MedPath

A Study Evaluating the Long-term Safety of VX-445 Combination Therapy

Phase 3
Completed
Conditions
Cystic Fibrosis
Interventions
Registration Number
NCT04043806
Lead Sponsor
Vertex Pharmaceuticals Incorporated
Brief Summary

This study evaluated the long-term safety and tolerability of elexacaftor (ELX), tezacaftor (TEZ), and ivacaftor (IVA) triple combination (TC) treatment in participants with cystic fibrosis (CF).

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
458
Inclusion Criteria
  • Currently participating in study VX17-659-105 (NCT03447262)
Exclusion Criteria
  • History of drug intolerance in study VX17-659-105 that would pose an additional risk to the participant in the opinion of the investigator
  • Current participation in an investigational drug trial (other than study VX17-659-105)

Other protocol defined Inclusion/Exclusion criteria may apply.

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
ELX/TEZ/IVAIVAPart A: Participants received ELX 200 milligram (mg) once daily (qd),TEZ 100 mg qd, and IVA 150 mg every 12 hours (q12h) in the treatment period for 96 weeks. Part B: Participants from certain countries participated in Part B and continued to received ELX 200 mg qd /TEZ 100 mg qd/IVA 150 mg q12h in the treatment period for 48 weeks.
ELX/TEZ/IVAELX/TEZ/IVAPart A: Participants received ELX 200 milligram (mg) once daily (qd),TEZ 100 mg qd, and IVA 150 mg every 12 hours (q12h) in the treatment period for 96 weeks. Part B: Participants from certain countries participated in Part B and continued to received ELX 200 mg qd /TEZ 100 mg qd/IVA 150 mg q12h in the treatment period for 48 weeks.
Primary Outcome Measures
NameTimeMethod
Part A: Safety and Tolerability as Assessed by Number of Participants With Treatment-Emergent Adverse Events (TEAEs) and Serious Adverse Events (SAEs)From Baseline through Week 100
Secondary Outcome Measures
NameTimeMethod

Trial Locations

Locations (97)

University of Alabama at Birmingham

🇺🇸

Birmingham, Alabama, United States

Stanford University

🇺🇸

Palo Alto, California, United States

Children's Hospital Colorado

🇺🇸

Aurora, Colorado, United States

Hartford Hospital

🇺🇸

Hartford, Connecticut, United States

Yale New Haven Hospital

🇺🇸

New Haven, Connecticut, United States

University of Miami Miller School of Medicine

🇺🇸

Miami, Florida, United States

Nicklaus Children's Hospital

🇺🇸

Miami, Florida, United States

Arnold Palmer Hospital Pulmonary and Sleep Medicine

🇺🇸

Orlando, Florida, United States

Johns Hopkins All Children's Hospital Outpatient Care Center

🇺🇸

Saint Petersburg, Florida, United States

St. Luke's CF Center of Idaho

🇺🇸

Boise, Idaho, United States

Scroll for more (87 remaining)
University of Alabama at Birmingham
🇺🇸Birmingham, Alabama, United States

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