MedPath

A Study to Evaluate Efficacy and Safety of Bitopertin in Participants With Persistent, Predominant Negative Symptoms of Schizophrenia

Phase 3
Completed
Conditions
Schizophrenia
Interventions
Drug: Placebo
Drug: Antipsychotics
Registration Number
NCT01192880
Lead Sponsor
Hoffmann-La Roche
Brief Summary

This Phase 3, multi-center, randomized, double blind, parallel-group, placebo-controlled study will evaluate the efficacy and safety of RO4917838 (bitopertin) in participants with persistent, predominant negative symptoms of schizophrenia. Participants, on stable treatment with antipsychotics, will be randomized to receive daily oral doses of RO4917838 or matching placebo for 52 weeks, followed by an optional treatment extension for up to 3 years.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
625
Inclusion Criteria
  • Based on the screening Structured Clinical Interview for and Statistical Manual of Mental Disorders, 4th Edition (DSM IV) - Clinical Trial (SCID CT), a DSM-IV- Text Revision (DSM-IV-TR) diagnosis of schizophrenia, paranoid, disorganized, residual, undifferentiated or catatonic subtype
  • A score of 40 or greater on the sum of the 14 PANSS negative and disorganized thought factor items (items scored 1-7 for a maximum possible score of 98)
  • A score of 22 or less on the sum of the 8 PANSS positive symptom factor items. The score of the items of P1 (delusions), P3 (hallucinatory behavior), P6 (suspiciousness) and G9 (unusual thought content) meet the following requirements: no more than 2 of the above items have a score of 4; all of the above items score less than 5
  • Clinical stability for 6 months prior to randomization as well as antipsychotic treatment stability for the past 8 weeks at the time of randomization
  • Are at least moderately ill, as defined by Clinical Global Impression - Severity (CGI S) of negative symptoms score more than or equal to (>/=) 4
  • Stable doses of anticholinergic, antidepressive medication for at least 8 weeks prior to randomization is allowed as long as the respective scales cut-off entry criteria are met
  • With the exception of clozapine, participants are on any of the available marketed atypical or typical antipsychotics (treatment with a maximum of 2 antipsychotics)
  • Have a caregiver considered reliable by the investigator
  • Female participants who are not either surgically sterile or post-menopausal must agree to use at least one effective forms of contraception from agree to remain sexually abstinent from screening until 90 days after the completion of the study medication
Exclusion Criteria
  • Evidence that participant has clinically significant, uncontrolled and unstable disorder (for example, cardiovascular, renal, hepatic disorder)
  • Body Mass Index (BMI) of less than (<) 17 or more than (>) 40 kilograms per meter square (kg/m^2)
  • Depressive symptoms, defined as a score of 9 or greater on the Calgary Depression Rating Scale for Schizophrenia (CDSS)
  • A severity score of >/=3 on the Parkinsonism item of the Extrapyramidal Symptoms Rating Scale - Abbreviated (ESRS-A) (Clinical Global Impression, Parkinsonism)
  • Positive result on the serum pregnancy test or are breast feeding at screening, or intend to become pregnant during the course of the trial.
  • History of neuroleptic malignant syndrome (NMS)
  • Based on the DSM-IV-TR criteria and screening SCID-CT have: other current DSM-IV-TR Axis I diagnosis; alcohol or substance dependence within 12 months or abuse within 3 months with the exception of nicotine; dementia, delirium and other amnestic disorder per DSM-IV-TR
  • Treated with electroconvulsive therapy (ECT) within 6 months prior to randomization
  • Ever received RO4917838 or another glycine transporter 1 (GLYT 1) inhibitor
  • Require high doses of benzodiazepines (> 4 mg per day lorazepam or equivalent)
  • Have a positive urine drug screen for amphetamines (including 3,4-Methylenedioxymethamphetamine [MDMA]/ecstasy), cocaine, barbiturate, cannabis and/or opiates

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Bitopertin 10 mg + AntipsychoticsAntipsychoticsTreatment Period 1: Participants will receive bitopertin 10 milligrams (mg) tablet orally once daily for 24 weeks. Treatment Period 2: Participants will receive bitopertin 10 mg tablet orally once daily for 28 weeks (up to Study Week 52). After Week 52 there will be a 4-week washout period for at least 50 percent (%) of participants (up to Week 56). Long-Term Extension: After Week 56, participants will enter the long term extension period and continue to receive bitopertin 10 mg tablet orally once daily up to 3 years. In addition, throughout the study, participants will continue their same stable antipsychotic treatment as they were receiving prior to entry in the study.
PlaceboAntipsychoticsTreatment Period 1: Participants will receive bitopertin matching placebo tablet orally once daily for 24 weeks. Treatment Period 2: Participants will receive bitopertin matching placebo tablet orally once daily for 32 weeks (up to Study Week 56). Long-Term Extension: After Week 56, participants will enter the long term extension period and will be switched to (in blinded manner) bitopertin 10 mg tablet orally once daily up to 3 years. In addition, throughout the study, participants will continue their same stable antipsychotic treatment as they were receiving prior to entry in the study.
Bitopertin 20 mg + AntipsychoticsAntipsychoticsTreatment Period 1: Participants will receive bitopertin 20 mg tablet orally once daily for 24 weeks. Treatment Period 2: Participants will receive bitopertin 20 mg tablet orally once daily for 28 weeks (up to Study Week 52). After Week 52 there will be a 4-week washout period for at least 50% of participants (up to Week 56). Long-Term Extension: After Week 56, participants will enter the long term extension period and continue to receive bitopertin 20 mg tablet orally once daily up to 3 years. In addition, throughout the study, participants will continue their same stable antipsychotic treatment as they were receiving prior to entry in the study.
PlaceboPlaceboTreatment Period 1: Participants will receive bitopertin matching placebo tablet orally once daily for 24 weeks. Treatment Period 2: Participants will receive bitopertin matching placebo tablet orally once daily for 32 weeks (up to Study Week 56). Long-Term Extension: After Week 56, participants will enter the long term extension period and will be switched to (in blinded manner) bitopertin 10 mg tablet orally once daily up to 3 years. In addition, throughout the study, participants will continue their same stable antipsychotic treatment as they were receiving prior to entry in the study.
Bitopertin 10 mg + AntipsychoticsBitopertinTreatment Period 1: Participants will receive bitopertin 10 milligrams (mg) tablet orally once daily for 24 weeks. Treatment Period 2: Participants will receive bitopertin 10 mg tablet orally once daily for 28 weeks (up to Study Week 52). After Week 52 there will be a 4-week washout period for at least 50 percent (%) of participants (up to Week 56). Long-Term Extension: After Week 56, participants will enter the long term extension period and continue to receive bitopertin 10 mg tablet orally once daily up to 3 years. In addition, throughout the study, participants will continue their same stable antipsychotic treatment as they were receiving prior to entry in the study.
Bitopertin 20 mg + AntipsychoticsBitopertinTreatment Period 1: Participants will receive bitopertin 20 mg tablet orally once daily for 24 weeks. Treatment Period 2: Participants will receive bitopertin 20 mg tablet orally once daily for 28 weeks (up to Study Week 52). After Week 52 there will be a 4-week washout period for at least 50% of participants (up to Week 56). Long-Term Extension: After Week 56, participants will enter the long term extension period and continue to receive bitopertin 20 mg tablet orally once daily up to 3 years. In addition, throughout the study, participants will continue their same stable antipsychotic treatment as they were receiving prior to entry in the study.
Primary Outcome Measures
NameTimeMethod
Mean Change From Baseline in the Positive and Negative Syndrome Scale (PANSS) Negative Symptom Factor Score at Week 24Baseline, Week 24
Percentage of Participants with Adverse EventsFrom baseline up to 24 weeks
Secondary Outcome Measures
NameTimeMethod
Mean Change from Baseline in the PANSS Total Score at Week 24Baseline, Week 24
Mean Change from Baseline in the PANSS Subscale Scores at Week 24Baseline, Week 24
Mean Change from Baseline in the PANSS Factor Scores at Week 24Baseline, Week 24
Mean Change from Baseline in the Personal and Social Performance (PSP) Total Score at Week 24Baseline, Week 24
Percentage of Participants with Response, as Assessed by CGI-I Overall and Negative Symptoms Rating ScoreWeek 24
Percentage of Participants With Response, as Assessed by PANSS Negative Symptom Factor ScoreWeek 24
Percentage of Participants with Both At Least 20% Improvement from Baseline in the PANSS Negative Symptom Factor Score and with a CGI-I Negative Symptoms Rating of Either Much or Very Much ImprovementWeek 24
Mean Change from Baseline in the CGI-S Overall and Negative Symptoms Rating ScoreBaseline, Week 24

Trial Locations

Locations (103)

Synergy Clinical Research of Escondido

🇺🇸

Escondido, California, United States

Excell Research

🇺🇸

Oceanside, California, United States

Behavioral Clinical Research Inc.

🇺🇸

Lauderhill, Florida, United States

Artemis Institute for Clinical Research, LLC

🇺🇸

San Diego, California, United States

Collaborative Neuroscience Network Inc.

🇺🇸

Torrance, California, United States

University of Miami Miller School of Medicine

🇺🇸

Miami, Florida, United States

Atlanta Center For Medical Research

🇺🇸

Atlanta, Georgia, United States

Medical Research Group of Central Florida

🇺🇸

Orange City, Florida, United States

Berma Research Group

🇺🇸

Plantation, Florida, United States

Indiana University; LaRue Carter Memorial Hospital-Research Unit

🇺🇸

Indianapolis, Indiana, United States

Clinical Insights, Inc.

🇺🇸

Glen Burnie, Maryland, United States

Ocean Rheumatology

🇺🇸

Toms River, New Jersey, United States

State University of New York at Buffalo; Department of Psychiatry

🇺🇸

Buffalo, New York, United States

Finger Lakes Clinical Research

🇺🇸

Rochester, New York, United States

Keystone Clinical Studies, LLC

🇺🇸

Norristown, Pennsylvania, United States

New York State Psychiatric Institute; Psychiatry Dept of Columbia University

🇺🇸

New York, New York, United States

Community Clinical Research Inc.

🇺🇸

Austin, Texas, United States

University Hills Clinical Research

🇺🇸

Irving, Texas, United States

Scranton Medical Institutes Llc.

🇺🇸

Scranton, Pennsylvania, United States

Eastside Therapeutic Resource

🇺🇸

Kirkland, Washington, United States

DDPDS Prof Dr Ivan Temkov EOOD

🇧🇬

Bourgas, Bulgaria

Lifetree Clinical Research

🇺🇸

Salt Lake City, Utah, United States

MHAT Dr.Hristo Stambolski EOOD; Psychiatry Ward of Acute Psychotic Disiorders in Severe Stage

🇧🇬

Kazanlak, Bulgaria

UMHAT Dr Georgi Stranski; EAD; Psychiatry

🇧🇬

Plovdiv, Bulgaria

State Psychiatric Hospital - Pazardzhik AD; Department for active treatment of men and for women

🇧🇬

Pazardzhik, Bulgaria

Beijing Huilongguan Hospital; Department of Psychiatric

🇨🇳

Beijing, China

Clinical Innovtions Inc

🇺🇸

Costa Mesa, California, United States

Azienda Ospedaliera Universitaria Federico II

🇮🇹

Napoli, Campania, Italy

The First Affilliated Hospital of Kunming Medical College

🇨🇳

Kunming, China

Saint Anne s.r.o.

🇨🇿

Brno, Czech Republic

Krajska nemocnice Liberec a.s.

🇨🇿

Liberec, Czech Republic

Psychiatricka ambulance

🇨🇿

Melnik, Czech Republic

Medical Services Prague s.r.o.

🇨🇿

Praha 6, Czech Republic

A-Shine s.r.o.

🇨🇿

Plzen, Czech Republic

Clintrial,s.r.o.

🇨🇿

Praha 10, Czech Republic

CTCenter MaVe s.r.o.

🇨🇿

Sternberk, Czech Republic

Azienda Ospedaliera di Padova

🇮🇹

Padova, Veneto, Italy

Kohnodai Hp., National Center for Global Health and Medicine

🇯🇵

Chiba, Japan

Koseikai Kusatsu Hospital

🇯🇵

Hiroshima-shi, Japan

Daiwakai Seimou Hospital

🇯🇵

Gunma, Japan

NHO Hizen Psychiatric Medical Center

🇯🇵

Kanzaki-gun, Japan

Fukkokai Soubu Hospital

🇯🇵

Funabashi-shi, Japan

Hokkaido University Hospital

🇯🇵

Hokkaido, Japan

NHO Higashiowari Hospital

🇯🇵

Nagoya-Shi, Japan

Sankeikai Nishigahara Hospital

🇯🇵

Kita-Ku, Japan

Jinseikai Hosogi Unity Hospital

🇯🇵

Kochi-shi, Japan

NHO Kikuchi National Hospital

🇯🇵

Koshi-shi, Japan

Hospital of the University of Occupational and Environmental Health,Japan

🇯🇵

Kitakyushu-shi, Japan

Shinkokai Shiranui Hospital

🇯🇵

Omuta-shi, Japan

Sawayamakai Teine Hospital

🇯🇵

Sapporo-shi, Japan

Asakayama General Hospital

🇯🇵

Sakai-shi, Japan

Tonankai Ashirbetsu Hospital

🇯🇵

Sapporo-shi, Japan

National Center Of Neurology And Psychiatry Hospital

🇯🇵

Tokyo, Japan

Tohoku Seishin Hokenkai Aoba Hospital

🇯🇵

Sendai-shi, Japan

Jisenkai Nanko Psychiatric Institute

🇯🇵

Shirakawa-shi, Japan

Tokyo Women's Medical University Hospital

🇯🇵

Tokyo, Japan

Yokohama Aihara Hospital

🇯🇵

Yokohama-shi, Japan

Deep Intention Hiyoshi Hospital

🇯🇵

Yokohama-shi, Japan

Institution of RAMS (Mental Health Research Center of RAMS); Psychopharmacology laboratory

🇷🇺

Moscow, Russian Federation

Kanagawa Prefectural Psychiatric Center Kinko Hospital

🇯🇵

Yokohama-shi, Japan

Kemerovo Regional Clinical Psychiatric Hospital

🇷🇺

Kemerovo, Russian Federation

GUZ Lipetsk Regional psychoneurological Hospital #1; Dispansary Department

🇷🇺

Lipetsk, Russian Federation

MHI City Clinical Hospital #2 named after V.I. Razumovsky; Psychiatric

🇷🇺

Sartatov, Russian Federation

Central Moscow Regional Clinical Psychiatric Hospital

🇷🇺

Moscow, Russian Federation

City Psychiatric Hospital #2 of St. Nikolay Chudotvorets

🇷🇺

St. Petersburg, Russian Federation

StP SR Psychoneurological Institute n.a.V.M.Bekhterev of MoH

🇷🇺

St. Petersburg, Russian Federation

Arkhangelsk Regional Clinical Psychiatric Hospital

🇷🇺

Talagi, Russian Federation

Hebei Mental Health Centre

🇨🇳

Baoding, China

The Second Xiangya Hospital of Central South University

🇨🇳

Changsha, China

West China Hospital, Sichuan University

🇨🇳

Chengdu, China

Guangzhou Brain Hospital

🇨🇳

GuangzhouGuangdong, China

The First Affiliated Hospital of College of Medicine, Zhejiang University(First Hospital of Zhejiang

🇨🇳

Hangzhou, China

The Second Affiliated Hospital of Zhejiang University College

🇨🇳

Hangzhou, China

Tongji Hospital of Tongji University

🇨🇳

Shanghai, China

Renmin Hospital of Wuhan University

🇨🇳

Wuhan, China

Wuxi Mental Health Center

🇨🇳

Wuxi, China

Peking University Sixth Hospital; Department of Psychiatry

🇨🇳

Beijing, China

Beijing An Ding Hosp.Capital Medical University; 5th Clinical Dept Depression Centre

🇨🇳

Beijing, China

Shanghai Mental Health Center

🇨🇳

Shanghai, China

The First Affiliated Hospital of The Fourth Military Medical University (Xijing Hospital)

🇨🇳

Xi'an, China

First Affiliated Hospital of Medical College of Xi'an Jiaotong University

🇨🇳

Xi'an, China

Xi'an Mental Health Center

🇨🇳

Xi'an, China

Asst Degli Spedali Civili Di Brescia; Servizio di farmacia

🇮🇹

Brescia, Lombardia, Italy

Clinica Mangiagalli

🇮🇹

Milano, Lombardia, Italy

ASST FATEBENEFRATELLI SACCO; Psichiatria (Fatebenefratelli)

🇮🇹

Milano, Lombardia, Italy

Azienda Ospedaliero Universitaria Molinette San Giovanni Bat

🇮🇹

Torino, Piemonte, Italy

Azienda Ospedaliero-Universitaria Consorziale Pol. di Bari; Neuroscienze e Organi di Senso

🇮🇹

Bari, Puglia, Italy

A.O. Universitaria Pisana; Psichiatria

🇮🇹

Pisa, Toscana, Italy

San Fernando Mental Health Center

🇺🇸

Granada Hills, California, United States

Psychiatricke Centrum Praha

🇨🇿

Praha 8 - Bohnice, Czech Republic

Fujita Health University Hospital

🇯🇵

Toyoake-shi, Japan

Duke University

🇺🇸

Durham, North Carolina, United States

State Psychiatric Hospital Dr. G. Kissiov; 3-d Women Ward 1-st Men Ward

🇧🇬

Radnevo, Bulgaria

Military Medical Academy- MHAT

🇧🇬

Sofia, Bulgaria

Precise Research Centers

🇺🇸

Flowood, Mississippi, United States

State Psychiatric Hospital Sv. Ivan Rilski Novi Iskar; First Man Dept. and First Woman Dept.

🇧🇬

Novi Iskar, Bulgaria

University of California San Diego

🇺🇸

La Jolla, California, United States

DDPDIU-Ruse; Men acute department Women acute department

🇧🇬

Rousse, Bulgaria

Yuge Hospital

🇯🇵

Kumamoto-shi, Japan

Jinkokai Kurayoshi Hospital

🇯🇵

Kurayoshi-shi, Japan

Korenkai Minamitoyama Nakagawa Hospital

🇯🇵

Toyama-shi, Japan

Altea Research Institute

🇺🇸

Las Vegas, Nevada, United States

Nanjing Brain Hospital

🇨🇳

Nanjing, China

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