MedPath

Brain Function in Young Patients Receiving Methotrexate for Acute Lymphoblastic Leukemia

Completed
Conditions
Childhood T Acute Lymphoblastic Leukemia
Cognitive Side Effects of Cancer Therapy
Long-Term Effects Secondary to Cancer Therapy in Children
Psychological Impact of Cancer
Untreated Childhood Acute Lymphoblastic Leukemia
Childhood B Acute Lymphoblastic Leukemia
Neurotoxicity Syndrome
Interventions
Procedure: Cognitive Assessment
Procedure: Diffusion Tensor Imaging
Other: Laboratory Biomarker Analysis
Other: Pharmacological Study
Procedure: Psychosocial Assessment and Care
Registration Number
NCT00437060
Lead Sponsor
Children's Oncology Group
Brief Summary

This clinical trial is looking at brain function in young patients receiving methotrexate for acute lymphoblastic leukemia. Learning about the long-term effects of methotrexate on brain function may help doctors plan cancer treatment.

Detailed Description

OBJECTIVES:

I. Determine the neuropsychological function in children with acute lymphoblastic leukemia treated with either high-dose methotrexate or escalating-dose methotrexate in the absence of cranial radiation and nelarabine.

II. Identify host polymorphisms that predict an increased risk of neurocognitive dysfunction or acute neurotoxicity in these patients.

III. Correlate neuropsychological outcome measures and the occurrence of acute neurotoxicity with host polymorphisms in these patients.

IV. Measure concentrations of 5-methyltetrahydrofolate, homocysteine, Ado, S-adenosylmethionine, S-adenosylhomocysteine, and other potentially relevant compounds in serum and cerebrospinal fluid during interim maintenance therapy with low- or high-dose methotrexate regimens, respectively, and correlate these endpoints with the occurrence of acute neurologic toxicity and long-term neurocognitive dysfunction in these patients.

V. Determine whether or not diffusion tensor imaging will identify areas of selective vulnerability in CNS and provide an imaging modality that predicts and/or correlates with neuropsychological outcome.

OUTLINE: This is a prospective, cohort, multicenter study.

Patients complete neurocognitive tests to assess thinking, memory, attention, and concentration. The baseline test is administered during the consolidation phase of chemotherapy and further tests are done at 1 year from baseline and 1 year after\* the completion of study therapy.

Patients undergo blood and cerebrospinal fluid collection periodically for biomarker, genotypic polymorphisms, and pharmacokinetic analysis. Patients undergo MRI diffusion-tensor imaging to correlate imaging with neuropsychological outcomes.

NOTE: \* Within 8 months to 24 months after the completion of study therapy for patients on AALL0232.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
233
Inclusion Criteria
  • Diagnosis of acute lymphoblastic leukemia

  • Enrolled on COG-AALL0434 (Cohort #1 only) or COG-AALL0232 (Cohorts #1 and #2)

    • Patients must have received either high-dose methotrexate or escalating-dose methotrexate during interim maintenance.
  • No CNS-3 disease

  • Patients must enroll within 8-24 months after completion of therapy on COG-AALL0232 and no evidence of relapsed or secondary malignancy

  • No known significant neurodevelopmental disability unrelated to cancer diagnosis including, but not limited to, any of the following:

    • Down syndrome
    • Fragile X mental retardation
    • Autism
    • Pervasive developmental disability
    • Seizure disorder
  • Attention-deficit hyperactivity disorder or specific learning disability (e.g., dyslexia) allowed

  • No sensory impairment (e.g., pre-existing uncorrectable vision impairment or deafness)

  • No cranial radiation therapy

Exclusion Criteria

Not provided

Study & Design

Study Type
OBSERVATIONAL
Study Design
Not specified
Arm && Interventions
GroupInterventionDescription
Ancillary/Correlative (neurocognitive assessment, biomarkers))Laboratory Biomarker AnalysisPatients complete neurocognitive tests to assess thinking, memory, attention, and concentration. The baseline test is administered during the consolidation phase of chemotherapy and further tests are done at 1 year from baseline and 1 year after\* the completion of study therapy. Patients undergo blood and cerebrospinal fluid collection periodically for biomarker, genotypic polymorphisms, and pharmacokinetic analysis. Patients undergo MRI diffusion-tensor imaging to correlate imaging with neuropsychological outcomes.
Ancillary/Correlative (neurocognitive assessment, biomarkers))Diffusion Tensor ImagingPatients complete neurocognitive tests to assess thinking, memory, attention, and concentration. The baseline test is administered during the consolidation phase of chemotherapy and further tests are done at 1 year from baseline and 1 year after\* the completion of study therapy. Patients undergo blood and cerebrospinal fluid collection periodically for biomarker, genotypic polymorphisms, and pharmacokinetic analysis. Patients undergo MRI diffusion-tensor imaging to correlate imaging with neuropsychological outcomes.
Ancillary/Correlative (neurocognitive assessment, biomarkers))Pharmacological StudyPatients complete neurocognitive tests to assess thinking, memory, attention, and concentration. The baseline test is administered during the consolidation phase of chemotherapy and further tests are done at 1 year from baseline and 1 year after\* the completion of study therapy. Patients undergo blood and cerebrospinal fluid collection periodically for biomarker, genotypic polymorphisms, and pharmacokinetic analysis. Patients undergo MRI diffusion-tensor imaging to correlate imaging with neuropsychological outcomes.
Ancillary/Correlative (neurocognitive assessment, biomarkers))Cognitive AssessmentPatients complete neurocognitive tests to assess thinking, memory, attention, and concentration. The baseline test is administered during the consolidation phase of chemotherapy and further tests are done at 1 year from baseline and 1 year after\* the completion of study therapy. Patients undergo blood and cerebrospinal fluid collection periodically for biomarker, genotypic polymorphisms, and pharmacokinetic analysis. Patients undergo MRI diffusion-tensor imaging to correlate imaging with neuropsychological outcomes.
Ancillary/Correlative (neurocognitive assessment, biomarkers))Psychosocial Assessment and CarePatients complete neurocognitive tests to assess thinking, memory, attention, and concentration. The baseline test is administered during the consolidation phase of chemotherapy and further tests are done at 1 year from baseline and 1 year after\* the completion of study therapy. Patients undergo blood and cerebrospinal fluid collection periodically for biomarker, genotypic polymorphisms, and pharmacokinetic analysis. Patients undergo MRI diffusion-tensor imaging to correlate imaging with neuropsychological outcomes.
Primary Outcome Measures
NameTimeMethod
Polymorphisms as predictors of neurocognitive dysfunction or acute neurotoxicityUp to 24 months
Change in neurocognitive function by the Pediatric Quality of Life (PedQL) battery, Full Scale Intelligence Quotient (FSIQ) scoreFrom baseline to up to 24 months

Vocabulary and Block Design, subtests of the Wechsler Preschool and Primary Scale of Intelligence (WPPSI-III), Wechsler Children Intelligence Scale (WISC-IV) and Wechsler Adult Intelligence Scale (WAIS-III) (based on age) will be used to estimate FSIQ, using the tables provided by Sattler.

Secondary Outcome Measures
NameTimeMethod
Correlation between neuropsychological outcomes and acute neurotoxicityUp to 24 months

Trial Locations

Locations (111)

Children's Hospital Central California

🇺🇸

Madera, California, United States

Nationwide Children's Hospital

🇺🇸

Columbus, Ohio, United States

Children's Hospital of Philadelphia

🇺🇸

Philadelphia, Pennsylvania, United States

Driscoll Children's Hospital

🇺🇸

Corpus Christi, Texas, United States

UT Southwestern/Simmons Cancer Center-Dallas

🇺🇸

Dallas, Texas, United States

Royal Brisbane and Women's Hospital

🇦🇺

Herston, Queensland, Australia

Royal Children's Hospital-Brisbane

🇦🇺

Herston, Queensland, Australia

Hospital for Sick Children

🇨🇦

Toronto, Ontario, Canada

University of Illinois

🇺🇸

Chicago, Illinois, United States

Baylor College of Medicine

🇺🇸

Houston, Texas, United States

University of Miami Miller School of Medicine-Sylvester Cancer Center

🇺🇸

Miami, Florida, United States

Riley Hospital for Children

🇺🇸

Indianapolis, Indiana, United States

Rady Children's Hospital - San Diego

🇺🇸

San Diego, California, United States

Children's Hospitals and Clinics of Minnesota - Minneapolis

🇺🇸

Minneapolis, Minnesota, United States

University of Texas Health Science Center at San Antonio

🇺🇸

San Antonio, Texas, United States

University of Minnesota/Masonic Cancer Center

🇺🇸

Minneapolis, Minnesota, United States

Nevada Cancer Research Foundation CCOP

🇺🇸

Las Vegas, Nevada, United States

Duke University Medical Center

🇺🇸

Durham, North Carolina, United States

Methodist Children's Hospital of South Texas

🇺🇸

San Antonio, Texas, United States

Primary Children's Hospital

🇺🇸

Salt Lake City, Utah, United States

UCSF Medical Center-Parnassus

🇺🇸

San Francisco, California, United States

Vanderbilt University/Ingram Cancer Center

🇺🇸

Nashville, Tennessee, United States

Wayne State University/Karmanos Cancer Institute

🇺🇸

Detroit, Michigan, United States

Saint John Hospital and Medical Center

🇺🇸

Detroit, Michigan, United States

University of Alabama at Birmingham Cancer Center

🇺🇸

Birmingham, Alabama, United States

Children's Hospital of Alabama

🇺🇸

Birmingham, Alabama, United States

Legacy Emanuel Children's Hospital

🇺🇸

Portland, Oregon, United States

Legacy Emanuel Hospital and Health Center

🇺🇸

Portland, Oregon, United States

Oregon Health and Science University

🇺🇸

Portland, Oregon, United States

Children's Hospital Colorado

🇺🇸

Aurora, Colorado, United States

Saint Joseph's Hospital/Children's Hospital-Tampa

🇺🇸

Tampa, Florida, United States

Mayo Clinic

🇺🇸

Rochester, Minnesota, United States

Midwest Children's Cancer Center

🇺🇸

Milwaukee, Wisconsin, United States

CancerCare Manitoba

🇨🇦

Winnipeg, Manitoba, Canada

University of Missouri - Ellis Fischel

🇺🇸

Columbia, Missouri, United States

T C Thompson Children's Hospital

🇺🇸

Chattanooga, Tennessee, United States

Children's Hospital Medical Center of Akron

🇺🇸

Akron, Ohio, United States

State University of New York Upstate Medical University

🇺🇸

Syracuse, New York, United States

Nicklaus Children's Hospital

🇺🇸

Miami, Florida, United States

Yale University

🇺🇸

New Haven, Connecticut, United States

All Children's Hospital

🇺🇸

Saint Petersburg, Florida, United States

Nemours Children's Clinic-Jacksonville

🇺🇸

Jacksonville, Florida, United States

Broward Health Medical Center

🇺🇸

Fort Lauderdale, Florida, United States

Saint Mary's Hospital

🇺🇸

West Palm Beach, Florida, United States

Saint Vincent Hospital and Health Care Center

🇺🇸

Indianapolis, Indiana, United States

Children's National Medical Center

🇺🇸

Washington, D.C., District of Columbia, United States

Memorial Regional Hospital/Joe DiMaggio Children's Hospital

🇺🇸

Hollywood, Florida, United States

Blank Children's Hospital

🇺🇸

Des Moines, Iowa, United States

Advocate Children's Hospital-Oak Lawn

🇺🇸

Oak Lawn, Illinois, United States

Massachusetts General Hospital Cancer Center

🇺🇸

Boston, Massachusetts, United States

Children's Hospital of Orange County

🇺🇸

Orange, California, United States

Nemours Children's Clinic - Pensacola

🇺🇸

Pensacola, Florida, United States

Cook Children's Medical Center

🇺🇸

Fort Worth, Texas, United States

East Tennessee Childrens Hospital

🇺🇸

Knoxville, Tennessee, United States

Golisano Children's Hospital of Southwest Florida

🇺🇸

Fort Myers, Florida, United States

Helen DeVos Children's Hospital at Spectrum Health

🇺🇸

Grand Rapids, Michigan, United States

Morristown Medical Center

🇺🇸

Morristown, New Jersey, United States

Southern California Permanente Medical Group

🇺🇸

Downey, California, United States

Cedars-Sinai Medical Center

🇺🇸

Los Angeles, California, United States

Lurie Children's Hospital-Chicago

🇺🇸

Chicago, Illinois, United States

Rainbow Babies and Childrens Hospital

🇺🇸

Cleveland, Ohio, United States

Miller Children's and Women's Hospital Long Beach

🇺🇸

Long Beach, California, United States

University of Massachusetts Medical School

🇺🇸

Worcester, Massachusetts, United States

Hurley Medical Center

🇺🇸

Flint, Michigan, United States

New York Medical College

🇺🇸

Valhalla, New York, United States

Lucile Packard Children's Hospital Stanford University

🇺🇸

Palo Alto, California, United States

University of Hawaii Cancer Center

🇺🇸

Honolulu, Hawaii, United States

Winthrop University Hospital

🇺🇸

Mineola, New York, United States

The Toledo Hospital/Toledo Children's Hospital

🇺🇸

Toledo, Ohio, United States

MedStar Georgetown University Hospital

🇺🇸

Washington, D.C., District of Columbia, United States

Children's Hospital Los Angeles

🇺🇸

Los Angeles, California, United States

University of Kansas Cancer Center

🇺🇸

Kansas City, Kansas, United States

Dartmouth Hitchcock Medical Center

🇺🇸

Lebanon, New Hampshire, United States

Saint Vincent Hospital

🇺🇸

Green Bay, Wisconsin, United States

Connecticut Children's Medical Center

🇺🇸

Hartford, Connecticut, United States

Kalamazoo Center for Medical Studies

🇺🇸

Kalamazoo, Michigan, United States

University of Kentucky/Markey Cancer Center

🇺🇸

Lexington, Kentucky, United States

Novant Health Presbyterian Medical Center

🇺🇸

Charlotte, North Carolina, United States

BI-LO Charities Children's Cancer Center

🇺🇸

Greenville, South Carolina, United States

Virginia Commonwealth University/Massey Cancer Center

🇺🇸

Richmond, Virginia, United States

Alfred I duPont Hospital for Children

🇺🇸

Wilmington, Delaware, United States

Overlook Hospital

🇺🇸

Summit, New Jersey, United States

Providence Sacred Heart Medical Center and Children's Hospital

🇺🇸

Spokane, Washington, United States

Children's Healthcare of Atlanta - Egleston

🇺🇸

Atlanta, Georgia, United States

Sinai Hospital of Baltimore

🇺🇸

Baltimore, Maryland, United States

Hackensack University Medical Center

🇺🇸

Hackensack, New Jersey, United States

Bronson Methodist Hospital

🇺🇸

Kalamazoo, Michigan, United States

Dayton Children's Hospital

🇺🇸

Dayton, Ohio, United States

Dell Children's Medical Center of Central Texas

🇺🇸

Austin, Texas, United States

Mary Bridge Children's Hospital and Health Center

🇺🇸

Tacoma, Washington, United States

Madigan Army Medical Center

🇺🇸

Tacoma, Washington, United States

Sanford USD Medical Center - Sioux Falls

🇺🇸

Sioux Falls, South Dakota, United States

Covenant Children's Hospital

🇺🇸

Lubbock, Texas, United States

Michigan State University Clinical Center

🇺🇸

East Lansing, Michigan, United States

Children's Hospital of Pittsburgh of UPMC

🇺🇸

Pittsburgh, Pennsylvania, United States

Cleveland Clinic Foundation

🇺🇸

Cleveland, Ohio, United States

Seattle Children's Hospital

🇺🇸

Seattle, Washington, United States

University of New Mexico Cancer Center

🇺🇸

Albuquerque, New Mexico, United States

University of Mississippi Medical Center

🇺🇸

Jackson, Mississippi, United States

Mission Hospital-Memorial Campus

🇺🇸

Asheville, North Carolina, United States

Greenville Cancer Treatment Center

🇺🇸

Greenville, South Carolina, United States

University of Alberta Hospital

🇨🇦

Edmonton, Alberta, Canada

Princess Margaret Hospital for Children

🇦🇺

Perth, Western Australia, Australia

Starship Children's Hospital

🇳🇿

Grafton, Auckland, New Zealand

Marshfield Clinic

🇺🇸

Marshfield, Wisconsin, United States

Saskatoon Cancer Centre

🇨🇦

Saskatoon, Saskatchewan, Canada

Christchurch Hospital

🇳🇿

Christchurch, New Zealand

British Columbia Children's Hospital

🇨🇦

Vancouver, British Columbia, Canada

C S Mott Children's Hospital

🇺🇸

Ann Arbor, Michigan, United States

Nemours Children's Hospital

🇺🇸

Orlando, Florida, United States

Wake Forest University Health Sciences

🇺🇸

Winston-Salem, North Carolina, United States

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