MedPath

A Study Evaluating the Safety, Pharmacokinetics, and Efficacy of Alectinib in Pediatric Participants With ALK Fusion-Positive Solid or CNS Tumors

Phase 1
Recruiting
Conditions
ALK Fusion-positive Solid or CNS Tumors
Interventions
Registration Number
NCT04774718
Lead Sponsor
Hoffmann-La Roche
Brief Summary

This study will evaluate the safety, pharmacokinetics, and efficacy of alectinib in children and adolescents with ALK fusion-positive solid or CNS tumors for whom prior treatment has proven to be ineffective or for whom there is no satisfactory standard treatment available.

Detailed Description

Not available

Recruitment & Eligibility

Status
RECRUITING
Sex
All
Target Recruitment
42
Inclusion Criteria

Not provided

Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
ALK-Fusion PositiveAlectinibPart 1 is a dose-confirmation phase to confirm the recommended phase 2 dose (RP2D). In Parts 2 and 3, participants will receive alectinib at the RP2D on Days 1-28 of each 28-day cycle
Primary Outcome Measures
NameTimeMethod
Plasma Concentration of AlectinibUp to 10 years
Confirmed Objective Response Rate (ORR): Defined as the Proportion of Participants with Complete Response (CR) or Partial Response (PR) on two Consecutive Occasions >/= 4 Weeks Apart, as Determined by Blinded Independent Central Review (BICR)Up to 10 years
Percentage of Participants with Adverse EventsUp to 10 years
Incidence of Participants with Dose-Limited Toxicities (DLTs)Cycle 1 (cycle length = 28 days)
Plasma Concentration of Alectinib Metabolite (M4)Up to 10 years
Secondary Outcome Measures
NameTimeMethod
Confirmed ORR as Determined by the InvestigatorUp to 10 years
Time to Response (TTR) as Determined by BICR and the InvestigatorFrom the first dose of alectinib to the first documentation of objective response (CR or PR) (up to 10 years)
Progression-Free Survival (PFS) as Determined by BICR and the InvestigatorFrom the first dose of alectinib to the first occurrence of disease progression or death from any cause, whichever occurs first (up to 10 years)
Overall Survival (OS)From the first dose of alectinib to the date of death due to any cause (up to 10 years)
Duration of Response (DOR) as Determined by BICR and the InvestigatorFrom the first occurrence of a documented objective response (CR or PR) to disease progression or death from any cause, whichever occurs first (up to 10 years)
Clinical Benefit Rate (CBR) as Determined by BICR and the Investigator6 months after the first dose of alectinib

Trial Locations

Locations (33)

Lucile Packard Children's Hospital

🇺🇸

Palo Alto, California, United States

Children's Minnesota

🇺🇸

Minneapolis, Minnesota, United States

Hospital de Cancer de Barretos

🇧🇷

Barretos, São Paulo, Brazil

Rigshospitalet

🇩🇰

København Ø, Denmark

Institut Curie - Centre de Lutte Contre le Cancer (CLCC) de Paris

🇫🇷

Paris, France

Universitätsklinikum Heidelberg

🇩🇪

Heidelberg, Germany

Istituto Nazionale Tumori di Milano

🇮🇹

Milano, Lombardia, Italy

Dipartimento di Scienze Pediatriche Adolescenza

🇮🇹

Torino, Piemonte, Italy

Hospital Universitario Virgen del Rocio

🇪🇸

Sevilla, Spain

Johns Hopkins All Children's Hospital

🇺🇸

Saint Petersburg, Florida, United States

Scroll for more (23 remaining)
Lucile Packard Children's Hospital
🇺🇸Palo Alto, California, United States

MedPath

Empowering clinical research with data-driven insights and AI-powered tools.

© 2025 MedPath, Inc. All rights reserved.