MedPath

A Descriptive Study of Baseline Characteristics, Clinical Outcomes, and Treatment Patterns of HR+/HER2- Advanced or Metastatic Breast Cancer Patients Treated With Alpelisib Plus Fulvestrant Who Have Received Fulvestrant in Any Prior Line of Therapy

Completed
Conditions
HR+/HER2- Advanced or Metastatic Breast Cancer
Registration Number
NCT05853432
Lead Sponsor
Novartis Pharmaceuticals
Brief Summary

This was a non-interventional, retrospective cohort study of patients with HR+/HER2- aBC treated with alpelisib (ALP) plus fulvestrant (FUL) who have received fulvestrant in any prior line of therapy (LoT). This study utilized de-identified individual patient data from the United States (US) ConcertAI Patient360 Breast Cancer database, sourced from electronic health records (EHR) (i.e., secondary use of data). Patients were indexed at their start date of the earliest alpelisib plus fulvestrant regimen and followed until their death date or last confirmed activity date in the absence of an observed death.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
157
Inclusion Criteria
  • Had a curated record for advanced or metastatic breast cancer diagnosis.
  • Note: Diagnosis of a/mBC is based on a curated record of M stage=M1, Stage 4/4a/4b, presence of metastatic tumor, Stage 3b/3c or presence of secondary neoplasm.
  • Had patient activity documented in ConcertAI Patient 360 Breast Cancer database (defined as a record of a clinic visit, medication administration, vital test, or lab test) or death within 90 days after the advanced or metastatic breast cancer diagnosis date.
  • Had documented receipt of treatment with alpelisib plus fulvestrant on or after the advanced or metastatic diagnosis date.
  • Had documented receipt of treatment with fulvestrant before the index date (start date of the earliest alpelisib plus fulvestrant regimen). This included (neo) adjuvant therapies.
  • Age ≥18 years on the index date.
Exclusion Criteria
  • Had documented hormone receptor-negative (defined as both estrogen receptor-negative and progesterone receptor-negative) or HER2-positive status any time prior to index date (but prioritizing results closest to index date, if there were conflicting results).
  • Patient had a clinical trial registration date (i.e., participated in a clinical trial) on or before the index date.
  • Patients with "negative" PIK3CA test before index date (in case of multiple tests, the one closer to the index date was used).

Study & Design

Study Type
OBSERVATIONAL
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Real-world progression-free survival (rwPFS)Up to approximately 21 months

rwPFS was defined as the length of time from the start date of the earliest alpelisib plus fulvestrant regimen to the first documented progression or death date occurring at least 14 days after the index date, or last adequate tumor assessment date in the absence of an observed progression or death event.

Line of treatment of ALP+FUL receivedBaseline
Line of treatment number of index regimens stratified by index yearBaseline
Starting dose of alpelisibBaseline
Number of prior fulvestrant regimens prior to alpelisib plus fulvestrantBaseline
Percentage of patients with prior exposure to chemotherapy in the metastatic settingBaseline
Prior fulvestrant treatment categoryBaseline
Prior regimens of patients who received alpelisib plus fulvestrant as first-line treatmentBaseline
Percentage of patients with prior exposure to CDK4/6i in the adjuvant settingBaseline
Time to treatment discontinuationUp to approximately 21 months
First antineoplastic regimen received after discontinuation of the alpelisib plus fulvestrant regimenUp to approximately 21 months
Number of prior regimensBaseline
Overall survival (OS)Up to approximately 21 months

OS was defined as the length of time from the start date of the earliest alpelisib plus fulvestrant regimen to the date of death, or last confirmed activity date in the absence of an observed death event.

Secondary Outcome Measures
NameTimeMethod
Percentage of patients with prior exposure to chemotherapy in the metastatic setting in subgroups of patients according to the prior lines of treatmentBaseline
Real-world progression-free survival (rwPFS) in subgroups of patients according to the prior lines of treatmentUp to approximately 21 months

rwPFS was defined as the length of time from the start date of the earliest alpelisib plus fulvestrant regimen to the first documented progression or death date occurring at least 14 days after the index date, or last adequate tumor assessment date in the absence of an observed progression or death event.

Overall survival (OS) in subgroups of patients according to the prior lines of treatmentUp to approximately 21 months

OS was defined as the length of time from the start date of the earliest alpelisib plus fulvestrant regimen to the date of death, or last confirmed activity date in the absence of an observed death event.

Line of treatment number of index regimens stratified by index year in subgroups of patients according to the prior lines of treatmentBaseline
Starting dose of alpelisib in subgroups of patients according to the prior lines of treatmentBaseline
Line of treatment of ALP+FUL received in subgroups of patients according to the prior lines of treatmentBaseline
Prior fulvestrant treatment category in subgroups of patients according to the prior lines of treatmentBaseline
Prior regimens of patients who received alpelisib plus fulvestrant as first-line treatment in subgroups of patients according to the prior lines of treatmentBaseline
Number of prior fulvestrant regimens prior to alpelisib plus fulvestrant in subgroups of patients according to the prior lines of treatmentBaseline
First antineoplastic regimen received after discontinuation of the alpelisib plus fulvestrant regimen in subgroups of patients according to the prior lines of treatmentUp to approximately 21 months
Percentage of patients with prior exposure to CDK4/6i in the adjuvant setting in subgroups of patients according to the prior lines of treatmentBaseline
Number of prior regimens in subgroups of patients according to the prior lines of treatmentBaseline
Time to treatment discontinuation in subgroups of patients according to the prior lines of treatmentUp to approximately 21 months

Trial Locations

Locations (1)

Novartis Pharmaceuticals

🇮🇪

Dublin, Ireland

© Copyright 2025. All Rights Reserved by MedPath