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HORIZON: A Phase II Study to Evaluate the Safety and Efficacy of Two Doses of GT005

Phase 2
Terminated
Conditions
Dry Age-related Macular Degeneration
Registration Number
NCT04566445
Lead Sponsor
Gyroscope Therapeutics Limited
Brief Summary

The purpose of this clinical study is to evaluate the safety and efficacy of two doses of GT005 administered as a single subretinal injection in subjects with geographic atrophy secondary to age-related macular degeneration (AMD).

Detailed Description

This is a Phase 2, open-label, outcomes-assessor masked, multicentre, randomised, controlled study to evaluate the safety and efficacy of two doses of GT005 administered as a single subretinal injection in subjects with GA secondary to AMD.

The trial includes a screening period of up to 8 weeks and a 96-week study period.

Subjects will be randomised to one of two groups; GT005 or the untreated control group.

Recruitment & Eligibility

Status
TERMINATED
Sex
All
Target Recruitment
255
Inclusion Criteria
  1. Able and willing to give written informed consent
  2. Age β‰₯55 years
  3. a. In Stage 1: Have a clinical diagnosis of GA secondary to AMD in the study eye, as determined by the Investigator, and a diagnosis of AMD in the contralateral eye; b. In Stage 2: Have a clinical diagnosis of GA secondary to AMD in the study eye, as determined by the Investigator, that is non-foveal, as determined by the central reading centre, or has a CFI rare variant genotype and meets inclusion criteria 3a, and a diagnosis of AMD in the contralateral eye (except if monocular)
  4. GA lesion(s) within an acceptable size on FAF, in the study eye
  5. The GA lesion in the study eye must reside completely within the FAF image
  6. Up to 25% of the enrolled study population are permitted to have CNV in the fellow eye
  7. Have a BCVA of β‰₯24 letters (6/95 or 20/320 Snellen acuity equivalent), using ETDRS charts, in the study eye
  8. a. In Stage 1: Meet one of the pre-specified AMD genetic subgroup criteria; b. In Stage 2: Genotyping is not required for study eligibility
  9. Able to attend all study visits and complete the study procedures
  10. Women of child-bearing potential must have a negative pregnancy test within 2 weeks prior to randomisation (not required for postmenopausal women) or provide documentation of being surgically sterilised
Exclusion Criteria
  1. a. In Stage 1: Carriers of excluded genetic variants; b. In Stage 2: Subjects are excluded if they have a clinical diagnosis of Stargardt Disease or other retinal dystrophies
  2. Have a history, or evidence, of CNV in the study eye
  3. Presence of moderate/severe or worse non-proliferative, diabetic retinopathy in the study eye
  4. Have history of vitrectomy, sub-macular surgery, or macular photocoagulation in the study eye
  5. History of intraocular surgery in the study eye within 12 weeks prior to Visit 1
  6. Have clinically significant cataract that may require surgery during the study period in the study eye
  7. Presence of moderate to severe glaucomatous optic neuropathy, uncontrolled intraocular pressure (IOP), despite use of two or more topical agents; or a history of glaucoma-filtering or valve surgery
  8. Axial myopia of greater than -8 diopters in the study eye
  9. Have received any investigational product for the treatment of GA within the past 6 months or 5 half-lives (whichever is longer), other than nutritional supplements such as the age-related eye disease study (AREDS) formula
  10. Have received a gene or cell therapy at any time.
  11. Have a contraindication to the protocol specified corticosteroid regimen
  12. Are unwilling to use two forms of contraception (one of which being a barrier method) for 90 days post-dosing, if relevant
  13. Active malignancy within the past 12 months, except for appropriately treated carcinoma in situ of the cervix, non-melanoma skin carcinoma, or prostate cancer with a stable prostate-specific antigen (PSA) β‰₯ 12 months
  14. Have any other significant ocular or non-ocular medical or psychiatric condition which, in the opinion of the Investigator, may either put the subject at risk or may influence the results of the study

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Primary Outcome Measures
NameTimeMethod
Progression of geographic atrophy72 weeks

The change from baseline to Week 72 in GA area as measured by fundus autofluorescence (FAF)

Secondary Outcome Measures
NameTimeMethod
Progression of geographic atrophy96 weeks

The change from baseline through Week 96 in GA area as measured by fundus autofluorescence (FAF)

Evaluation of the effect of GT005 on retinal anatomical measures96 weeks

Change in retinal morphology on multimodal imaging

Evaluation of the effect of GT005 on functional measures96 weeks

Change in low luminance difference (LLD) via the ETDRS chart

Evaluation of the effect of GT005 on visual function96 weeks

Change in functional reading independence (FRI) index

Evaluation of the safety and tolerability of GT00596 weeks

Frequency of treatment emergent adverse events (AEs)

Evaluation of the effect of GT005 on patient-reported outcomes96 weeks

Change in quality of life measured on the Visual Function Questionnaire-25 (VFQ-25)

Trial Locations

Locations (62)

Retina Consultants of Houston

πŸ‡ΊπŸ‡Έ

The Woodlands, Texas, United States

Cleveland Clinic

πŸ‡ΊπŸ‡Έ

Cleveland, Ohio, United States

Retina Vitreous Associates Medical Group

πŸ‡ΊπŸ‡Έ

Beverly Hills, California, United States

Retina Consultants of Orange County

πŸ‡ΊπŸ‡Έ

Fullerton, California, United States

Northern California Retina Vitreous Associates

πŸ‡ΊπŸ‡Έ

Mountain View, California, United States

Byers Eye Institute at Stanford

πŸ‡ΊπŸ‡Έ

Palo Alto, California, United States

Retina Consultants of San Diego

πŸ‡ΊπŸ‡Έ

Poway, California, United States

University of California (UC) Davis Medical Group Eye Center

πŸ‡ΊπŸ‡Έ

Sacramento, California, United States

Rand Eye Institute

πŸ‡ΊπŸ‡Έ

Deerfield Beach, Florida, United States

Southwest Retina Research Center

πŸ‡ΊπŸ‡Έ

Durango, Colorado, United States

Bascom Palmer Eye Institute

πŸ‡ΊπŸ‡Έ

Miami, Florida, United States

VitreoRetinal Associates, P.A.

πŸ‡ΊπŸ‡Έ

Gainesville, Florida, United States

Retina Vitreous Associates of Florida

πŸ‡ΊπŸ‡Έ

Saint Petersburg, Florida, United States

Southeast Retina Center

πŸ‡ΊπŸ‡Έ

Augusta, Georgia, United States

Georgia Retina PC

πŸ‡ΊπŸ‡Έ

Marietta, Georgia, United States

University Retina Macula Associates PC

πŸ‡ΊπŸ‡Έ

Lemont, Illinois, United States

Retina Associates, LLC

πŸ‡ΊπŸ‡Έ

Shawnee Mission, Kansas, United States

Midwest Eye Institute Northside

πŸ‡ΊπŸ‡Έ

Indianapolis, Indiana, United States

The Retina Care Center

πŸ‡ΊπŸ‡Έ

Baltimore, Maryland, United States

Wolfe Eye Clinic

πŸ‡ΊπŸ‡Έ

West Des Moines, Iowa, United States

Retina Associates of Michigan

πŸ‡ΊπŸ‡Έ

Grand Blanc, Michigan, United States

Ophthalamic Consultants of Boston (OCB)

πŸ‡ΊπŸ‡Έ

Boston, Massachusetts, United States

Associated Retinal Consultants PC

πŸ‡ΊπŸ‡Έ

Royal Oak, Michigan, United States

Sierra Eye Associates

πŸ‡ΊπŸ‡Έ

Reno, Nevada, United States

Columbia University Medical Center

πŸ‡ΊπŸ‡Έ

New York, New York, United States

Retina Associates of Western New York

πŸ‡ΊπŸ‡Έ

Rochester, New York, United States

Duke Eye Center

πŸ‡ΊπŸ‡Έ

Durham, North Carolina, United States

Cincinnati Eye Institute

πŸ‡ΊπŸ‡Έ

Cincinnati, Ohio, United States

Oregon Retina

πŸ‡ΊπŸ‡Έ

Eugene, Oregon, United States

Mid Atlantic Retina - Wills Eye Hospital

πŸ‡ΊπŸ‡Έ

Philadelphia, Pennsylvania, United States

Erie Retinal Surgery ,INC

πŸ‡ΊπŸ‡Έ

Erie, Pennsylvania, United States

Southeastern Retina Associates, PC

πŸ‡ΊπŸ‡Έ

Knoxville, Tennessee, United States

Austin Research Center for Retina, PLLC

πŸ‡ΊπŸ‡Έ

Austin, Texas, United States

Retina Foundation of the Southwest

πŸ‡ΊπŸ‡Έ

Dallas, Texas, United States

Retina Consultants of Houston-TMC

πŸ‡ΊπŸ‡Έ

Bellaire, Texas, United States

Texas Retina Associates (Dallas)

πŸ‡ΊπŸ‡Έ

Dallas, Texas, United States

Retinal Consultants of San Antonio

πŸ‡ΊπŸ‡Έ

San Antonio, Texas, United States

Department of Ophthalmology UW Medicine

πŸ‡ΊπŸ‡Έ

Seattle, Washington, United States

Retina Center Northwest

πŸ‡ΊπŸ‡Έ

Silverdale, Washington, United States

CHU Dijon - Hopital Mitterrand

πŸ‡«πŸ‡·

Dijon, France

Centre Paradis Monticelli

πŸ‡«πŸ‡·

Marseille, France

Sydney Hospital and Sydney Eye Hospital

πŸ‡¦πŸ‡Ί

Sydney, New South Wales, Australia

CHU de Nantes - HΓ΄tel-Dieu

πŸ‡«πŸ‡·

Nantes, France

Internationale Innovative Ophthalmochirurgie

πŸ‡©πŸ‡ͺ

DΓΌsseldorf, Germany

UniversitΓ€tsklinikum Bonn

πŸ‡©πŸ‡ͺ

Bonn, Germany

Universitaetsklinikum Schleswig-Holstein - Campus LΓΌbeck

πŸ‡©πŸ‡ͺ

LΓΌbeck, Germany

Universitaetsklinikum Tuebingen

πŸ‡©πŸ‡ͺ

Tuebingen, Germany

Instituto de microcirugΓ­a ocular

πŸ‡ͺπŸ‡Έ

Barcelona, Spain

Clinica Baviera

πŸ‡ͺπŸ‡Έ

Madrid, Spain

Clinica Universidad de Navarra - Pamplona

πŸ‡ͺπŸ‡Έ

Pamplona, Spain

Moorfields Eye Hospital - NHS Foundation Trust

πŸ‡¬πŸ‡§

London, United Kingdom

John Radcliffe Hospital

πŸ‡¬πŸ‡§

Oxford, United Kingdom

Retina Clinic London

πŸ‡¬πŸ‡§

London, United Kingdom

Sunderland Eye Infirmary

πŸ‡¬πŸ‡§

Sunderland, United Kingdom

Rocky Mountain Retina Consultants

πŸ‡ΊπŸ‡Έ

Salt Lake City, Utah, United States

Palmetto Retina Center

πŸ‡ΊπŸ‡Έ

West Columbia, South Carolina, United States

Charles Retina Institute

πŸ‡ΊπŸ‡Έ

Germantown, Tennessee, United States

Illinois Retina Associates

πŸ‡ΊπŸ‡Έ

Chicago, Illinois, United States

Oftalmika Spolka z ograniczona odpowiedzialnoscia

πŸ‡΅πŸ‡±

Bydgoszcz, Poland

The University of Melbourne - The Centre for Eye Research Australia (CERA)

πŸ‡¦πŸ‡Ί

Melbourne E., Victoria, Australia

Retinal Research Institute (retina consultants of AZ)

πŸ‡ΊπŸ‡Έ

Phoenix, Arizona, United States

Casey Eye Institute - OHSU

πŸ‡ΊπŸ‡Έ

Portland, Oregon, United States

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