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Temozolomide in Treating Young Patients With High-Risk Relapsed or Refractory Neuroblastoma

Phase 2
Completed
Conditions
Neuroblastoma
Registration Number
NCT00276679
Lead Sponsor
Children's Cancer and Leukaemia Group
Brief Summary

RATIONALE: Drugs used in chemotherapy, such as temozolomide, work in different ways to stop the growth of tumor cells, either by killing the cells or by stopping them from dividing.

PURPOSE: This phase II trial is studying how well temozolomide works in treating patients with high-risk relapsed or refractory neuroblastoma.

Detailed Description

OBJECTIVES:

Primary

* Determine the anti-tumor activity of temozolomide in young patients with high-risk relapsed or refractory neuroblastoma.

Secondary

* Determine the duration of response in patients treated with this drug.

* Determine tolerability of this drug in these patients

* Determine the tumor expression of the cellular repair mechanisms which repair DNA damage (O6-methylguanine-DNA methyltransferase \[MGMT\] and mismatch repair \[MMR\] systems) in patients treated with this drug.

* Correlate MGMT and MMR expression with outcomes in patients treated with this drug.

* Determine if MGMT and MMR expression/activity changes in the tumor during initial presentation, treatment, and relapse/progression in patients treated with this drug.

* Determine the activity of MGMT in bone marrow taken at relapse, in terms of hematological toxicity, in patients treated with this drug.

OUTLINE: This is a multicenter, open label, nonrandomized study.

Patients receive oral temozolomide once daily for 5 days. Treatment repeats every 28 days for 2 courses. Patients achieving stable or responding disease after completion of the 2 courses may receive up to 10 additional courses of treatment in the absence of disease progression or unacceptable toxicity.

PROJECTED ACCRUAL: A total of 25 patients will be accrued for this study.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
Not specified
Inclusion Criteria

Not provided

Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Secondary Outcome Measures
NameTimeMethod

Trial Locations

Locations (21)

Leeds Cancer Centre at St. James's University Hospital

🇬🇧

Leeds, England, United Kingdom

Royal London Hospital

🇬🇧

London, England, United Kingdom

Children's Hospital - Sheffield

🇬🇧

Sheffield, England, United Kingdom

Institute of Child Health at University of Bristol

🇬🇧

Bristol, England, United Kingdom

Centre Hospitalier Regional de Purpan

🇫🇷

Toulouse, France

Sir James Spence Institute of Child Health

🇬🇧

Newcastle-Upon-Tyne, England, United Kingdom

Our Lady's Hospital for Sick Children

🇮🇪

Dublin, Ireland

Leicester Royal Infirmary

🇬🇧

Leicester, England, United Kingdom

Addenbrooke's Hospital at Cambridge University Hospitals NHS Foundation Trust

🇬🇧

Cambridge, England, United Kingdom

Royal Liverpool Children's Hospital, Alder Hey

🇬🇧

Liverpool, England, United Kingdom

Birmingham Children's Hospital

🇬🇧

Birmingham, England, United Kingdom

Great Ormond Street Hospital for Children NHS Trust

🇬🇧

London, England, United Kingdom

Oxford Radcliffe Hospital

🇬🇧

Oxford, England, United Kingdom

Central Manchester and Manchester Children's University Hospitals NHS Trust

🇬🇧

Manchester, England, United Kingdom

Queen's Medical Centre

🇬🇧

Nottingham, England, United Kingdom

Southampton General Hospital

🇬🇧

Southampton, England, United Kingdom

Royal Marsden NHS Foundation Trust - Surrey

🇬🇧

Sutton, England, United Kingdom

Royal Aberdeen Children's Hospital

🇬🇧

Aberdeen, Scotland, United Kingdom

Royal Belfast Hospital for Sick Children

🇬🇧

Belfast, Northern Ireland, United Kingdom

Royal Hospital for Sick Children

🇬🇧

Glasgow, Scotland, United Kingdom

Childrens Hospital for Wales

🇬🇧

Cardiff, Wales, United Kingdom

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