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The Global Angelman Syndrome Registry

Recruiting
Conditions
Angelman Syndrome
Interventions
Other: Observational study only
Registration Number
NCT05293184
Lead Sponsor
Foundation for Angelman Syndrome Therapeutics, Australia
Brief Summary

The Global Angelman Syndrome Registry is an online patient organisation driven registry to collect information about the natural history of children and adults with Angelman Syndrome. The registry will facilitate 1) recruitment for clinical trials into therapies and interventions to benefit participants with Angelman Syndrome and their families, and 2) advancement of research and best standards of care for Angelman Syndrome.

The registry is currently available in English, Spanish, Traditional Chinese, Italian, Polish, Hindi, and Brazilian Portuguese.

Detailed Description

Not available

Recruitment & Eligibility

Status
RECRUITING
Sex
All
Target Recruitment
5000
Inclusion Criteria
  • Diagnosis of Angelman Syndrome
Exclusion Criteria

Study & Design

Study Type
OBSERVATIONAL
Study Design
Not specified
Arm && Interventions
GroupInterventionDescription
Individuals with Angelman SyndromeObservational study onlyIndividuals from birth to adulthood with Angelman Syndrome
Primary Outcome Measures
NameTimeMethod
Gather longitudinal data on individuals living with Angelman Syndrome70 years (lifespan)

Parent/ caregiver reporting on diagnosis, clinical status, and patient-reported outcomes of individual living with Angelman Syndrome. This will be achieved by inviting parents/ caregivers with additional questionnaire like modules, and tracking changes in their responses over time.

Secondary Outcome Measures
NameTimeMethod

Trial Locations

Locations (1)

Queensland University of Technology

🇦🇺

Brisbane, Queensland, Australia

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