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Observational Study of Obstructive Lung Disease (NOVELTY)

Completed
Conditions
Chronic Obstructive Pulmonary Disease
COPD
Asthma
Interventions
Procedure: Blood draw
Procedure: Urine
Procedure: Lung function measurements
Procedure: Fractional Exhaled Nitric Oxide (FENO)
Registration Number
NCT02760329
Lead Sponsor
AstraZeneca
Brief Summary

The NOVEL Observational longiTudinal studY (NOVELTY) is an observational study of obstructive lung disease and is a multi-country, multi-centre, prospective, longitudinal cohort study which will recruit patients with a diagnosis, or suspected diagnosis, of asthma and/or Chronic Obstructive Pulmonary Disease (COPD). Patients will undergo clinical assessments and receive standard medical care as determined by their treating physician. Patients enrolled in NOVELTY will be followed up yearly by their treating physician for a total duration of three years. In addition, patients will be followed up remotely every 3 months. The NOVELTY study will collect data currently lacking to allow for multinational data collection to fill regional/local gaps and improve comparability across regions.

Detailed Description

The NOVELTY study is a multi-country, multicentre, observational, prospective, longitudinal cohort study which will include patients with a physician diagnosis, or suspected diagnosis, of asthma and/or COPD. Patients will undergo clinical assessments and receive standard medical care as determined by the treating physician. All patients enrolled in the NOVELTY study will be followed up yearly by their treating physician for a total duration of three years. In addition, patients are expected to be followed up remotely once every quarter.

It is estimated that approximately 7,700 patients with suspected or primary diagnosis of asthma and 7,100 patients with suspected or primary diagnosis of COPD will be enrolled by a diverse set of physicians (e.g. primary care physicians, allergists, pulmonologists) from community and hospital outpatient settings within the countries targeted for NOVELTY.

Exposure(s):

The NOVELTY study is a longitudinal cohort study which does not involve or study a specific medicinal product; it will constitute a disease registry. Information about exposure to treatments as part of routine care will be collected (frequency, treatment, duration).

Sample Size Estimations:

The target minimum number of 100 patients per diagnostic label (asthma or COPD), physician-assessed severity level and country has been chosen to support many basic local reimbursement specific requirements with reasonable precision, and to provide large sample size for scientific questions applicable across severities and countries. Therefore, considering the targeted countries, it is estimated that approximately 7,700 patients with asthma and 7,100 patients with COPD will be enrolled.

Statistical Analysis:

After baseline data collection and each annual data collection, data will be summarized for the population overall and by pre specified subgroups, including by country, demographics, exposures, symptom history, treatment history, concurrent clinical features, treatment setting, socioeconomic setting and access to healthcare, where relevant.

Patients' changes regarding their treatment, disease or severity among and other variables that are observed between baseline and follow-up visits, will also be described.

To identify potential differences in disease diagnosis and severity classifications between physicians and guidelines, data collected on lung function results, symptom questionnaires, exacerbation occurrences and medication will allow the formal and consistent classification of the patients according to relevant international guidelines and other current and future phenotypic/diagnostic classifications.

Multivariable models will be used to assess the following: the occurrence of exacerbations and other conditions, including upper and lower Respiratory Tract Infections (RTIs) and their relationship with clinical outcomes, the relationship between Patient Reported Outcomes (PRO) and disease control with impact on daily activity and quality of life, and the relationship between healthcare resource use overall and related to respiratory diseases with disease severity, clinical outcomes, disease type, etc.

Multivariable analysis techniques will be used to identify phenotypes and endotypes, based on biomarkers and/or clinical parameters that are associated with differential outcomes for symptom burden, clinical evolution and healthcare utilisation.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
12255
Inclusion Criteria
  • Diagnosis, or suspected diagnosis, of asthma and/or COPD, according to clinician's judgment
  • Age: 12 years or older (note: in most countries it will only be feasible to include patients aged 18 years or older)
  • Willing and able to sign written, informed consent (or having a responsible, legally authorised representative acting on patient's behalf)
  • Enrolment from an active clinical practice
Exclusion Criteria
  • Patients who participated in any respiratory interventional trial during the 12 months prior to enrolment or at enrolment
  • Patients who, in the opinion of the physician, are unlikely to complete 3 years of follow-up, e.g. poor literacy, substance abuse, life-threatening co-morbidity
  • Patients whose primary respiratory diagnosis (i.e. the condition causing most of their respiratory symptoms) is not asthma or COPD (however, a co-diagnosis of another respiratory disease such as bronchiectasis or interstitial lung disease together with asthma or COPD will be accepted)

In addition, the following are considered criteria for exclusion from the exploratory genetic research (donation of blood for DNA and RNA analysis)

  • Previous allogeneic bone marrow transplant
  • Non-leukocyte depleted whole blood transfusion within 120 days of the date of the genetic sample collection

Study & Design

Study Type
OBSERVATIONAL
Study Design
Not specified
Arm && Interventions
GroupInterventionDescription
Chronic airways diseaseUrinePatients with suspected or primary diagnosis of asthma or COPD
Chronic airways diseaseLung function measurementsPatients with suspected or primary diagnosis of asthma or COPD
Chronic airways diseaseFractional Exhaled Nitric Oxide (FENO)Patients with suspected or primary diagnosis of asthma or COPD
Chronic airways diseaseBlood drawPatients with suspected or primary diagnosis of asthma or COPD
Primary Outcome Measures
NameTimeMethod
Spirometry - change in Forced Vital Capacity (FVC) (L)Change from baseline FVC at Year 1, 2 and 3

Lung function test

Spirometry - change in Peak Expiratory Flow (PEF) (Litre/second [L/s])Change from baseline PEF at Year 1, 2 and 3

Lung function test

Spirometry - change in Inspiratory Capacity (IC) (L)Change from baseline IC at Year 1, 2 and 3

Lung function test

Post-bronchodilator spirometry - FVC (L)Baseline

Bronchodilator reversibility test

Spirometry - change in Forced Expiratory Flow at 25-75% of the forced vital capacity (FEF25-75%) (L/s)Change from baseline FEF25-75% at Year 1, 2 and 3

Lung function test

Change in symptoms/symptom control assessed by the Respiratory Symptoms Questionnaire (RSQ)Change from baseline RSQ scores at Year 1, 2 and 3

Patient reported outcome questionnaire

Spirometry - change in Forced Expiratory Volume in 1 second (FEV1) (Litres [L])Change from baseline FEV1 at Year 1, 2 and 3

Lung function test

Change in symptoms/symptom control assessed by the Asthma Control Test (ACT)Change from baseline ACT scores at Year 1, 2 and 3

Patient reported outcome questionnaire

Post-bronchodilator spirometry - PEF (L/s)Baseline

Bronchodilator reversibility test

Post-bronchodilator spirometry - IC (L)Baseline

Bronchodilator reversibility test

Post-bronchodilator spirometry - FEF25-75% (L/s)Baseline

Bronchodilator reversibility test

Fractional exhaled nitric oxide (FeNO) (parts per billion [ppb])Baseline

Test to measure fractional exhaled nitric oxide (ppb) levels in exhaled breath

COPD Foundation Primary Care Tool for Undiagnosed Respiratory Disease and Exacerbation Risk (CAPTURE) - to identify undiagnosed patients with clinically significant COPDBaseline

Patient reported outcome questionnaire

Post-bronchodilator spirometry - FEV1 (L)Baseline

Bronchodilator reversibility test

Change in symptoms/symptom control assessed by the Chronic Airways Assessment Test (CAAT)Change from baseline CAAT scores at Year 1, 2, and 3

Patient reported outcome questionnaire

Symptoms/symptom control assessed by the modified Medical Research Council (mMRC) scaleBaseline

Patient reported outcome questionnaire

Secondary Outcome Measures
NameTimeMethod

Trial Locations

Locations (1)

Research Site

🇬🇧

York, United Kingdom

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