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Long Term Safety and Efficacy Study of ProSavin in Parkinson's Disease

Phase 1
Terminated
Conditions
Parkinson's Disease
Interventions
Registration Number
NCT01856439
Lead Sponsor
Axovant Sciences Ltd.
Brief Summary

The study is designed to assess the long term tolerability of ProSavin and whether it is safe and efficacious in patients administered ProSavin from the PS1/001/07 study .

Detailed Description

Not available

Recruitment & Eligibility

Status
TERMINATED
Sex
All
Target Recruitment
15
Inclusion Criteria
  • must have met all inclusion criteria for study PS1/001/07
  • willing to have L-DOPA dosage reduced/withdrawn at the discretion of the investigator at regular intervals to allow assessment of ProSavin in the absence of concomitant antiparkinsonian medication.
  • affiliated with the French social security health care system (Patients enrolled in France only)
  • signed and dated written informed consent obtained from the patient and/or the patient's legally acceptable representative, if applicable, in accordance with the local regulations
  • must have been treated with ProSavin/Sham
Exclusion Criteria

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
Long term follow upProSavinLong term follow up of patient's who received ProSavin in previous study
Primary Outcome Measures
NameTimeMethod
To assess the long term safety and tolerability of ProSavin10 years

The number and severity of any adverse event

Secondary Outcome Measures
NameTimeMethod
Patients' responses to ProSavin administration10 years

Assessed using Unified Parkinson's Disease Rating Score(UPDRS) Part III, evaluating percentage of time during waking day that patient is in the "off" state through patient diaries and activities of daily living using PDQ-39 at 36 months post administration.

Trial Locations

Locations (2)

Henri Mondor Hospital

🇫🇷

Paris, France

Addenbrookes Hospital

🇬🇧

Cambridge, United Kingdom

Henri Mondor Hospital
🇫🇷Paris, France

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