MedPath

Efficacy and Safety Trial of Rimegepant for Migraine Prevention in Adults

Phase 2
Completed
Conditions
Migraine
Interventions
Drug: Placebo
Registration Number
NCT03732638
Lead Sponsor
Pfizer
Brief Summary

The purpose of this is study is to compare the efficacy of BHV-3000 (rimegepant) to placebo as a preventive treatment for migraine, as measured by the reduction in the number of migraine days per month.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
1590
Inclusion Criteria
  1. Subject has at least 1 year history of migraine (with or without aura) consistent with a diagnosis according to the International Classification of Headache Disorders, 3rd Edition, including the following:

    1. Age of onset of migraines prior to 50 years of age
    2. Migraine attacks, on average, lasting 4 - 72 hours if untreated
    3. Per subject report, 4 - 18 migraine attacks of moderate to severe intensity per month within the last 3 months prior to the Screening Visit
    4. 6 or more migraine days during the Observation Period
    5. Not more than 18 headache days during the Observation Period
    6. Ability to distinguish migraine attacks from tension/cluster headaches
    7. Subjects on prophylactic migraine medication are permitted to remain on 1 medication with possible migraine-prophylactic effects if the dose has been stable for at least 3 months prior to the Screening Visit, and the dose is not expected to change during the course of the study.
Exclusion Criteria
  1. Subject with a history of HIV disease
  2. Subject history with current evidence of uncontrolled, unstable or recently diagnosed cardiovascular disease, such as ischemic heart disease, coronary artery vasospasm, and cerebral ischemia. Subjects with Myocardial Infarction (MI), Acute Coronary Syndrome (ACS), Percutaneous Coronary Intervention (PCI), cardiac surgery, stroke or transient ischemic attack (TIA) during the 6 months prior to screening
  3. Uncontrolled hypertension (high blood pressure), or uncontrolled diabetes (however subjects can be included who have stable hypertension and/or diabetes for at least 3 months prior to screening).
  4. Subjects with major depressive episode within the last 12 months, major depressive disorder or any anxiety disorder requiring more than 1 medication for each disorder. Medications to treat major depressive disorder or an anxiety disorder must have been at a stable dose for at least 3 months prior to the Screening visit.
  5. Subjects with other pain syndromes, psychiatric conditions, dementia, or significant neurological disorders (other than migraine) that, in the Investigator's opinion, might interfere with study assessments
  6. Subject has a history of gastric, or small intestinal surgery (including Gastric Bypass, Gastric Banding, Gastric Sleeve, Gastric Balloon, etc.), or has disease that causes malabsorption
  7. Body mass index ≥ 33 kg/m2
  8. Subject has current diagnosis of major depressive disorder requiring treatment with atypical antipsychotics, schizophrenia, bipolar disorder, or borderline personality disorder
  9. History of gallstones or cholecystectomy.
  10. The subject has a history or current evidence of any unstable medical conditions (e.g., history of congenital heart disease or arrhythmia, known or suspected infection, hepatitis B or C, or cancer) that, in the investigator's opinion, would expose them to undue risk of a significant adverse event (AE) or interfere with assessments of safety or efficacy during the course of the trial.

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
DBT Placebo/OL RimegepantPlaceboDBT Phase (Weeks 1 through 12): Participants received a single oral dose of placebo matching to rimegepant tablet EOD for 12 weeks. OLE Phase (Weeks 13 through 64): Participants who continued to meet study entry criteria and had acceptable laboratory test results per protocol, entered the OLE phase and received a single oral dose of rimegepant 75 mg tablet EOD for 52 weeks. If participants had a migraine on a day that they were not scheduled to dose with rimegepant, they could take one tablet of rimegepant 75 mg on that calendar day to treat a migraine (PRN dosing). After completing the OLE phase, participants had follow-up safety visits 2 and 8 weeks after the End-of-Treatment (EOT) visit. Participants who did not complete the DBT phase and/or did not enter or complete the OLE phase were to complete the EOT visit, the 2-week follow-up safety visit, and the 8-week follow-up safety visit after their early discontinuation.
DBT Rimegepant/OL RimegepantRimegepantDBT Phase (Weeks 1 through 12): Participants received a single oral dose of rimegepant 75 mg tablet every other day (EOD) for 12 weeks. OLE Phase (Weeks 13 through 64): Participants who continued to meet study entry criteria and had acceptable laboratory test results per protocol, entered the OLE phase and received a single oral dose of rimegepant 75 mg tablet EOD for 52 weeks. If participants had a migraine on a day that they were not scheduled to dose with rimegepant, they could take one tablet of rimegepant 75 mg on that calendar day to treat a migraine (as needed \[PRN\] dosing). After completing the OLE phase, participants had follow-up safety visits 2 and 8 weeks after the End-of-Treatment (EOT) visit. Participants who did not complete the DBT phase and/or did not enter or complete the OLE phase were to complete the EOT visit, the 2-week follow-up safety visit, and the 8-week follow-up safety visit after their early discontinuation.
DBT Placebo/OL RimegepantRimegepantDBT Phase (Weeks 1 through 12): Participants received a single oral dose of placebo matching to rimegepant tablet EOD for 12 weeks. OLE Phase (Weeks 13 through 64): Participants who continued to meet study entry criteria and had acceptable laboratory test results per protocol, entered the OLE phase and received a single oral dose of rimegepant 75 mg tablet EOD for 52 weeks. If participants had a migraine on a day that they were not scheduled to dose with rimegepant, they could take one tablet of rimegepant 75 mg on that calendar day to treat a migraine (PRN dosing). After completing the OLE phase, participants had follow-up safety visits 2 and 8 weeks after the End-of-Treatment (EOT) visit. Participants who did not complete the DBT phase and/or did not enter or complete the OLE phase were to complete the EOT visit, the 2-week follow-up safety visit, and the 8-week follow-up safety visit after their early discontinuation.
Primary Outcome Measures
NameTimeMethod
Change From Baseline in the Mean Number of Total Migraine Days Per Month in the Last 4 Weeks of the DBT PhaseOP and Weeks 9 to 12 of the DBT phase

A migraine day: any calendar day in which the participant experienced a qualified migraine headache (onset, continuation, or recurrence of the migraine headache). A qualified migraine headache: a migraine with or without aura, lasting for ≥30 minutes, and meeting at least 1 of the following criteria (a and/or b): a) ≥2 of the following: unilateral location, pulsating quality, moderate to severe pain intensity, aggravation by or causing avoidance of routine physical activity; b) ≥1 of the following: nausea and/or vomiting, photophobia, and phonophobia. If the participant took a migraine-specific medication during aura or to treat headache on a calendar day, it was counted as a migraine day regardless of the duration and pain features/associated symptoms.

Months were defined as 28-day intervals. The change from baseline was calculated as the number of monthly migraine days during the last 4 weeks of the DBT phase (Weeks 9 to 12) minus number of monthly migraine days during the OP.

Secondary Outcome Measures
NameTimeMethod
Number of Participants Who Had ≥ 50% Reduction in Moderate or Severe Migraine Days Per Month in the Last 4 Weeks of the DBT PhaseOP and Weeks 9 to 12 of the DBT phase

A migraine day was any calendar day in which the participant experienced a qualified migraine headache (as previously described). If the participant took a migraine-specific medication during aura or to treat headache on a calendar day, it was counted as a migraine day regardless of the duration and pain features/associated symptoms. A moderate or severe migraine day was a migraine day of moderate or severe pain intensity. Months were defined as 28-day intervals.

A reduction of at least 50% in the mean number of moderate or severe monthly migraine days was determined if the number of moderate or severe monthly migraine days in the last 4 weeks of the DBT (Weeks 9 to 12) was less than or equal to half (50%) of the number of moderate or severe monthly migraine days in the OP.

Change From Baseline in the Mean Number of Migraine Days Per Month Over the Entire Course of the DBT PhaseOP and Weeks 1 to 12 of the DBT phase

A migraine day was any calendar day in which the participant experienced a qualified migraine headache (as previously described). If the participant took a migraine-specific medication during aura or to treat headache on a calendar day, it was counted as a migraine day regardless of the duration and pain features/associated symptoms. Months were defined as 28-day intervals.

The change from baseline was calculated as the number of monthly migraine days during the DBT phase (Weeks 1 to 12) minus the number of monthly migraine days during the OP.

Number of Participants With AEs, SAEs, AEs Leading to Study Drug Discontinuation in the OLE PhaseOLE Phase (Weeks 13 through 64)

An AE was defined as any new untoward medical occurrence or worsening of a pre-existing medical condition on-treatment in a patient or clinical investigation participant administered an investigational (medicinal) product and that did not necessarily have a causal relationship with this treatment. An SAE was defined as any event that met any of the following criteria: death; life-threatening; inpatient hospitalization or prolongation of existing hospitalization; persistent or significant disability/incapacity; congenital anomaly/birth defect in the offspring of a participant who received rimegepant; other important medical events that may not have resulted in death, be life-threatening, or required hospitalization, based upon appropriate medical judgment, they may have jeopardized the participant and may have required medical or surgical intervention.

Number of Participants With Clinically Significant Laboratory Abnormalities in the DBT PhaseWeeks 1 to 12 of the DBT phase

Clinically significant laboratory abnormalities were defined as Grade 3 to 4 laboratory test results according to numeric laboratory test criteria found in Common Technical Criteria for Adverse Events (CTCAE) Version 5.0 (2017) if available; otherwise, according to Division of Acquired Immune Deficiency Syndrome (DAIDS) Table for Grading the Severity of Adult and Pediatric Adverse Events Corrected Version 2.1 (2017) for glucose, LDL-cholesterol, uric acid, and urinalysis. Laboratory test groups of clinical interest included hematology, serum chemistry, and urinalysis. Participants must have had a non-missing measurement in the DBT phase to be included for a given parameter.

Number of Participants With Hepatic-related AEs and Hepatic-related AEs Leading to Discontinuation During the OLE PhaseOLE Phase (Weeks 13 through 64)

Hepatic AEs were defined as all preferred terms in the OLE phase under the "Hepatic Disorders" SMQ, except those preferred terms in the "Congenital, Familial, Neonatal and Genetic Disorders of the Liver" SMQ.

Frequency of Use of Rescue Medication Days Per Month in the Last Month of the DBT PhaseWeeks 9 to 12 of the DBT phase

A rescue medication day was a day on which the participant took triptan, ergotamine, or other permitted medication to acutely treat headache or aura. Months were defined as 28-day intervals.

Number of Participants With Clinically Significant Laboratory Abnormalities in the OLE PhaseOLE Phase (Weeks 13 through 64)

Clinically significant laboratory abnormalities were defined as Grade 3 to 4 laboratory test results according to numeric laboratory test criteria found in CTCAE Version 5.0 (2017) if available; otherwise, according to DAIDS Table for Grading the Severity of Adult and Pediatric Adverse Events Corrected Version 2.1 (2017) for glucose, LDL-cholesterol, uric acid, and urinalysis. Laboratory test groups of clinical interest included hematology, serum chemistry, and urinalysis. Participants must have had a non-missing measurement in the OLE phase to be included for a given parameter.

Number of Participants With Elevations of AST or ALT > 3 x Upper Limit of Normal (ULN) Concurrent With Total Bilirubin (TBL) > 2 x ULN During the DBT PhaseWeeks 1 to 12 of the DBT phase

Elevations of AST or ALT \> 3 x ULN concurrent with TBL \> 2 x ULN were defined as elevations on the same collection date. Participants must have had a non-missing AST, ALT, or TBL measurement in the OLE phase to be included.

Change From Baseline in the Mean Number of Total Migraine Days Per Month in the First Month of the DBT PhaseOP and Weeks 1 to 4 of the DBT phase

A migraine day was any calendar day in which the participant experienced a qualified migraine headache (as previously described). If the participant took a migraine-specific medication during aura or to treat headache on a calendar day, it was counted as a migraine day regardless of the duration and pain features/associated symptoms. Months were defined as 28-day intervals.

The change from baseline was calculated as the number of monthly migraine days during the first 4 weeks of the DBT phase (Weeks 1 to 4) minus the number of monthly migraine days during the OP.

Number of Participants With Adverse Events (AEs), Serious AEs (SAEs), AEs Leading to Study Drug Discontinuation in the DBT PhaseWeeks 1 to 12 of the DBT phase

An AE was defined as any new untoward medical occurrence or worsening of a pre-existing medical condition on-treatment in a patient or clinical investigation participant administered an investigational (medicinal) product and that did not necessarily have a causal relationship with this treatment. An SAE was defined as any event that met any of the following criteria: death; life-threatening; inpatient hospitalization or prolongation of existing hospitalization; persistent or significant disability/incapacity; congenital anomaly/birth defect in the offspring of a participant who received rimegepant; other important medical events that may not have resulted in death, be life-threatening, or required hospitalization, based upon appropriate medical judgment, they may have jeopardized the participant and may have required medical or surgical intervention.

Percentage of Participants With Elevations of AST or ALT > 3 x ULN Concurrent With TBL > 2 x ULN During the OLE PhaseOLE Phase (Weeks 13 through 64)

Elevations of AST or ALT \> 3 x ULN concurrent with TBL \> 2 x ULN were defined as elevations on the same collection date. Participants must have had a non-missing AST, ALT, or TBL measurement in the DBT phase to be included.

Mean Change From Baseline in the Migraine Disability Assessment (MIDAS) Total Score at Week 12 of the DBT PhaseBaseline, Week 12 of the DBT Phase

The Migraine Disability Assessment (MIDAS) is a retrospective, self-administered, 5-item questionnaire that measures headache-related disability as lost time due to headache from paid work or school, household work, and non-work activities. Participants provide the number of missed work or school days; missed household chores days; missed social or leisure activity days; and days at work or school, and separately at home, where productivity was reduced by half or more in the last 3 months (scale: 0 - 90 for each of 5 subscales). The 5 subscale scores are summed to compute the MIDAS total score (scale: 0 - 450). Lower scores indicate less headache-related disability.

The change from baseline was calculated as the MIDAS total score at Week 12 of the DBT phase minus the MIDAS total score at baseline.

Number of Participants With Hepatic-related AEs and Hepatic-related AEs Leading to Discontinuation During the DBT PhaseWeeks 1 to 12 of the DBT phase

Hepatic AEs were defined as all preferred terms in the DBT phase under the "Hepatic Disorders" Standardized Medical Dictionary (Version 21.1) for Regulatory Activities Query (SMQ), except those preferred terms in the "Congenital, Familial, Neonatal and Genetic Disorders of the Liver" SMQ.

Mean Change From Baseline in the Migraine Specific Quality of Life (MSQoL) Role Function-Restrictive Domain Score at Week 12 of the DBT PhaseBaseline, Week 12 of the DBT Phase

The Migraine Specific Quality of Life (MSQoL) is a self-administered, 14-item instrument that has been validated in 3 domains: role restriction, role prevention, and the emotional function. The role function-restrictive domain consists of 7 items that describe how migraine limits one's daily social and work-related activities. Participants respond to items using a 6-point scale: "none of the time," "a little bit of the time," "some of the time," "a good bit of the time," "most of the time," and "all of the time," which are assigned scores of 1 to 6, respectively. Item scores are recoded using (7 - original score). Next, raw dimension scores are computed as a sum of recoded item scores and rescaled from a 0 to 100 scale such that higher scores indicate better quality of life.

The change from baseline was calculated as the MSQoL restrictive role function domain score at Week 12 of the DBT phase minus the MSQoL restrictive role function domain score at baseline.

Trial Locations

Locations (87)

Cedar Crosse Research Center

🇺🇸

Chicago, Illinois, United States

Oklahoma Headache Center

🇺🇸

Norman, Oklahoma, United States

Clinical Investigation Specialists, Inc.

🇺🇸

Kenosha, Wisconsin, United States

MDFirst Research-Chandler

🇺🇸

Chandler, Arizona, United States

Multi-Specialty Research Associates, Inc.

🇺🇸

Lake City, Florida, United States

Hassman Research Institute

🇺🇸

Berlin, New Jersey, United States

OnSite Clinical Solutions

🇺🇸

Dillon, South Carolina, United States

Texas Center for Drug Development, Inc.

🇺🇸

Houston, Texas, United States

Qps Mra, Llc

🇺🇸

Miami, Florida, United States

AppleMed Research Group, LLC

🇺🇸

Miami, Florida, United States

Family Medicine Specialists/CIS

🇺🇸

Wauconda, Illinois, United States

Community Clinical Research Center

🇺🇸

Anderson, Indiana, United States

PMG Research

🇺🇸

Raleigh, North Carolina, United States

Hometown Urgent Care

🇺🇸

Cincinnati, Ohio, United States

North Texas Institute of Neurology & Headache

🇺🇸

Frisco, Texas, United States

Victorium Clinical Research

🇺🇸

San Antonio, Texas, United States

Optimus Medical Group

🇺🇸

San Francisco, California, United States

Wasatch Clinical Research, LLC

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Salt Lake City, Utah, United States

Heartland Research Associates, LLC

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Wichita, Kansas, United States

Lillestol Research LLC

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Fargo, North Dakota, United States

Northwest Clinical Trials, Inc

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Boise, Idaho, United States

Axiom Research, LLC

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Colton, California, United States

Summit Research Network (Oregon) Inc.

🇺🇸

Portland, Oregon, United States

Michigan Head Pain & Neurological Institute

🇺🇸

Ann Arbor, Michigan, United States

JSV Clinical Research Study Inc.

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Tampa, Florida, United States

MedPharmics, LLC

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Biloxi, Mississippi, United States

Tucson Neuroscience Research

🇺🇸

Tucson, Arizona, United States

eStudySite

🇺🇸

La Mesa, California, United States

Baptist Health Center for Clinical Research

🇺🇸

Little Rock, Arkansas, United States

Anaheim Clinical Trials

🇺🇸

Anaheim, California, United States

Synergy San Diego

🇺🇸

Lemon Grove, California, United States

Pacific Research Partners, LLC

🇺🇸

Oakland, California, United States

Collaborative Neuroscience Network, LLC

🇺🇸

Long Beach, California, United States

Artemis Institute for Clinical Research

🇺🇸

San Marcos, California, United States

Ki Health Partners, LLC, dba New England Institute for Clinical Research

🇺🇸

Stamford, Connecticut, United States

California Neuroscience Research Medical Group

🇺🇸

Sherman Oaks, California, United States

Riverside Clinical Research

🇺🇸

Edgewater, Florida, United States

Galiz Research

🇺🇸

Hialeah, Florida, United States

Harmony Clinical Research

🇺🇸

North Miami Beach, Florida, United States

Ormond Medical Arts Pharmaceutical Research Center

🇺🇸

Ormond Beach, Florida, United States

Premiere Research Institute

🇺🇸

West Palm Beach, Florida, United States

iResearch Atlanta, LLC

🇺🇸

Decatur, Georgia, United States

R&R Clinical Research

🇺🇸

Idaho Falls, Idaho, United States

Crescent City Headache and Neurology Center

🇺🇸

Chalmette, Louisiana, United States

Phoenix Medical Research

🇺🇸

Prairie Village, Kansas, United States

Boston Clinical Trials

🇺🇸

Boston, Massachusetts, United States

ActivMed Practices & Research, Inc.

🇺🇸

Methuen, Massachusetts, United States

Regeneris Medical

🇺🇸

North Attleboro, Massachusetts, United States

Michigan Pain Consultants

🇺🇸

Grand Rapids, Michigan, United States

Clinical Research Professionals, Inc.

🇺🇸

Chesterfield, Missouri, United States

StudyMetrix Research

🇺🇸

Saint Peters, Missouri, United States

Sundance Clinical Research, LLC

🇺🇸

Saint Louis, Missouri, United States

Meridian Clinical Research, LLC

🇺🇸

Norfolk, Nebraska, United States

Albuquerque Neuroscience, Inc.

🇺🇸

Albuquerque, New Mexico, United States

Quality Clinical Research, Inc

🇺🇸

Omaha, Nebraska, United States

Nevada Headache Institute

🇺🇸

Las Vegas, Nevada, United States

Mid Hudson Medical Research, PLLC

🇺🇸

New Windsor, New York, United States

PharmQuest, LLC

🇺🇸

Greensboro, North Carolina, United States

Hometown Urgent Care and Research

🇺🇸

Dayton, Ohio, United States

Neurology Diagnostics Research

🇺🇸

Dayton, Ohio, United States

Aventiv Research, Inc

🇺🇸

Dublin, Ohio, United States

Clinical Research of Philadelphia, LLC

🇺🇸

Philadelphia, Pennsylvania, United States

Oregon Center for Clinical Investigations, Inc. (OCCI, Inc.)

🇺🇸

Salem, Oregon, United States

Coastal Carolina Research Center

🇺🇸

Mount Pleasant, South Carolina, United States

BTC of Lincoln, LLC

🇺🇸

Lincoln, Rhode Island, United States

Volunteer Research Group

🇺🇸

Knoxville, Tennessee, United States

Meridian Clinical Research

🇺🇸

Dakota Dunes, South Dakota, United States

FutureSearch Trials of Dallas, LP

🇺🇸

Dallas, Texas, United States

Ventavia Research Group, LLC

🇺🇸

Fort Worth, Texas, United States

Red Star Research, LLC

🇺🇸

Lake Jackson, Texas, United States

DM Clinical Research

🇺🇸

Tomball, Texas, United States

Charlottesville Medical Research

🇺🇸

Charlottesville, Virginia, United States

FMC Science

🇺🇸

Lampasas, Texas, United States

Tidewater Integrated Medical Research

🇺🇸

Virginia Beach, Virginia, United States

Seattle Women's

🇺🇸

Seattle, Washington, United States

MedStar Georgetown Headache - Georgetown University

🇺🇸

McLean, Virginia, United States

Northwest Clinical Research Center

🇺🇸

Bellevue, Washington, United States

Neurological Research Institute

🇺🇸

Santa Monica, California, United States

Clinvest Research LLC

🇺🇸

Springfield, Missouri, United States

New Orleans Center for Clinical Research

🇺🇸

New Orleans, Louisiana, United States

DelRicht Research

🇺🇸

New Orleans, Louisiana, United States

The Center for Pharmaceutical Research, LLC

🇺🇸

Kansas City, Missouri, United States

Tekton Research

🇺🇸

Austin, Texas, United States

Central New York Clinical Research

🇺🇸

Manlius, New York, United States

Island Neurological, A Division of Prohealth Care Associates, LLP

🇺🇸

Plainview, New York, United States

Upstate Clinical Research Associates, LLC

🇺🇸

Williamsville, New York, United States

Carolina Research Institute Center, Inc.

🇺🇸

Shelby, North Carolina, United States

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