MedPath

An Investigation of the Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of GSK2245035 in Healthy Volunteers and Allergic Rhinitics.

Phase 1
Completed
Conditions
Rhinitis, Allergic, Seasonal
Interventions
Drug: 20ng GSK2445053
Drug: Placebo
Drug: 400ng GSK2445053
Drug: 100ng GSK2445053
Drug: 1000ng GSK2445053
Drug: 4000ng GSK2445053
Drug: 200ng GSK2445053
Drug: 2000ng GSK2445053
Registration Number
NCT01480271
Lead Sponsor
GlaxoSmithKline
Brief Summary

GSK2245035 is a highly selective Toll-like Receptor 7(TLR7) agonist capable of preferentially inducing the production of interferon alpha (IFNα) versus tumor necrosis factor alpha (TNFα). The aim of this FTIH study is to collect tolerability, pharmacokinetic (PK) and pharmacodynamic (PD) information to enable the identification of appropriate safe doses of intranasal (i.n) GSK2245035, associated with up-regulation of TLR7-mediated genes in the nasal milieu, for use in subsequent clinical drug development studies. There will be two parts to the study: Healthy Volunteers will be dosed in escalating single doses in Part 1, followed by Allergic Rhinitis (AR) subjects dosed similarly in Part 2.

Detailed Description

This is a First Time in Human (FTIH) study to investigate the safety, tolerability, pharmacokinetics (PK) and pharmacodynamics (PD) of single, escalating doses of intranasal (i.n.) GSK2245035 in healthy male volunteers (HVT) and male subjects with allergic rhinitis (AR). The safety and tolerability of single i.n. GSK2245035 dosing will be assessed and established in HVT before the initiation of evaluation in AR.

GSK2245035 is a highly selective Toll-like Receptor 7 (TLR7) agonist capable of preferentially inducing the production of IFNα rather than TNFα. Activation of TLR7 is known to result in upregulation of co-stimulatory signals on antigen-presenting cells and in generation of pro-inflammatory mediators that can shift bystander immune responses towards a Helper T-cell Type 1/ Regulatory T cell (Th1/Treg) phenotype and therefore reduce the magnitude of Helper T-cell Type 2 (Th2) reactivity. In this context, it is proposed that i.n. GSK2245035 administration may alter the airways immune environment in a way that results in long-lasting control of AR symptoms and potentially disease remission through persistent modification of the underlying aberrant Th2 responsiveness to aeroallergens.

The aim of this study is to collect tolerability, PK and PD information to enable the identification of appropriate safe doses of i.n. GSK2245035, associated with up-regulation of TLR7-mediated genes in the nasal milieu, for use in subsequent clinical drug development studies. The study will be divided in to two parts. Part 1, involving only healthy volunteers, will consist of 8 cohorts receiving doses from 2 nanograms (2 ng) to 4000ng or a placebo dose. Administration within each cohort will be staggered so that two subjects (one receiving drug and one placebo) will be dosed and monitored for 24 hours before any subsequent doses.

Screening for part 2 of the study will begin once data from cohort 4 in part 1 has been found to be satisfactory. Part 2 will involve subjects with Allergic Rhinitis and be divided into three cohorts receiving doses between 20ng and 4000ng or a placebo dose.

Recruitment & Eligibility

Status
COMPLETED
Sex
Male
Target Recruitment
61
Inclusion Criteria

Not provided

Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
Part 1 Cohort 1 GSK24450532 ng GSK24450532ng GSK2245053
Part 1 Cohort 2 GSK244505320ng GSK244505320ng GSK2445053
Part 1 Cohort 4 PlaceboPlaceboPlacebo
Part 1 Cohort 3 PlaceboPlaceboPlacebo
Part 1 Cohort 2 PlaceboPlaceboPlacebo
Part 1 Cohort 1 PlaceboPlaceboPlacebo
Part 1 Cohort 5 GSK245053400ng GSK2445053400ng GSK2445053
Part 1 Cohort 3 GSK2245053100ng GSK2445053100ng GSK2445053
Part 1 Cohort 5 PlaceboPlaceboPlacebo
Part 1 Cohort 6 GSK24450531000ng GSK24450531000ng GSK2245053
Part 1 Cohort 7 PlaceboPlaceboPlacebo
Part 1 Cohort 8 GSK24450534000ng GSK24450534000ng GSK2445053
Part 1 Cohort 4 GSK2445053200ng GSK2445053200ng GSK2445053
Part 1 Cohort 6 PlaceboPlaceboPlacebo
Part 1 Cohort 7 GSK24450532000ng GSK24450532000ng GSK2445053
Part 1 Cohort 8 PlaceboPlaceboPlacebo
Primary Outcome Measures
NameTimeMethod
Nasal TolerabilityFrom screening until follow-up

Nasal examination and nasal symptom to assess nasal tolerability of single escalating doses of GSK2245035 in subjects with Allergic Rhinitis

TLR7-associated BiomarkersFrom pre-dose until 3 days post-dose

Evaluation of the induction of TLR7-induced blood biomarkers in the nasal lavage and nasal tissues of individuals with AR following single GSK2245035 administration versus placebo.

SafetyFrom screening until follow-up

General safety endpoints, including AEs, vital signs, 12-lead ECG, body temperature and clinical laboratory safety tests to evaluate the safety and nasal tolerability of single escalation doses of GSK2245035 in healthy volunteers and individuals with Allergic Rhinitis.

Secondary Outcome Measures
NameTimeMethod
Correlation EvaluationFrom pre-dose until 3 days post-dose

To evaluate the correlation between GSK2245035 dose - systemic PK - PD blood biomarkers - PD nasal biomarkers in healthy volunteer and subjects with Allergic Rhinitis.

Systemic PKFrom pre-dose until 3 days post-dose

Standard single dose derived plasma PK parameters for GSK2245035 in healthy volunteers and individuals with Allergic Rhinitis

Trial Locations

Locations (1)

GSK Investigational Site

🇳🇱

Zuidlaren, Netherlands

© Copyright 2025. All Rights Reserved by MedPath