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Niraparib as Maintenance Therapy in Patients With Platinum Sensitive Recurrent Ovarian Cancer

Completed
Conditions
Epithelial Ovarian Cancer
Fallopian Tube Cancer
Primary Peritoneal Cancer
Registration Number
NCT04546373
Lead Sponsor
Grupo Español de Investigación en Cáncer de Ovario
Brief Summary

In April 2017, Tesaro, Inc. opened an expanded access program (EAP) to make niraparib, an investigational poly (ADP-ribose) polymerase (PARP) inhibitor, available to eligible women with recurrent epithelial ovarian, fallopian tube, or primary peritoneal cancer following a complete or partial response to platinum-based chemotherapy, mainly for BRCA wild-type (BRCAwt) tumor patients, a clear unmet medical need for these ovarian cancer patients. As of 19 August 2019, the EAP closing date, there were 446 patients enrolled in 105 Spanish sites.

All eligible deceased and consenting living patients at the participating centers will be included. Data will be directly retrieved from hospital medical records and reported in the electronic Case Report Form (eCRF).

This study seeks to evaluate the safety profile and dose adjustments of niraparib in platinum sensitive recurrent ovarian cancer patients treated in a real world setting within the Spanish expanded access program (EAP).

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
Female
Target Recruitment
316
Inclusion Criteria
  • Female participants 18 years old or older.

  • Participant must be able to understand the study procedures and agree to participate in the study by providing written informed consent.

  • Participant must have received niraparib within the Spanish expanded access program (EAP).

  • Patients must have received at least 1 week of treatment with niraparib.

  • Histological diagnosis of high grade serous ovarian cancer, fallopian tube cancer, or primary peritoneal cancer.

  • Participants must have completed at least 2 previous courses of platinum-containing therapy (e.g., carboplatin, oxaliplatin, or cisplatin).

  • For the penultimate (next to last) platinum-based chemotherapy course prior to enrolment on the program the patient must have platinum sensitive disease after this treatment; defined as achieving a response (complete response (CR) or partial response (PR)) and disease progression occurring no sooner than 6 months, after completion of the last dose of platinum chemotherapy.

  • For the last chemotherapy course prior to inclusion in the program the patient must have received a platinum-containing regimen for a minimum of 4 cycles.

  • For the last chemotherapy course prior to inclusion in the program the Patient must have achieved a partial (PR) or complete (CR) tumor response.

  • The last platinum regimen does not necessarily have to immediately follow the next to last (penultimate) platinum regimen. For example, if a patient received a non-platinum regimen between the penultimate platinum regimen and last platinum regimen, they could be eligible, so long as they meet all entry criteria.

  • When entering the EAP, patients must have met the following:

    • Eastern Cooperative Oncology Group (ECOG) performance status 0 or 1.
    • Adequate organ function - Absolute neutrophil count (ANC) ≥ (greater than or equal to) 1,500/μL.
    • Adequate organ function - Platelets ≥ (greater than or equal to) 100,000/μL.
    • Adequate organ function - Hemoglobin ≥ (greater than or equal to) 9 g/dL.
    • No transfusions of erythrocytes or platelets within 2 weeks prior to assessing adequate hematological blood counts as listed above.
Exclusion Criteria
  • Patients without medical record available (lost, empty or unretrievable clinical information).
  • Patients who decline consent.
  • Patients who are deceased with prior express order to preserve their data.

Study & Design

Study Type
OBSERVATIONAL
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
DemographicsMonth 4-6
Medical HistoryMonth 4-6
Ovarian Cancer DiagnosisMonth 4-6
Ovarian Cancer Treatments (pre-Niraparib)Month 4-6
Baseline (pre-Niraparib)Month 4-6
Niraparib TreatmentMonth 4-6
Niraparib Disease ProgressionMonth 4-6
Best Response AssessmentMonth 4-6
Niraparib-Related Adverse EventsMonth 4-6
Relevant Concomitant MedicationsMonth 4-6
DeathMonth 4-6
Survival StatusMonth 4-6
Subsequent Therapies for Ovarian CancerMonth 4-6
Secondary Outcome Measures
NameTimeMethod

Trial Locations

Locations (57)

Hospital Universitari Dexeus - Grupo Quirónsalud

🇪🇸

Barcelona, Spain

Institut Català d´ Oncologia-Hospital Duran y Reynals

🇪🇸

L'Hospitalet De Llobregat, Barcelona, Spain

Hospital de la Santa Creu i Sant Pau

🇪🇸

Barcelona, Spain

Hospital Virgen de los Lirios

🇪🇸

Alcoy, Alicante, Spain

Hospital General de Granollers

🇪🇸

Granollers, Barcelona, Spain

Hospital Universitario Puerta de Hierro

🇪🇸

Majadahonda, Madrid, Spain

Clínica Corachan

🇪🇸

Barcelona, Spain

Complejo Hospitalario Universitario A Coruña (Juan Canalejo)

🇪🇸

A Coruña, Spain

Hospital Universitari Sant Joan d'Alacant

🇪🇸

Alicante, Spain

Hospital Universitario Clínico San Cecilio

🇪🇸

Granada, Spain

Hospital Lluís Alcanyís de Xàtiva

🇪🇸

Xàtiva, Valencia, Spain

Clínica Universidad de Navarra

🇪🇸

Madrid, Spain

Hospital Quirónsalud Sagrado Corazón

🇪🇸

Sevilla, Spain

Hospital Clínico San Carlos

🇪🇸

Madrid, Spain

Hospital Universitario HM Sanchinarro

🇪🇸

Madrid, Spain

Hospital Clínico Universitario de Salamanca

🇪🇸

Salamanca, Spain

Hospital Universitario de La Princesa

🇪🇸

Madrid, Spain

Hospital Universitari i Politècnic La Fe

🇪🇸

Valencia, Spain

Hospital Clínico Universitario Lozano Blesa

🇪🇸

Zaragoza, Spain

Hospital Universitario de Galdakao

🇪🇸

Galdakao, Bizkaia, Spain

Hospital Universitario de Jerez

🇪🇸

Jerez De La Frontera, Cádiz, Spain

Hospital Provincial de Castellón

🇪🇸

Castelló de la Plana, Castellón, Spain

Hospital Marina Baixa

🇪🇸

Villajoyosa, Alicante, Spain

Hospital Álvaro Cunqueiro

🇪🇸

Vigo, Pontevedra, Spain

Hospital Universitario Donostia

🇪🇸

San Sebastián, Gipuzkoa, Spain

Consorci Sanitari de Terrassa

🇪🇸

Rubí, Barcelona, Spain

Hospital Clínic i Provincial de Barcelona

🇪🇸

Barcelona, Spain

Hospital General San Jorge

🇪🇸

Huesca, Spain

Hospital Universitario Reina Sofía

🇪🇸

Córdoba, Spain

MD Anderson Cancer Center Madrid

🇪🇸

Madrid, Spain

Hospital Universitari Arnau de Vilanova

🇪🇸

Lleida, Spain

Hospital Universitario Ramón y Cajal

🇪🇸

Madrid, Spain

Hospital Universitario 12 De Octubre

🇪🇸

Madrid, Spain

Hospital Universitario La Paz

🇪🇸

Madrid, Spain

Hospital Universitario Doctor Peset

🇪🇸

Valencia, Spain

Hospital Clínico Universitario de Valladolid

🇪🇸

Valladolid, Spain

Hospital Universitario de Valme

🇪🇸

Sevilla, Spain

Hospital Universitario de Guadalajara

🇪🇸

Guadalajara, Spain

Hospital Clínico Universitario de Santiago

🇪🇸

Santiago De Compostela, A Coruña, Spain

Hospital Universitario Central de Asturias

🇪🇸

Oviedo, Asturias, Spain

Institut Català d'Oncología Badalona

🇪🇸

Badalona, Barcelona, Spain

Hospital Universitario Marqués de Valdecilla

🇪🇸

Santander, Cantabria, Spain

Hospital Universari Son Espases

🇪🇸

Palma De Mallorca, Islas Baleares, Spain

Hospital Universitario Infanta Sofia

🇪🇸

San Sebastián De Los Reyes, Madrid, Spain

Hospital Universitario Torrecárdenas

🇪🇸

Almería, Spain

Hospital del Mar

🇪🇸

Barcelona, Spain

Hospital Universitario de Basurto

🇪🇸

Bilbao, Vizcaya, Spain

Hospital Universitario Puerta del Mar

🇪🇸

Cádiz, Spain

Hospital San Pedro de Alcántara

🇪🇸

Cáceres, Spain

Complejo Hospitalario de Jaén - Hospital Médico-Quirúrgico

🇪🇸

Jaén, Spain

Complejo Hospitalario Universitario de Pontevedra (Hospital Montecelo)

🇪🇸

Pontevedra, Spain

Hospital Universitario Nuestra Señora de Candelaria

🇪🇸

Santa Cruz De Tenerife, Spain

Hospital Universitario Virgen del Rocio

🇪🇸

Sevilla, Spain

Consorcio Hospital General Universitario de Valencia

🇪🇸

Valencia, Spain

Hospital Universitario Miguel Servet

🇪🇸

Zaragoza, Spain

Consorci Corporació Sanitària Parc Taulí de Sabadell

🇪🇸

Sabadell, Barcelona, Spain

Hospital Universitario Fundación Alcorcón

🇪🇸

Alcorcón, Madrid, Spain

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