MedPath

A Study to Evaluate the Risk of Tumor Lysis Syndrome (TLS) in Adult Participants Receiving Oral Venetoclax in Combination With Intravenously Infused Obinutuzumab or Oral Acalabrutinib for Previously Untreated Chronic Lymphocytic Leukemia (CLL)

Phase 3
Recruiting
Conditions
Chronic Lymphocytic Leukemia
Interventions
Registration Number
NCT06428019
Lead Sponsor
AbbVie
Brief Summary

Chronic lymphocytic leukemia (CLL) is the most common leukemia (cancer of blood cells). The purpose of this study is to assess the safety of venetoclax in combination with obinutuzumab or acalabrutinib in the treatment of CLL. Adverse events and change in disease activity will be assessed.

Venetoclax in combination with obinutuzumab or acalabrutinib is being investigated in the treatment of CLL. Study doctors put the participants in 1 of 4 groups, called treatment arms. Participants will receive oral venetoclax in combination with intravenously (IV) infused obinutuzumab or oral acalabrutinib at in different dosing schemes as part of treatment. Approximately 120 adult participants with CLL who are being treated with venetoclax will be enrolled in the study in approximately 80 sites worldwide.

Participants in Arm A will receive oral venetoclax in combination with IV infused obinutuzumab, with a 5 week venetoclax ramp up. Participants in Arm B will receive oral venetoclax in combination with oral acalabrutinib, with a 5 week venetoclax ramp up. Participants in Arm C and Arm D will receive oral venetoclax in combination with oral acalabrutinib, with differing venetoclax ramp up periods. The total study duration is approximately 28 months.

There may be higher treatment burden for participants in this trial compared to their standard of care. Participants will attend regular visits during the study at a hospital or clinic. The effect of the treatment will be checked by medical assessments, blood tests, checking for side effects and completing questionnaires.

Detailed Description

Not available

Recruitment & Eligibility

Status
RECRUITING
Sex
All
Target Recruitment
120
Inclusion Criteria
  • Diagnosis of documented, previously untreated, chronic lymphocytic leukemia (CLL) requiring treatment according to the 2018 international workshop on chronic lymphocytic leukemia (iwCLL) criteria and have a life expectancy of > 6 months.
  • Previously untreated small lymphocytic lymphoma (SLL) meeting the 2018 iwCLL criteria for treatment will also be equally considered as CLL for eligibility, screening, treatment and evaluation.
  • Eastern Cooperative Oncology Group (ECOG) performance status <= 2.
  • Adequate marrow function independent of growth factor or transfusion support within 2 weeks of screening, unless cytopenia is due to marrow involvement of CLL as listed in the protocol.
  • Creatinine clearance (CrCl) >= 30 mL/min using the Cockcroft-Gault formula are eligible for inclusion.
Exclusion Criteria
  • Active/uncontrolled infection, no Richter's transformation, no active immune thrombocytopenia.

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Arm D: Venetoclax + AcalabrutinibAcalabrutinibParticipants will receive venetoclax in combination with acalabrutinib, with a modified venetoclax ramp up B.
Arm D: Venetoclax + AcalabrutinibVenetoclaxParticipants will receive venetoclax in combination with acalabrutinib, with a modified venetoclax ramp up B.
Arm A: Venetoclax + ObinutuzumabObinutuzumabParticipants will receive venetoclax in combination with obinutuzumab, with a 5 week venetoclax ramp up.
Arm A: Venetoclax + ObinutuzumabVenetoclaxParticipants will receive venetoclax in combination with obinutuzumab, with a 5 week venetoclax ramp up.
Arm B: Venetoclax + AcalabrutinibVenetoclaxParticipants will receive venetoclax in combination with acalabrutinib, with a 5 week venetoclax ramp up.
Arm B: Venetoclax + AcalabrutinibAcalabrutinibParticipants will receive venetoclax in combination with acalabrutinib, with a 5 week venetoclax ramp up.
Arm C: Venetoclax + AcalabrutinibVenetoclaxParticipants will receive venetoclax in combination with acalabrutinib, with a modified venetoclax ramp up A.
Arm C: Venetoclax + AcalabrutinibAcalabrutinibParticipants will receive venetoclax in combination with acalabrutinib, with a modified venetoclax ramp up A.
Primary Outcome Measures
NameTimeMethod
Part 1: Percentage of Participants with Treatment-Emergent Laboratory Tumor Lysis Syndrome (TLS)-VenetoclaxUp to 28 Months

TLS is defined per Howard criteria that require a clinical intervention per independent review committee (IRC) assessment during the venetoclax ramp-up period in previously untreated participants with chronic lymphocytic leukemia (CLL) achieving a medium tumor burden with creatinine clearance (CrCl) of at least 80 ml/min or low tumor burden (regardless of CrCl level) after debulking therapy.

Part 1: Percentage of Participants with Hyperkalemia-VenetoclaxUp to 28 Months

Hyperkalemia (potassium \>6.0 mmol/L) is defined per Howard criteria that require a clinical intervention per IRC assessment during the venetoclax ramp-up period in previously untreated participants with CLL achieving a medium tumor burden with CrCl of at least 80 ml/min or low tumor burden (regardless of CrCl level) after debulking therapy.

Secondary Outcome Measures
NameTimeMethod
Part 1: Percentage of Participants with Treatment-Emergent Laboratory TLSUp to 28 Months

TLS is defined per Howard criteria that require a clinical intervention per IRC assessment, at each dose level and at each laboratory monitoring point during ramp-up period in previously untreated participants with CLL achieving a medium tumor burden with CrCl of at least 80 ml/min or low tumor burden (regardless of CrCl level) after debulking therapy.

Part 1: Percentage of Participants with HyperkalemiaUp to 28 Months

Hyperkalemia (potassium \>6.0 mmol/L) is defined per Howard criteria that require a clinical intervention per independent review committee (IRC) assessment during the venetoclax ramp-up period in previously untreated participants with CLL achieving a medium tumor burden with CrCl of at least 80 ml/min or low tumor burden (regardless of CrCl level) after debulking therapy.

Part 1: Percentage of Participants with Treatment-Emergent TLS-Related EventsUp to 28 Months

TLS-related events are defined as laboratory TLS per Howard criteria requiring clinical intervention per IRC assessment, hyperkalemia (potassium \>6.0 mmol/L) requiring clinical intervention per IRC assessment, laboratory TLS per Howard criteria irrespective of clinical intervention, Hyperkalemia (potassium \>6.0 mmol/L) irrespective of clinical intervention, clinical TLS per Howard criteria irrespective of clinical intervention, any single TLS-related lab abnormality requiring clinical intervention per Investigator.

Part 1: Percentage of Participants with Adverse Events (AE) of TLSUp to 28 Months

AEs of TLS is defined as a blood chemistry changes or symptom suggestive of TLS.

Part 1: Percentage of Participants with Reduction of Tumor Burden from BaselineUp to 28 Months

Percentage of participants with reduction of tumor burden.

Trial Locations

Locations (64)

West Virginia University School of Medicine /ID# 267645

🇺🇸

Morgantown, West Virginia, United States

Arizona Oncology - Tucson - Rudasill /ID# 267552

🇺🇸

Tucson, Arizona, United States

UCSF FRESNO/Community Cancer Institute /ID# 270874

🇺🇸

Clovis, California, United States

Valkyrie Clinical Trials /ID# 268151

🇺🇸

Los Angeles, California, United States

Rocky Mountain Cancer Centers - Aurora /ID# 267549

🇺🇸

Aurora, Colorado, United States

Yale University School of Medicine /ID# 266224

🇺🇸

New Haven, Connecticut, United States

Malcolm Randall V.A. Medical Center /ID# 267825

🇺🇸

Gainesville, Florida, United States

Cancer Specialists of North Florida - Jacksonville - AC Skinner Parkway /ID# 266713

🇺🇸

Jacksonville, Florida, United States

Mid Florida Hematology And Oncology Center /ID# 269159

🇺🇸

Orange City, Florida, United States

Comprehensive Hematology Oncology /ID# 267644

🇺🇸

Saint Petersburg, Florida, United States

Springfield Clinic /ID# 270145

🇺🇸

Springfield, Illinois, United States

Northwest Cancer Center - Dyer Clinic /ID# 268478

🇺🇸

Dyer, Indiana, United States

University of Iowa Health Care /ID# 267206

🇺🇸

Des Moines, Iowa, United States

Willis-Knighton Medical Center /ID# 270569

🇺🇸

Shreveport, Louisiana, United States

American Oncology Partners of Maryland /ID# 266445

🇺🇸

Bethesda, Maryland, United States

Maryland Oncology Hematology - Silver Spring /ID# 267557

🇺🇸

Silver Spring, Maryland, United States

Saint Luke's Hospital of Kansas City /ID# 267270

🇺🇸

Kansas City, Missouri, United States

Cleveland Clinic Main Campus /ID# 271292

🇺🇸

Cleveland, Ohio, United States

Oklahoma Cancer Specialists and Research Institute /ID# 267643

🇺🇸

Tulsa, Oklahoma, United States

Willamette Valley Cancer Institute and Research Center /ID# 266326

🇺🇸

Eugene, Oregon, United States

Lifespan Cancer Institute - Providence /ID# 266550

🇺🇸

Providence, Rhode Island, United States

Texas Oncology - Austin Midtown /ID# 268152

🇺🇸

Austin, Texas, United States

University of Texas - Southwestern Medical Center /ID# 266528

🇺🇸

Dallas, Texas, United States

Virginia Cancer Specialists - Gainesville /ID# 268155

🇺🇸

Gainesville, Virginia, United States

Vista Oncology - East Olympia /ID# 267337

🇺🇸

Olympia, Washington, United States

Northwest Medical Specialties Tacoma /ID# 266327

🇺🇸

Tacoma, Washington, United States

Calvary Mater Newcastle /ID# 267408

🇦🇺

Waratah, New South Wales, Australia

Townsville University Hospital /ID# 266954

🇦🇺

Townsville, Queensland, Australia

St Vincent's Hospital - Melbourne /ID# 270027

🇦🇺

Fitzroy, Victoria, Australia

Royal Perth Hospital /ID# 266906

🇦🇺

Perth, Western Australia, Australia

Centre Hospitalier Universitaire de Saint Etienne - Hopital Nord /ID# 266319

🇫🇷

St-Priest-en-Jarez, Loire, France

CHR Metz-Thionville - Hôpital de Mercy /ID# 266852

🇫🇷

Ars Laquenexy, Moselle, France

Hopitaux Universitaires Henri Mondor - Hopital Henri Mondor /ID# 266270

🇫🇷

Creteil, Paris, France

Hopitaux Universitaires Paris Centre-Hopital Cochin /ID# 267438

🇫🇷

Paris CEDEX 14, Paris, France

Centre Antoine-Lacassagne /ID# 266894

🇫🇷

Nice, Provence-Alpes-Cote-d Azur, France

Centre Hospitalier de la Côte Basque /ID# 266847

🇫🇷

Bayonne, Pyrenees-Atlantiques, France

Centre Hospitalier Métropole Savoie - Site Hôpital de Chambéry /ID# 266854

🇫🇷

Chambery CEDEX, Savoie, France

CHU d'Amiens-Picardie - Hôpital Sud /ID# 266849

🇫🇷

Amiens CEDEX 1, Somme, France

Centre Hospitalier d'Argenteuil Victor Dupouy /ID# 266322

🇫🇷

Argenteuil, France

Centre Hospitalier Régional d'Orléans - Hôpital de la Source /ID# 266272

🇫🇷

Orléans, France

Olympion General Clinic /ID# 266819

🇬🇷

Patras, Achaia, Greece

Evangelismos Hospital /ID# 266815

🇬🇷

Athens, Attiki, Greece

General Hospital of Athens Laiko /ID# 266813

🇬🇷

Athens, Attiki, Greece

University General Hospital Attikon /ID# 266814

🇬🇷

Athens, Attiki, Greece

University General Hospital of Alexandroupoli /ID# 266816

🇬🇷

Alexandroupoli, Evros, Greece

Pan American Center for Oncology Trials /ID# 266243

🇵🇷

Rio Piedras, Puerto Rico

Clinical Hospital Center Zvezdara /ID# 266560

🇷🇸

Belgrade, Beograd, Serbia

University Clinical Center Serbia /ID# 266579

🇷🇸

Belgrade, Beograd, Serbia

Clinical Hospital Center - Bežanijska Kosa /ID# 266567

🇷🇸

Belgrade, Beograd, Serbia

University Clinical Center Nis /ID# 266580

🇷🇸

Niš, Nisavski Okrug, Serbia

University Clinical Center Kragujevac /ID# 266568

🇷🇸

Kragujevac, Sumadijski Okrug, Serbia

Institute for Oncology of Vojvodina /ID# 266556

🇷🇸

Sremska Kamenica, Vojvodina, Serbia

University Clinical Center Vojvodina /ID# 266674

🇷🇸

Novi Sad, Serbia

Complejo Hospitalario Universitario de Santiago (CHUS) /ID# 267164

🇪🇸

Santiago de Compostela, A Coruna, Spain

Hospital Universitario Puerta de Hierro - Majadahonda /ID# 266967

🇪🇸

Majadahonda, Madrid, Spain

Clinica Universidad de Navarra - Pamplona /ID# 267762

🇪🇸

Pamplona, Navarra, Spain

CLINICA UNIVERSIDAD DE NAVARRA-Madrid /ID# 266969

🇪🇸

Madrid, Spain

Hospital MD Anderson Cancer Center Madrid /ID# 267167

🇪🇸

Madrid, Spain

Hospital Universitario Virgen del Rocio /ID# 266968

🇪🇸

Sevilla, Spain

Kaohsiung Chang Gung Memorial Hospital /ID# 267046

🇨🇳

Kaohsiung City, Kaohsiung, Taiwan

National Taiwan University Hospital /ID# 267017

🇨🇳

Taipei City, Taipei, Taiwan

China Medical University Hospital /ID# 267018

🇨🇳

Taichung, Taiwan

Linkou Chang Gung Memorial Hospital /ID# 267045

🇨🇳

Taoyuan City, Taiwan

Nottingham City Hospital /ID# 266991

🇬🇧

Nottingham, Nottinghamshire, United Kingdom

© Copyright 2025. All Rights Reserved by MedPath