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A Safety and Tolerability Study of PCI-24781 in Subjects With Cancer

Phase 1
Completed
Conditions
Lymphoma
Non-Hodgkin's Lymphoma
Hodgkin Disease
Multiple Myeloma
Leukemia
Lymphocytic
Interventions
Registration Number
NCT01149668
Lead Sponsor
Pharmacyclics LLC.
Brief Summary

The purpose of this study is to determine the long-term (\> 6 months) safety of PCI 24781 PO in subjects with lymphoma.

Detailed Description

An open-label, monotherapy, multicenter, extension study open to subjects who have derived benefit from PCI 24781 PO for at least 6 months and want to continue receiving study drug.

Subjects enrolled in this study will receive PCI-24781 at the schedule and dosage from their prior protocol. Treatment may be continued as long as there is no evidence of progressive disease or unacceptable toxicity.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
7
Inclusion Criteria
  1. Men and women with cancer that did not progress while treated with PCI 24781 PO for at least 6 months and who want to continue receiving study drug
  2. Eastern Cooperative Oncology Group (ECOG) performance status of ≤ 2
  3. Agreement to use contraception during the study and for 30 days after the last dose of study drug if sexually active and able to bear children
  4. Willing and able to participate in all required evaluations and procedures in this study protocol including swallowing capsules without difficulty
  5. Ability to understand the purpose and risks of the study and provide signed and dated informed consent and authorization to use protected health information (in accordance with national and local subject privacy regulations)
Exclusion Criteria
  1. A life-threatening illness, medical condition or organ system dysfunction which, in the investigator's opinion, could compromise the subject's safety, interfere with the absorption or metabolism of oral PCI-24781, or put the study outcomes at undue risk
  2. Significant cardiovascular disease such as uncontrolled or symptomatic arrhythmias, congestive heart failure, or myocardial infarction within 6 months of screening, or any Class 3 or 4 cardiac disease as defined by the New York Heart Association Functional Classification
  3. Malabsorption syndrome, disease significantly affecting gastrointestinal function, or resection of the stomach or small bowel or ulcerative colitis, symptomatic inflammatory bowel disease, or partial or complete bowel obstruction
  4. Immunotherapy, chemotherapy, radiotherapy, corticosteroids (at dosages equivalent to prednisone > 20 mg/day) or experimental therapy (other than PCI-24781 PO) within 4 weeks before first dose of study drug
  5. Concomitant use of medicines known to cause QT prolongation or torsades de points (see Appendix 2)
  6. Central nervous system involvement by lymphoma
  7. Known history of Human Immunodeficiency Virus (HIV) or active infection with Hepatitis C Virus (HCV) or Hepatitis B Virus (HBV) or any uncontrolled active systemic infection
  8. Creatinine > 1.5 x institutional upper limit of normal (ULN); total bilirubin > 1.5 x ULN (unless due to Gilbert's disease); and aspartate aminotransferase (AST) or alanine aminotransferase (ALT) > 2.5 x ULN
  9. Lactating or pregnant

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
PCI-24781PCI-24781-
Primary Outcome Measures
NameTimeMethod
Safety30 days after last dose of study drug

frequency, severity and relatedness of adverse events

Secondary Outcome Measures
NameTimeMethod
Tumor Responsefrequency of tumor assessments done per standard of care

tumor response will be assessed per established response criteria. This study will capture time to disease progression and duration of response.

Trial Locations

Locations (5)

Northwestern Univ. Med School

🇺🇸

Chicago, Illinois, United States

Nebraska Methodist Hospital

🇺🇸

Omaha, Nebraska, United States

Univ. of Nebraska Medical Center

🇺🇸

Omaha, Nebraska, United States

Horizon Oncology Center

🇺🇸

Lafayette, Indiana, United States

Sarah Cannon Research Institute

🇺🇸

Nashville, Tennessee, United States

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