surgery outer limit; submission of tissue earlier than 28 days post-surgery is highly recommended
  • The tumor must have a supratentorial component

  • History/physical examination, including neurologic examination, within 14 days prior to step 2 registration

  • The patient must have recovered from the effects of surgery, post-operative infection, and other complications before step 2 registration

  • A diagnostic contrast-enhanced magnetic resonance imaging (MRI) of the brain must be performed preoperatively and postoperatively prior to step 1 registration; the postoperative scan must be performed within 28 days prior to step 1 registration

  • Documentation of steroid doses/concurrent medications within 14 days prior to step 2 registration

  • Karnofsky performance status >= 70 within 14 days prior to step 2 registration

  • Complete blood count (CBC)/differential obtained within 14 days prior to step 2 registration on study, with adequate bone marrow function defined as follows:

  • Absolute neutrophil count (ANC) >= 1,800 cells/mm^3

  • Platelets >= 100,000 cells/mm^3

  • Hemoglobin >=10.0 g/dl (Note: The use of transfusion or other intervention to achieve hemoglobin (Hgb) >= 10.0 g/dl is acceptable)

  • Adequate renal function, as defined below:

  • Blood urea nitrogen (BUN) =< 30 mg/dl within 14 days prior to step 2 registration

  • Creatinine =< 1.7 mg/dl within 14 days prior to step 2 registration

  • Alanine aminotransferase (ALT)/aspartate aminotransferase (AST) =< 3 x normal range within 14 days prior to step 2 registration

  • Systolic blood pressure =< 140 mm Hg AND diastolic pressure =< 90 mm Hg within 14 days prior to step 2 registration in the presence or absence of a stable regimen of anti-hypertensive therapy

  • Prothrombin time/international normalized ratio (PT INR) < 1.4 for patients not on warfarin confirmed by testing within 1 week of step 2 registration

  • Patients on full-dose anticoagulants (e.g., warfarin or low molecular weight [LMW] heparin) must meet both of the following criteria:

    • No active bleeding or pathological condition that carries a high risk of bleeding (e.g., tumor involving major vessels or known varices)
    • In-range INR (usually between 2 and 3) on a stable dose of oral anticoagulant or on a stable dose of low molecular weight heparin
  • Patient must provide study specific informed consent prior to step 1 registration

  • Women of childbearing potential and male participants must practice adequate contraception

  • For females of child-bearing potential, negative serum pregnancy test within 14 days prior to step 2 registration

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Exclusion Criteria
  • Prior invasive malignancy (except for non-melanomatous skin cancer) unless disease free for >= 3 years; (for example, carcinoma in situ of the breast, oral cavity, and cervix are all permissible)

  • Recurrent or multifocal malignant gliomas

  • Metastases detected below the tentorium or beyond the cranial vault

  • Prior chemotherapy or radiosensitizers for cancers of the head and neck region; note that prior chemotherapy for a different cancer is allowable (except temozolomide or cediranib); prior use of Gliadel wafers or any other intratumoral or intracavitary treatment are not permitted

  • Prior radiotherapy to the head or neck (except for T1 glottic cancer), resulting in overlap of radiation fields

  • Severe, active co-morbidity, defined as follows:

    • Unstable angina and/or congestive heart failure requiring hospitalization
    • Transmural myocardial infarction within the last 6 months
    • Evidence of recent myocardial infarction or ischemia by the findings of S-T elevations of >= 2 mm using the analysis of an electrocardiogram (EKG) performed within 14 days of step 2 registration
    • New York Heart Association grade II or greater congestive heart failure requiring hospitalization within 12 months prior to step 2 registration
    • History of stroke, cerebral vascular accident (CVA) or transient ischemic attack within 6 months
    • Serious and inadequately controlled cardiac arrhythmia
    • Significant vascular disease (e.g., aortic aneurysm, history of aortic dissection) or clinically significant peripheral vascular disease
    • Evidence of bleeding diathesis or coagulopathy
    • Serious or non-healing wound, ulcer, or bone fracture or history of abdominal fistula, gastrointestinal perforation, intra-abdominal abscess major surgical procedure, open biopsy, or significant traumatic injury within 28 days prior to step 2 registration, with the exception of the craniotomy for tumor resection
    • Acute bacterial or fungal infection requiring intravenous antibiotics at the time of step 2 registration
    • Chronic obstructive pulmonary disease exacerbation or other respiratory illness requiring hospitalization or precluding study therapy at the time of step 2 registration
    • Hepatic insufficiency resulting in clinical jaundice and/or coagulation defects
    • Acquired immune deficiency syndrome (AIDS) based upon current Centers for Disease Control (CDC) definition; note, however, that human immunodeficiency virus (HIV) testing is not required for entry into this protocol
    • Active connective tissue disorders, such as lupus or scleroderma, which in the opinion of the treating physician may put the patient at high risk for radiation toxicity
    • Any other major medical illnesses or psychiatric impairments that in the investigator's opinion will prevent administration or completion of protocol therapy
  • Pregnancy or women of childbearing potential and men who are sexually active and not willing/able to use medically acceptable forms of contraception

  • Pregnant or lactating women

  • Prior allergic reaction to temozolomide

  • Patients treated on any other therapeutic clinical protocols within 30 days prior to step 1 registration or during participation in the study

  • History of allergic reactions attributed to compounds of similar chemical or biologic composition to cediranib

  • Mean QTc >500 msec (with Bazett's correction) in screening electrocardiogram or history of familial long QT syndrome or other significant ECG abnormality noted within 14 days of treatment

  • Patients receiving concurrent vascular endothelial growth factor (VEGF) inhibitors are prohibited from participating in this study

  • Patients must not be on enzyme-inducing anti-epileptic drugs (EIAED); patients may be on non-enzyme inducing anti-epileptic drugs (NEIAED) or may not be taking any anti-epileptic drugs; in patients who have previously been on EIAED there must be at least a 14 day period since the last dose of an EIAED before the first dose of cediranib

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Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Placebo, TMZ, and RTPlacebo AdministrationPlacebo (3 days) followed by radiation therapy (RT) + daily temozolomide (TMZ) + placebo followed by placebo monotherapy (4 weeks) followed by TMZ + placebo for 12 cycle maximum.
Placebo, TMZ, and RTIntensity-Modulated Radiation TherapyPlacebo (3 days) followed by radiation therapy (RT) + daily temozolomide (TMZ) + placebo followed by placebo monotherapy (4 weeks) followed by TMZ + placebo for 12 cycle maximum.
Placebo, TMZ, and RT3-Dimensional Conformal Radiation TherapyPlacebo (3 days) followed by radiation therapy (RT) + daily temozolomide (TMZ) + placebo followed by placebo monotherapy (4 weeks) followed by TMZ + placebo for 12 cycle maximum.
Placebo, TMZ, and RTLaboratory Biomarker AnalysisPlacebo (3 days) followed by radiation therapy (RT) + daily temozolomide (TMZ) + placebo followed by placebo monotherapy (4 weeks) followed by TMZ + placebo for 12 cycle maximum.
Cediranib, TMZ, and RT3-Dimensional Conformal Radiation TherapyCediranib (3 days) followed by radiation therapy (RT) + daily temozolomide (TMZ) + cediranib followed by cediranib monotherapy (4 weeks) followed by TMZ + cediranib for 12 cycle maximum.
Cediranib, TMZ, and RTIntensity-Modulated Radiation TherapyCediranib (3 days) followed by radiation therapy (RT) + daily temozolomide (TMZ) + cediranib followed by cediranib monotherapy (4 weeks) followed by TMZ + cediranib for 12 cycle maximum.
Cediranib, TMZ, and RTLaboratory Biomarker AnalysisCediranib (3 days) followed by radiation therapy (RT) + daily temozolomide (TMZ) + cediranib followed by cediranib monotherapy (4 weeks) followed by TMZ + cediranib for 12 cycle maximum.
Cediranib, TMZ, and RTCediranib MaleateCediranib (3 days) followed by radiation therapy (RT) + daily temozolomide (TMZ) + cediranib followed by cediranib monotherapy (4 weeks) followed by TMZ + cediranib for 12 cycle maximum.
Cediranib, TMZ, and RTTemozolomideCediranib (3 days) followed by radiation therapy (RT) + daily temozolomide (TMZ) + cediranib followed by cediranib monotherapy (4 weeks) followed by TMZ + cediranib for 12 cycle maximum.
Placebo, TMZ, and RTTemozolomidePlacebo (3 days) followed by radiation therapy (RT) + daily temozolomide (TMZ) + placebo followed by placebo monotherapy (4 weeks) followed by TMZ + placebo for 12 cycle maximum.
Primary Outcome Measures
NameTimeMethod
6-month Progression-free Survival RateFrom randomization to 6 months.

Six-month progression-free survival is the rate of patients who have NOT progressed at six months, where progressive disease is defined as any of the following: ≥ 25% increase in sum of the products of perpendicular diameters of enhancing lesions; any new lesion; or clinical deterioration. Progression will be determined by central review of MRI exams, assessed using MacDonald criteria for progression versus response on 2D T1 and T2 weighted images.

Secondary Outcome Measures
NameTimeMethod
Overall Survival (OS)From randomization to time of death due to any cause. Patients are followed until death. Analysis occurs after all patients have been potentially followed for six months.

OS will be estimated using the Kaplan-Meier method and differences between treatment arms will be tested using the log rank test. Multivariate analyses with the Cox proportional hazard model for OS will be performed with the stratification variables as fixed variables to assess the treatment effect adjusting patient-specific risk factors.

Progression-free Survival (PFS)From randomization to time of first progression or death due to any cause. Patients are followed until death. Analysis occurs after all patients have been potentially followed for six months.

Progression-free survival time is defined as time from randomization to date of first progression or death from any cause and is estimated by the Kaplan-Meier method. Patients last known to be alive without progression are censored at the date of last contact. Progression is defined as any of the following: ≥ 25% increase in sum of the products of perpendicular diameters of enhancing lesions; any new lesion; or clinical deterioration.

Incidence of Grade 3+ ToxicitiesFrom randomization to six months.

The number of patients with reported grade 3 and higher treatment-related toxicities as assessed by Common Terminology Criteria for Adverse Events version 4.0

Trial Locations

Locations (105)

University of Maryland/Greenebaum Cancer Center

🇺🇸

Baltimore, Maryland, United States

Thomas Jefferson University Hospital

🇺🇸

Philadelphia, Pennsylvania, United States

Rush University Medical Center

🇺🇸

Chicago, Illinois, United States

Massachusetts General Hospital Cancer Center

🇺🇸

Boston, Massachusetts, United States

Brigham and Women's Hospital

🇺🇸

Boston, Massachusetts, United States

University of Washington Medical Center - Montlake

🇺🇸

Seattle, Washington, United States

University of Cincinnati Cancer Center-UC Medical Center

🇺🇸

Cincinnati, Ohio, United States

Kansas City NCI Community Oncology Research Program

🇺🇸

Prairie Village, Kansas, United States

University of Kansas Cancer Center

🇺🇸

Kansas City, Kansas, United States

LDS Hospital

🇺🇸

Salt Lake City, Utah, United States

The Kirklin Clinic at Acton Road

🇺🇸

Birmingham, Alabama, United States

Henry Ford Hospital

🇺🇸

Detroit, Michigan, United States

Ascension Saint John Hospital

🇺🇸

Detroit, Michigan, United States

Legacy Good Samaritan Hospital and Medical Center

🇺🇸

Portland, Oregon, United States

Northwestern University

🇺🇸

Chicago, Illinois, United States

Saint Alphonsus Cancer Care Center-Boise

🇺🇸

Boise, Idaho, United States

Radiation Oncology Associates PC

🇺🇸

Fort Wayne, Indiana, United States

OSF Saint Francis Medical Center

🇺🇸

Peoria, Illinois, United States

UH Seidman Cancer Center at Salem Regional Medical Center

🇺🇸

Salem, Ohio, United States

Summa Health System - Akron Campus

🇺🇸

Akron, Ohio, United States

Dana-Farber Cancer Institute

🇺🇸

Boston, Massachusetts, United States

Cancer Treatment Center

🇺🇸

Wooster, Ohio, United States

Northeast Radiation Oncology Center

🇺🇸

Dunmore, Pennsylvania, United States

UPMC Washington Hospital Radiation Oncology

🇺🇸

Washington, Pennsylvania, United States

Saint John Macomb-Oakland Hospital

🇺🇸

Warren, Michigan, United States

Jefferson Abington Hospital

🇺🇸

Abington, Pennsylvania, United States

West Michigan Cancer Center

🇺🇸

Kalamazoo, Michigan, United States

Ohio State University Comprehensive Cancer Center

🇺🇸

Columbus, Ohio, United States

University of Rochester

🇺🇸

Rochester, New York, United States

Ascension Saint Mary's Hospital

🇺🇸

Saginaw, Michigan, United States

Bryn Mawr Hospital

🇺🇸

Bryn Mawr, Pennsylvania, United States

Mercy Hospital

🇺🇸

Coon Rapids, Minnesota, United States

Lake Huron Medical Center

🇺🇸

Port Huron, Michigan, United States

Summa Health System - Barberton Campus

🇺🇸

Barberton, Ohio, United States

Regions Hospital

🇺🇸

Saint Paul, Minnesota, United States

Washington University School of Medicine

🇺🇸

Saint Louis, Missouri, United States

Cleveland Clinic Akron General

🇺🇸

Akron, Ohio, United States

Sparrow Hospital

🇺🇸

Lansing, Michigan, United States

UPMC Cancer Centers - Arnold Palmer Pavilion

🇺🇸

Greensburg, Pennsylvania, United States

Rapid City Regional Hospital

🇺🇸

Rapid City, South Dakota, United States

Natalie Warren Bryant Cancer Center at Saint Francis

🇺🇸

Tulsa, Oklahoma, United States

Saint George Regional Medical Center

🇺🇸

Saint George, Utah, United States

Reading Hospital

🇺🇸

West Reading, Pennsylvania, United States

Allegheny General Hospital

🇺🇸

Pittsburgh, Pennsylvania, United States

University of Texas Health Science Center at San Antonio

🇺🇸

San Antonio, Texas, United States

Aspirus Regional Cancer Center

🇺🇸

Wausau, Wisconsin, United States

Virginia Mason Medical Center

🇺🇸

Seattle, Washington, United States

Intermountain Medical Center

🇺🇸

Murray, Utah, United States

Swedish Medical Center-First Hill

🇺🇸

Seattle, Washington, United States

Wheeling Hospital/Schiffler Cancer Center

🇺🇸

Wheeling, West Virginia, United States

Utah Valley Regional Medical Center

🇺🇸

Provo, Utah, United States

Utah Cancer Specialists-Salt Lake City

🇺🇸

Salt Lake City, Utah, United States

IU Health Methodist Hospital

🇺🇸

Indianapolis, Indiana, United States

Providence Portland Medical Center

🇺🇸

Portland, Oregon, United States

University Hospitals Portage Medical Center

🇺🇸

Ravenna, Ohio, United States

Compass Oncology Vancouver

🇺🇸

Vancouver, Washington, United States

Maine Medical Center- Scarborough Campus

🇺🇸

Scarborough, Maine, United States

Banner University Medical Center - Tucson

🇺🇸

Tucson, Arizona, United States

Arizona Oncology Services Foundation

🇺🇸

Scottsdale, Arizona, United States

City of Hope Comprehensive Cancer Center

🇺🇸

Duarte, California, United States

Saint Joseph Hospital - Orange

🇺🇸

Orange, California, United States

Poudre Valley Hospital

🇺🇸

Fort Collins, Colorado, United States

AdventHealth Orlando

🇺🇸

Orlando, Florida, United States

Christiana Care Health System-Christiana Hospital

🇺🇸

Newark, Delaware, United States

The Hospital of Central Connecticut

🇺🇸

New Britain, Connecticut, United States

Smilow Cancer Hospital Care Center at Saint Francis

🇺🇸

Hartford, Connecticut, United States

Bay Medical Center

🇺🇸

Panama City, Florida, United States

Emory University Hospital Midtown

🇺🇸

Atlanta, Georgia, United States

Emory University Hospital/Winship Cancer Institute

🇺🇸

Atlanta, Georgia, United States

Parkview Hospital Randallia

🇺🇸

Fort Wayne, Indiana, United States

Carle Cancer Center

🇺🇸

Urbana, Illinois, United States

United Hospital

🇺🇸

Saint Paul, Minnesota, United States

Clackamas Radiation Oncology Center

🇺🇸

Clackamas, Oregon, United States

Providence Saint Vincent Medical Center

🇺🇸

Portland, Oregon, United States

Saint Luke's University Hospital-Bethlehem Campus

🇺🇸

Bethlehem, Pennsylvania, United States

Paoli Memorial Hospital

🇺🇸

Paoli, Pennsylvania, United States

Penn State Milton S Hershey Medical Center

🇺🇸

Hershey, Pennsylvania, United States

Lankenau Medical Center

🇺🇸

Wynnewood, Pennsylvania, United States

UT Southwestern/Simmons Cancer Center-Dallas

🇺🇸

Dallas, Texas, United States

Spartanburg Medical Center

🇺🇸

Spartanburg, South Carolina, United States

University of Texas Medical Branch

🇺🇸

Galveston, Texas, United States

McKay-Dee Hospital Center

🇺🇸

Ogden, Utah, United States

Inova Fairfax Hospital

🇺🇸

Falls Church, Virginia, United States

Genesys Regional Medical Center-West Flint Campus

🇺🇸

Flint, Michigan, United States

Henry Ford Macomb Hospital-Clinton Township

🇺🇸

Clinton Township, Michigan, United States

University of Alabama at Birmingham Cancer Center

🇺🇸

Birmingham, Alabama, United States

Carolinas Medical Center/Levine Cancer Institute

🇺🇸

Charlotte, North Carolina, United States

Saint Joseph Mercy Oakland

🇺🇸

Pontiac, Michigan, United States

Sparta Cancer Treatment Center

🇺🇸

Sparta, New Jersey, United States

Minnesota Oncology Hematology PA-Maplewood

🇺🇸

Maplewood, Minnesota, United States

University of Cincinnati Cancer Center-West Chester

🇺🇸

West Chester, Ohio, United States

University of Hawaii Cancer Center

🇺🇸

Honolulu, Hawaii, United States

The Cancer Center of Hawaii-Liliha

🇺🇸

Honolulu, Hawaii, United States

Yale University

🇺🇸

New Haven, Connecticut, United States

Queen's Medical Center

🇺🇸

Honolulu, Hawaii, United States

Nebraska Methodist Hospital

🇺🇸

Omaha, Nebraska, United States

University of Wisconsin Carbone Cancer Center

🇺🇸

Madison, Wisconsin, United States

Baptist Health Lexington

🇺🇸

Lexington, Kentucky, United States

University of Kentucky/Markey Cancer Center

🇺🇸

Lexington, Kentucky, United States

Saint Joseph Mercy Hospital

🇺🇸

Ann Arbor, Michigan, United States

Saint Luke's Hospital of Kansas City

🇺🇸

Kansas City, Missouri, United States

Medical College of Wisconsin

🇺🇸

Milwaukee, Wisconsin, United States

Novant Health Forsyth Medical Center

🇺🇸

Winston-Salem, North Carolina, United States

Wake Forest University Health Sciences

🇺🇸

Winston-Salem, North Carolina, United States

Medical University of South Carolina

🇺🇸

Charleston, South Carolina, United States

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