MedPath

Efficacy and Safety of Cadazolid Versus Vancomycin in Subjects With Clostridium Difficile-associated Diarrhea

Phase 3
Completed
Conditions
Clostridium Difficile Infection
Interventions
Drug: Vancomycin-matching placebo
Drug: Cadazolid-matching placebo
Registration Number
NCT01983683
Lead Sponsor
Actelion
Brief Summary

This clinical study is conducted to assess the efficacy of cadazolid compared to vancomycin in subjects with Clostridium difficile-associated diarrhea (CDAD).

Detailed Description

Subjects selected to participate in the study are treated either with cadazolid or vancomycin for 10 days. At the end of treatment, clinical cure is assessed; subjects are then followed-up to assess any disease recurrence.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
631
Inclusion Criteria
  • Signed Informed Consent.
  • Male or female ≥ 18 years of age. Females of childbearing potential must agree to use an adequate and reliable method of contraception.
  • Subject with a diagnosis of mild-moderate or severe CDAD (first occurrence or first recurrence within 3 months) with: Diarrhea: a change in bowel habits with > 3 liquid or unformed bowel movements (UBM) within 24 hours prior to randomization, AND Positive C. difficile toxin test on a stool sample produced within 72 hours prior to randomization.
Exclusion Criteria
  • More than one previous episode of CDAD in the 3-month period prior to randomization.
  • Evidence of life-threatening or fulminant CDAD.
  • Likelihood of death within 72 hours from any cause.
  • History of inflammatory colitides, chronic abdominal pain, or chronic diarrhea.
  • Antimicrobial treatment active against CDAD administered for > 24 hours except for metronidazole treatment failures (MTF)
  • Known hypersensitivity or contraindication to study drugs, oxazolidinones, or quinolones.
  • Unable or unwilling to comply with all protocol requirements.
  • Any circumstances or conditions, which, in the opinion of the investigator, may affect full participation in the study or compliance with the protocol

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
CadazolidVancomycin-matching placeboSubjects receive oral cadazolid 250 mg twice daily (bid) and oral vancomycin-matching placebo 4 times per day (qid) for 10 days
VancomycinCadazolid-matching placeboSubjects receive oral vancomycin 125 mg qid and oral cadazolid-matching placebo bid for 10 days
VancomycinVancomycinSubjects receive oral vancomycin 125 mg qid and oral cadazolid-matching placebo bid for 10 days
CadazolidCadazolidSubjects receive oral cadazolid 250 mg twice daily (bid) and oral vancomycin-matching placebo 4 times per day (qid) for 10 days
Primary Outcome Measures
NameTimeMethod
Clinical Cure Rate (CCR) in the Modified Intent-to-treat PopulationUp to Day 12 on average (end-of-treatment + 2 days)

Clinical Cure is defined as: • Resolution of Diarrhea (ROD) (≤ 3 unformed bowel movement (UBM) per day for at least 2 consecutive days) on study treatment and maintained for 2 days after end-of-treatment (EOT), AND • No additional antimicrobial treatment active against Clostridium difficile-associated diarrhea (CDAD) or fecal microbiota transplant (FMT) between first dose of study drug and 2 days after EOT (inclusive). CCR is the percentage of subjects with Clinical Cure. Analyses are performed on two analysis sets. Results on the modified intent-to-treat set (mITT) are reported below.

Clinical Cure Rate (CCR) in the Per-protocol PopulationUp to Day 12 on average (end-of-treatment + 2 days)

Clinical Cure (CC) is defined as: • Resolution of Diarrhea (≤ 3 unformed bowel movement per day for at least 2 consecutive days) on study treatment and maintained for 2 days after end-of-treatment (EOT), AND • No additional antimicrobial treatment active against Clostridium difficile-associated diarrhea (CDAD) or fecal microbiota transplant between first dose of study drug and 2 days after EOT. CCR is the percentage of subjects with Clinical Cure. Analyses are performed on two analysis sets. Results on the per-protocol set (PPS) are reported below.

Secondary Outcome Measures
NameTimeMethod
Sustained Cure Rate (SCR) in the Modified Intent-to-treat PopulationBetween Day 38 and Day 42 on average (end-of-treatment + 28-32 days)

Sustained Cure is defined for each subject having Clinical Cure and no recurrence. SCR is the percentage of subjects with Sustained Cure. The main analysis is performed on the modified intent-to-treat set (mITT).

Kaplan-Meier Estimates for Resolution of Diarrhea (ROD)Up to Day 10

Resolution of Diarrhea (ROD) is defined as no more than 3 unformed bowel movements per day for at least two consecutive days for subjects on study treatment.

The Kaplan-Meier estimates (KM estimates) for having an event (ROD) are reported for each time point.

Change From Baseline to Day 3 in Clostridium Difficile Infection (CDI) Daily Symptoms Patient-Reported Outcome (CDI-DaySyms PRO) Domain ScoresBaseline to End of Treatment (10 days after starting study drug) + 2 days

CDI-DaySyms PRO is a questionnaire assessing 10 symptoms relevant to subjects with CDAD and grouped into 3 domains: Diarrhea symptoms, Abdominal symptoms and Systemic/Other. The subjects rate the severity of each item as None, Mild, Moderate, Severe or Very severe, converted to numeric scores from 0 to 4, respectively. The daily domain score is calculated as the mean of the non-missing responses for that domain on that day. A negative value for change from baseline corresponds to an improvement in domain score. The three domains are evaluated in a hierarchical manner, starting with Diarrhea Symptoms, then Abdominal Symptoms, and finally Systemic/Other Symptoms.

Trial Locations

Locations (7)

Investigator Site 2784

🇭🇷

Zagreb, Croatia

Investigator Site 2786

🇭🇷

Zagreb, Croatia

Investigator Site 2780

🇭🇷

Zagreb, Croatia

Investigator Site 2788

🇭🇷

Pozega, Croatia

Investigator Site 2785

🇭🇷

Zagreb, Croatia

Investigator Site 2781

🇭🇷

Zagreb, Croatia

Investigator Site

🇸🇰

Nitra, Slovakia

© Copyright 2025. All Rights Reserved by MedPath