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ongitudinal investigation of quantitative MR imaging marker in leg muscles in Morbus Pompe

Not Applicable
Recruiting
Conditions
E74.0
Glycogen storage disease
Registration Number
DRKS00023874
Lead Sponsor
BG UK Bergmannsheil / Neurologie
Brief Summary

Not available

Detailed Description

Not available

Recruitment & Eligibility

Status
Recruiting
Sex
All
Target Recruitment
30
Inclusion Criteria

Ensured diagnosis of Morbus Pompe OR no neuromuscular disorders at all (healthy controls)

Exclusion Criteria

MR contraindications e.g. implants, respiratory insufficency

Study & Design

Study Type
interventional
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
i)After finishing acquisition and evaluation of all participants for timepoint 1, we will perform initial cross sectional comparisons between LOPD patients and matched controls to reproduce our previous findings, of increased diffusivity in LOPD muscles with <10% fat.<br>ii)After finishing all acquisitions longitudinal analysis of quantitative parameters (diffusion, fat and T2) in LOPD patients and in controls, and the analysis of the interaction between the timespan and the population group will be performed<br>
Secondary Outcome Measures
NameTimeMethod
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