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A Companion Sample Collection Protocol to Support the Discovery of Breast Cancer Aberrations With Treatment of CDK4/6 Therapy/LEE011/Ribociclib

Phase 3
Terminated
Conditions
Breast Cancer
Interventions
Registration Number
NCT03050398
Lead Sponsor
Novartis Pharmaceuticals
Brief Summary

This study was a companion study to CLEE011A2404 which provided the opportunity for the collection of tumor tissue samples to better understand relevant mutations and the mechanisms responsible for resistance to treatment.

Detailed Description

This was a multicenter, non-treatment based companion sample collection protocol conducted in the US only. This protocol sought to evaluate the aberrations of common pathways for newly diagnosed HR+/HER2- advanced breast cancer tumors and responses to ribociclib in diverse patient populations. This companion sample collection protocol was available for all US patients enrolled on CLEE011A2404 (CompLEEment-1) and did not alter the planned treatment. Tumor collection required for this study occurred at two time points: at baseline/screening and upon the development of progressive disease as shown in the protocol. Patients eligible for this companion study were required to sign an optional additional consent form at the time of enrolling into the core trial.

After eight patients had consented and samples had been taken, it was determined that the companion study protocol had not been properly initiated or monitored at the sites. This was determined to be a significant GCP violation and the clinical team made the decision to terminate the trial. In addition to the GCP issues, enrollment had been closed to the core study so enrolling additional patients was no longer possible. The limited number of samples would not provide any meaningful analysis. The samples were never analyzed. The study was not terminated due to safety or efficacy concerns. Samples collected were either destroyed or will be retained for up to 15 years based upon the decision of the patient.

Recruitment & Eligibility

Status
TERMINATED
Sex
All
Target Recruitment
8
Inclusion Criteria
  • Written informed consent was to have been obtained prior to any baseline/screening procedures.
  • Patients eligible for this companion sample collection protocol sample collection protocol must have met all inclusion in CLEE011A2404.
Exclusion Criteria
  • Patients eligible for this companion sample collection protocol must not have met any of the exclusion criteria in the CLEE011A2404 study, in addition to the following:
  • Patients without either fresh or archival tumor tissue accessible.

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
ribociclib + letrozoleRibociclibribociclib with letrozole per the core study
ribociclib + letrozoleletrozoleribociclib with letrozole per the core study
Primary Outcome Measures
NameTimeMethod
Identify Mutations of Genes From Tissue Samples Between Baseline and Time to Progression to Determine Modes of Resistance to Ribociclib After Disease ProgressionBaseline, time of progression approximately 24 months

Mutations of genes that were relevant to HR+ and the CDK4/6 pathway such as but not limited to CCND1, CDKN2A, PIK3CA and PTEN to identify the potential mechanisms of progression.

Secondary Outcome Measures
NameTimeMethod
Compare the Differences in Mutations Across Various Races / Ethnicities Based on Baseline SamplesBaseline, time of progression approximately 24 months

Change in mutations would have been assessed based on baseline samples and compared across diverse races/ethnicities with HR+ HER2- advanced breast cancer - specifically Caucasian, African America, Hispanic, Native American and Pacific Islander.

Trial Locations

Locations (6)

PeaceHealth St Joseph Medical Center

🇺🇸

Bellingham, Washington, United States

Arizona Oncology Associates PC HAL

🇺🇸

Sedona, Arizona, United States

Oncology Speciialists of Charlotte

🇺🇸

Charlotte, North Carolina, United States

Pacific Shores Medical Group SC

🇺🇸

Long Beach, California, United States

McLeod Center for Cancer Treatment and Research

🇺🇸

Florence, South Carolina, United States

Carolina Blood and Cancer Care of South Carolina

🇺🇸

Rock Hill, South Carolina, United States

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