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A Longitudinal Observational Study of Patients With Nonalcoholic Steatohepatitis (NASH) and Related Conditions Across the Entire Spectrum of Nonalcoholic Fatty Liver Disease (NAFLD)

Recruiting
Conditions
Nonalcoholic Fatty Liver
Nonalcoholic Steatohepatitis
Registration Number
NCT02815891
Lead Sponsor
Target PharmaSolutions, Inc.
Brief Summary

TARGET-NASH is a longitudinal observational cohort study of patients being managed for NASH and related conditions across the entire spectrum NAFLD in usual clinical practice. TARGET-NASH is a research registry of patients with NAFL or NASH within academic and community real-world practices maintained in order to assess the safety and effectiveness of current and future therapies.

Detailed Description

Not available

Recruitment & Eligibility

Status
RECRUITING
Sex
All
Target Recruitment
15000
Inclusion Criteria
  1. Adults and children (age 2 or older) being managed or treated for nonalcoholic fatty liver disease. Diagnosis is based on the clinical judgement of the care provider.
Exclusion Criteria
  1. Inability to provide informed assent/consent.

Study & Design

Study Type
OBSERVATIONAL
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Estimate adverse event frequency and severity and describe management practices10 years

NASH can often be an asymptomatic disease in the setting of other disease-related comorbidities such as diabetes and cardiovascular disease. Once NASH progresses to cirrhosis, these patients can suffer the attendant complications of decompensated liver disease including debilitating fatigue, muscle wasting, ascites, bleeding, encephalopathy, hepatocellular carcinoma, and death. NASH therapies may increase the frequency and severity of certain adverse events, such as edema (pioglitazone), some cancers (vitamin E), and new agents or combinations of agents may have their own unique adverse event profiles and varying needs for management plans (e.g., pruritus and dyslipidemia).

Evaluate the impact of NASH therapies on medical co-morbidities10 years
Establish an understanding of the current natural history of NASH at academic and community medical centers10 years

A detailed analysis of demographics, concurrent medications, metabolic and cardiovascular co-morbidities, staging of liver disease, and outcomes for patients with NASH managed in diverse clinical settings will serve as an important comparator for subsequent interventions that alter the treatment paradigm for this disease.

Evaluate NASH treatment regimens being used in clinical practice10 years

Currently, there are no FDA approved therapies for NASH, however clinicians may use a variety of interventions including diet and exercise programs, vitamin E, bariatric surgery or other unapproved uses of some cholesterol, lipid lowering, anti-diabetic and anti-inflammatory medications as well as alternative medications. TARGET-NASH will monitor the safety and effectiveness of the various treatment choices in enrolled patients.

Examine populations underrepresented in phase II-III clinical trials10 years

Patients with cirrhosis, age \> 70, patients who consume moderate amounts of alcohol and patients with multiple comorbidities such as severe depression, chronic fatigue, fibromyalgia, type 2 diabetes, inflammatory bowel disease, or cardiovascular disease.

Evaluate optimal duration and combination of NASH therapies to achieve clinical response and clinical remission10 years

In addition to diet and exercise, type, dose and duration of therapy of each NASH treatment (both current unapproved therapies and future FDA approved drugs) will be closely followed, with a goal to monitor treatment paradigms and various combination regimens for clinical response and clinical remission.

Examine liver histology10 years
Secondary Outcome Measures
NameTimeMethod

Trial Locations

Locations (74)

Banner University Medical Center - Phoenix Transplant Center and Advanced Liver Clinic

🇺🇸

Phoenix, Arizona, United States

Stanford University

🇺🇸

Palo Alto, California, United States

California Liver Research Institute

🇺🇸

Pasadena, California, United States

University of California, Davis

🇺🇸

Sacramento, California, United States

Silicon Valley Research Institute

🇺🇸

San Jose, California, United States

University of Colorado Anschutz Medical Campus

🇺🇸

Aurora, Colorado, United States

Connecticut Gastroenterology

🇺🇸

Hartford, Connecticut, United States

Connecticut Children's Medical Center

🇺🇸

Hartford, Connecticut, United States

Medstar Georgetown Transplant Institute

🇺🇸

Washington, District of Columbia, United States

Gastro Florida

🇺🇸

Clearwater, Florida, United States

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Banner University Medical Center - Phoenix Transplant Center and Advanced Liver Clinic
🇺🇸Phoenix, Arizona, United States

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