MedPath

Rituximab, Cladribine, and Temsirolimus in Treating Patients With Newly Diagnosed Mantle Cell Lymphoma

Phase 1
Completed
Conditions
Lymphoma
Interventions
Biological: rituximab
Biological: Filgrastim
Biological: Pegfilgrastim
Registration Number
NCT00787969
Lead Sponsor
Alliance for Clinical Trials in Oncology
Brief Summary

This phase I/II trial studies the side effects and best dose of temsirolimus when given together with cladribine and rituximab and to see how well it works in treating patients with newly diagnosed mantle cell lymphoma. Monoclonal antibodies, such as rituximab, may interfere with the ability of cancer cells to grow and spread. Drugs used in chemotherapy, such as cladribine, work in different ways to stop the growth of cancer cells, either by killing the cells, by stopping them from dividing, or by stopping them from spreading. Temsirolimus may stop the growth of cancer cells by blocking some of the enzymes needed for cell growth. Giving temsirolimus together with cladribine and rituximab may kill more cancer cells.

Detailed Description

PRIMARY OBJECTIVES:

I. To assess the efficacy and safety of the combination of rituximab, cladribine, and temsirolimus for newly diagnosed mantle cell lymphoma.

II. To determine the maximum tolerated dose (MTD) of temsirolimus combined with a fixed dose and schedule of rituximab and cladribine. (Phase I) III. To assess the efficacy of the combination of rituximab, cladribine, and temsirolimus for newly diagnosed mantle cell lymphoma with the proportion of complete responses as the primary endpoint. (Phase II)

SECONDARY OBJECTIVES:

I. To assess other measures of efficacy of the regimen including progression free survival, duration of response, and overall survival.

II. To assess the toxicity profile of the combination of rituximab, cladribine, and temsirolimus.

III. To assess efficacy using traditional lymphoma parameters and absolute lymphocyte count.

IV. To assess metabolic markers (hyperglycemia, hyperlipidemia) as markers of mammalian target of rapamycin (mTOR) inhibition using the glucose and lipid measurements being performed in the clinical laboratory as part of routine care.

V. To correlate response with serum free light chains, single nucleotide polymorphisms (SNPs) in host immune genes, vitamin D metabolites, and phosphatidylinositide 3-kinase (PI3K) pathway member expression.

VI. As part of ongoing research for North Central Cancer Treatment Group (NCCTG) lymphoma studies, paraffin-embedded tissue blocks/slides and blood products will be banked for future studies.

OUTLINE: This is a phase I, dose-escalation study of temsirolimus followed by a phase II study.

Patients receive rituximab intravenously (IV) on day 1 and cladribine IV over 2 hours on days 1-5. Patients then receive temsirolimus IV over 30 minutes on days 1, 8, 15, and 22. Patients also receive filgrastim subcutaneously (SC) on days 6-15 or pegfilgrastim SC on day 6. Treatment repeats every 28 days for up to 6 courses in the absence of disease progression or unacceptable toxicity.

After completion of study treatment, patients are followed up every 3 months for 2 years and then every 4 months for 3 years.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
74
Inclusion Criteria
  • Histologically confirmed mantle cell lymphoma (MCL); the diagnosis must be confirmed by NCCTG pre-registration pathology review by Dr. Paul Kurtin or his designate; it is recommended that the biopsy be an excisional biopsy, but adequate core-needle biopsies will be accepted as long as they are considered adequate for registration by Dr. Kurtin or his designate; the tumor must be cyclin D-1 positive by immunohistochemistry or have evidence of a t(11;14) translocation by fluorescence based in situ hybridization (FISH) or cytogenetics

  • Measurable or assessable disease, defined as at least one of the following:

    • A lymph node or tumor mass that is >= 2.0 cm in at least one dimension by positron emission tomography (PET)/computed tomography (CT), CT, magnetic resonance imaging (MRI), or plain radiograph imaging
    • Splenic enlargement may be used as a measurable parameter if the spleen is palpable >= 3 cm below the left costal margin
    • Diffuse infiltration of an organ such as the stomach, bone marrow, peripheral blood, liver, lungs, or bowel by lymphoma without a discrete mass would constitute assessable, but not measurable, disease
  • Eastern Cooperative Oncology Group (ECOG) performance status (PS) of 0, 1, 2, or 3

  • Life expectancy >= 12 weeks

  • Absolute neutrophil count (ANC) >= 1,500/mm³

  • Platelet count (PLT) >= 100,000/mm³

  • Serum creatinine =< 2.0 mg/dL

  • Serum total bilirubin (or direct bilirubin if total is abnormal) =< institutional upper limit of normal (ULN) with or without secondary liver involvement

  • Serum glutamic oxaloacetic transaminase (SGOT) =< 3 x institutional ULN (exception: if there is liver involvement, SGOT must be =< 5 x institutional ULN)

  • Negative pregnancy test done =< 7 days prior to registration, for women of childbearing potential only

  • Willingness to return to NCCTG enrolling institution for follow-up

  • Willingness to provide the blood specimens as required by the protocol

  • Willingness to provide tissue specimens as required by the protocol

  • Willing to return to NCCTG enrolling institution for follow-up

  • Willing to provide blood and tissue specimens as required by the protocol

  • Willing to abstain from eating grapefruit or drinking grapefruit juice

  • Willingness to abstain from eating grapefruit or drinking grapefruit juice for the duration of the study

Exclusion Criteria

  • Any prior therapy for mantle cell non-Hodgkin lymphoma including radiation therapy; exception: patient may have undergone a splenectomy for diagnosis, cytopenia, or systematic splenomegaly

  • Active or uncontrolled infection

  • Any of the following cardiac conditions:

    • Uncontrolled high blood pressure
    • Unstable angina
    • Active congestive heart failure
    • Myocardial infarction =< 6 months
    • Serious uncontrolled cardiac arrhythmia
  • Known central nervous system (CNS) involvement

  • Any of the following:

    • Pregnant women or women of reproductive ability who are unwilling to use effective contraception while taking the drug and for 12 months after stopping treatment
    • Nursing women
    • Men who are unwilling to use a condom (even if they have undergone a prior vasectomy) while having intercourse with any woman, while taking the drug and for 12 months after stopping treatment
  • Medical or psychiatric conditions which, in the opinion of the investigator, make the patient a poor risk for participation

  • Known to be human immunodeficiency virus (HIV) positive; HIV testing is not required but should be done if clinically indicated; HIV-positive patients receiving combination anti-retroviral therapy are excluded from the study

  • Concurrent malignancy =< 5 years ago; exceptions: carcinoma in situ of the cervix, resected basal cell or squamous cell carcinomas of the skin, or prostate cancer that is in remission following a radical retropubic prostatectomy or radiation therapy; if there is a history of prior malignancy, they must not be receiving other specific treatment (other than hormonal therapy) for their cancer

  • Known hypersensitivity to rituximab or its components, or to murine proteins

  • Receiving any other investigational agent which would be considered as a treatment for the primary neoplasm

  • Prior treatment with an mTOR inhibitor

  • Autologous or allogeneic stem cell transplant planned as part of initial therapy

  • Receiving enzyme-inducing antiepileptic drugs (enzyme inducing anti-epileptic drugs [EIAEDs]; e.g., phenytoin, fosphenytoin, carbamazepine, oxcarbazepine, phenobarbital, or primidone); any other potent cytochrome P450, family 3, subfamily A, polypeptide 4 (CYP3A4) inducer such as rifampin, glucocorticoids at greater than adrenal replacement levels, or St. John's wort; or receiving strong CYP3A4 inhibitors * Note: if these agents are discontinued, temsirolimus therapy can begin >= 7 days after discontinuation of such agent

Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
Treatment (rituximab, cladribine, temsirolimus)rituximabPatients receive rituximab IV on day 1 and cladribine IV over 2 hours on days 1-5. Patients then receive temsirolimus IV over 30 minutes on days 1, 8, 15, and 22. Patients also receive filgrastim SC on days 6-15 or pegfilgrastim SC on day 6. Treatment repeats every 28 days for up to 6 courses in the absence of disease progression or unacceptable toxicity.
Treatment (rituximab, cladribine, temsirolimus)PegfilgrastimPatients receive rituximab IV on day 1 and cladribine IV over 2 hours on days 1-5. Patients then receive temsirolimus IV over 30 minutes on days 1, 8, 15, and 22. Patients also receive filgrastim SC on days 6-15 or pegfilgrastim SC on day 6. Treatment repeats every 28 days for up to 6 courses in the absence of disease progression or unacceptable toxicity.
Treatment (rituximab, cladribine, temsirolimus)FilgrastimPatients receive rituximab IV on day 1 and cladribine IV over 2 hours on days 1-5. Patients then receive temsirolimus IV over 30 minutes on days 1, 8, 15, and 22. Patients also receive filgrastim SC on days 6-15 or pegfilgrastim SC on day 6. Treatment repeats every 28 days for up to 6 courses in the absence of disease progression or unacceptable toxicity.
Treatment (rituximab, cladribine, temsirolimus)cladribinePatients receive rituximab IV on day 1 and cladribine IV over 2 hours on days 1-5. Patients then receive temsirolimus IV over 30 minutes on days 1, 8, 15, and 22. Patients also receive filgrastim SC on days 6-15 or pegfilgrastim SC on day 6. Treatment repeats every 28 days for up to 6 courses in the absence of disease progression or unacceptable toxicity.
Treatment (rituximab, cladribine, temsirolimus)temsirolimusPatients receive rituximab IV on day 1 and cladribine IV over 2 hours on days 1-5. Patients then receive temsirolimus IV over 30 minutes on days 1, 8, 15, and 22. Patients also receive filgrastim SC on days 6-15 or pegfilgrastim SC on day 6. Treatment repeats every 28 days for up to 6 courses in the absence of disease progression or unacceptable toxicity.
Primary Outcome Measures
NameTimeMethod
Number of dose limiting toxicity incidents as per National Cancer Institute (NCI) Common Terminology Criteria for Adverse Events (CTCAE) version (v) 3.0 (Phase I)28 days
Proportion of complete tumor responses defined as complete remission (CR) as the objective status (Phase II)Up to 5 years
Secondary Outcome Measures
NameTimeMethod
Progression-free survival (PFS)up to 5 years
Time to disease progressionup to 5 years
Survival timeUp to 5 years
Overall survivalup to 5 years
Duration of response, defined as date at which the patient's objective status is first noted to be either a CR or partial remission to the date progression is documentedUp to 5 years
Frequency and severity of adverse events assessed by CTCAE v3.0Up to 5 years

Trial Locations

Locations (144)

Elkhart General Hospital

🇺🇸

Elkhart, Indiana, United States

Bismarck Cancer Center

🇺🇸

Bismarck, North Dakota, United States

St. Alexius Medical Center Cancer Center

🇺🇸

Bismarck, North Dakota, United States

Mayo Clinic Scottsdale

🇺🇸

Scottsdale, Arizona, United States

St. Mary's Hospital Medical Center - Green Bay

🇺🇸

Green Bay, Wisconsin, United States

Rapid City Regional Hospital

🇺🇸

Rapid City, South Dakota, United States

Holy Family Memorial Medical Center Cancer Care Center

🇺🇸

Manitowoc, Wisconsin, United States

Green Bay Oncology, Limited at St. Mary's Hospital

🇺🇸

Green Bay, Wisconsin, United States

Illinois CancerCare - Galesburg

🇺🇸

Galesburg, Illinois, United States

Illinois CancerCare - Macomb

🇺🇸

Macomb, Illinois, United States

Illinois CancerCare - Monmouth

🇺🇸

Monmouth, Illinois, United States

Eureka Community Hospital

🇺🇸

Eureka, Illinois, United States

CCOP - Northern Indiana CR Consortium

🇺🇸

South Bend, Indiana, United States

BroMenn Regional Medical Center

🇺🇸

Normal, Illinois, United States

Illinois CancerCare - Community Cancer Center

🇺🇸

Normal, Illinois, United States

Community Hospital of Ottawa

🇺🇸

Ottawa, Illinois, United States

Michiana Hematology-Oncology, PC - South Bend

🇺🇸

Mishawaka, Indiana, United States

McDonough District Hospital

🇺🇸

Macomb, Illinois, United States

Illinois CancerCare - Peru

🇺🇸

Peru, Illinois, United States

Illinois CancerCare - Kewanee Clinic

🇺🇸

Kewanee, Illinois, United States

Community Cancer Center

🇺🇸

Normal, Illinois, United States

OSF St. Francis Medical Center

🇺🇸

Peoria, Illinois, United States

Cancer Treatment Center at Pekin Hospital

🇺🇸

Pekin, Illinois, United States

St. Joseph Medical Center

🇺🇸

Bloomington, Illinois, United States

Illinois CancerCare - Canton

🇺🇸

Canton, Illinois, United States

Illinois CancerCare - Havana

🇺🇸

Havana, Illinois, United States

Illinois CancerCare - Spring Valley

🇺🇸

Spring Valley, Illinois, United States

Michiana Hematology Oncology PC - Plymouth

🇺🇸

Plymouth, Indiana, United States

Galesburg Clinic, PC

🇺🇸

Galesburg, Illinois, United States

OSF Holy Family Medical Center

🇺🇸

Monmouth, Illinois, United States

Illinois CancerCare - Pekin

🇺🇸

Pekin, Illinois, United States

Proctor Hospital

🇺🇸

Peoria, Illinois, United States

Perry Memorial Hospital

🇺🇸

Princeton, Illinois, United States

Methodist Medical Center of Illinois

🇺🇸

Peoria, Illinois, United States

Oncology Hematology Associates of Central Illinois, PC - Ottawa

🇺🇸

Ottawa, Illinois, United States

Center for Cancer Therapy at LaPorte Hospital and Health Services

🇺🇸

La Porte, Indiana, United States

Cedar Rapids Oncology Associates

🇺🇸

Cedar Rapids, Iowa, United States

Northern Montana Hospital

🇺🇸

Havre, Montana, United States

CCOP - Montana Cancer Consortium

🇺🇸

Billings, Montana, United States

Billings Clinic - Downtown

🇺🇸

Billings, Montana, United States

Green Bay Oncology, Limited - Sturgeon Bay

🇺🇸

Sturgeon Bay, Wisconsin, United States

St. James Healthcare Cancer Care

🇺🇸

Butte, Montana, United States

Kalispell Medical Oncology at KRMC

🇺🇸

Kalispell, Montana, United States

Bay Area Cancer Care Center at Bay Area Medical Center

🇺🇸

Marinette, Wisconsin, United States

Bozeman Deaconess Cancer Center

🇺🇸

Bozeman, Montana, United States

St. Peter's Hospital

🇺🇸

Helena, Montana, United States

Glacier Oncology, PLLC

🇺🇸

Kalispell, Montana, United States

Kalispell Regional Medical Center

🇺🇸

Kalispell, Montana, United States

St. Vincent Healthcare Cancer Care Services

🇺🇸

Billings, Montana, United States

Great Falls Clinic - Main Facility

🇺🇸

Great Falls, Montana, United States

Regions Hospital Cancer Care Center

🇺🇸

Saint Paul, Minnesota, United States

Hennepin County Medical Center - Minneapolis

🇺🇸

Minneapolis, Minnesota, United States

Virginia Piper Cancer Institute at Abbott - Northwestern Hospital

🇺🇸

Minneapolis, Minnesota, United States

Park Nicollet Cancer Center

🇺🇸

Saint Louis Park, Minnesota, United States

Mercy and Unity Cancer Center at Mercy Hospital

🇺🇸

Coon Rapids, Minnesota, United States

Humphrey Cancer Center at North Memorial Outpatient Center

🇺🇸

Robbinsdale, Minnesota, United States

Cancer Center of Kansas - Fort Scott

🇺🇸

Fort Scott, Kansas, United States

HealthEast Cancer Care at St. John's Hospital

🇺🇸

Maplewood, Minnesota, United States

Mercy and Unity Cancer Center at Unity Hospital

🇺🇸

Fridley, Minnesota, United States

St. Francis Cancer Center at St. Francis Medical Center

🇺🇸

Shakopee, Minnesota, United States

Welch Cancer Center at Sheridan Memorial Hospital

🇺🇸

Sheridan, Wyoming, United States

Mid Dakota Clinic, PC

🇺🇸

Bismarck, North Dakota, United States

Miller - Dwan Medical Center

🇺🇸

Duluth, Minnesota, United States

Minnesota Oncology Hematology, PA - Maplewood

🇺🇸

Maplewood, Minnesota, United States

CCOP - Duluth

🇺🇸

Duluth, Minnesota, United States

Fairview Ridges Hospital

🇺🇸

Burnsville, Minnesota, United States

Hutchinson Area Health Care

🇺🇸

Hutchinson, Minnesota, United States

Cancer Center of Kansas, PA - Dodge City

🇺🇸

Dodge City, Kansas, United States

Illinois Valley Community Hospital

🇺🇸

Peru, Illinois, United States

Michiana Hematology Oncology PC - La Porte

🇺🇸

Westville, Indiana, United States

CCOP - Illinois Oncology Research Association

🇺🇸

Peoria, Illinois, United States

Howard Community Hospital

🇺🇸

Kokomo, Indiana, United States

Saint Joseph Regional Medical Center

🇺🇸

Mishawaka, Indiana, United States

Mercy Regional Cancer Center at Mercy Medical Center

🇺🇸

Cedar Rapids, Iowa, United States

Mercy Cancer Center at Mercy Medical Center - Des Moines

🇺🇸

Des Moines, Iowa, United States

CCOP - Iowa Oncology Research Association

🇺🇸

Des Moines, Iowa, United States

Illinois CancerCare - Bloomington

🇺🇸

Bloomington, Illinois, United States

Graham Hospital

🇺🇸

Canton, Illinois, United States

Illinois CancerCare - Carthage

🇺🇸

Carthage, Illinois, United States

Memorial Hospital

🇺🇸

Carthage, Illinois, United States

Illinois CancerCare - Eureka

🇺🇸

Eureka, Illinois, United States

Mason District Hospital

🇺🇸

Havana, Illinois, United States

Oncology Hematology Associates of Central Illinois, PC - Peoria

🇺🇸

Peoria, Illinois, United States

Illinois CancerCare - Princeton

🇺🇸

Princeton, Illinois, United States

Elkhart Clinic, LLC

🇺🇸

Elkhart, Indiana, United States

Memorial Hospital of South Bend

🇺🇸

South Bend, Indiana, United States

McFarland Clinic, PC

🇺🇸

Ames, Iowa, United States

Medical Oncology and Hematology Associates - West Des Moines

🇺🇸

Clive, Iowa, United States

John Stoddard Cancer Center at Iowa Methodist Medical Center

🇺🇸

Des Moines, Iowa, United States

Medical Oncology and Hematology Associates at John Stoddard Cancer Center

🇺🇸

Des Moines, Iowa, United States

Medical Oncology and Hematology Associates at Mercy Cancer Center

🇺🇸

Des Moines, Iowa, United States

John Stoddard Cancer Center at Iowa Lutheran Hospital

🇺🇸

Des Moines, Iowa, United States

Siouxland Hematology-Oncology Associates, LLP

🇺🇸

Sioux City, Iowa, United States

Mercy Cancer Center at Mercy Medical Center - North Iowa

🇺🇸

Mason City, Iowa, United States

Mercy Medical Center - Sioux City

🇺🇸

Sioux City, Iowa, United States

Cancer Center of Kansas, PA - Chanute

🇺🇸

Chanute, Kansas, United States

St. Luke's Regional Medical Center

🇺🇸

Sioux City, Iowa, United States

Cancer Center of Kansas, PA - El Dorado

🇺🇸

El Dorado, Kansas, United States

Cancer Center of Kansas-Independence

🇺🇸

Independence, Kansas, United States

Cancer Center of Kansas, PA - Kingman

🇺🇸

Kingman, Kansas, United States

Lawrence Memorial Hospital

🇺🇸

Lawrence, Kansas, United States

Cancer Center of Kansas, PA - Liberal

🇺🇸

Liberal, Kansas, United States

Cancer Center of Kansas, PA - Newton

🇺🇸

Newton, Kansas, United States

Cancer Center of Kansas, PA - Parsons

🇺🇸

Parsons, Kansas, United States

Cancer Center of Kansas, PA - Pratt

🇺🇸

Pratt, Kansas, United States

Cancer Center of Kansas, PA - Salina

🇺🇸

Salina, Kansas, United States

Cancer Center of Kansas, PA - Wellington

🇺🇸

Wellington, Kansas, United States

Associates in Womens Health, PA - North Review

🇺🇸

Wichita, Kansas, United States

Cancer Center of Kansas, PA - Medical Arts Tower

🇺🇸

Wichita, Kansas, United States

Cancer Center of Kansas, PA - Wichita

🇺🇸

Wichita, Kansas, United States

CCOP - Wichita

🇺🇸

Wichita, Kansas, United States

Cancer Center of Kansas, PA - Winfield

🇺🇸

Winfield, Kansas, United States

Via Christi Cancer Center at Via Christi Regional Medical Center

🇺🇸

Wichita, Kansas, United States

Battle Creek Health System Cancer Care Center

🇺🇸

Battle Creek, Michigan, United States

Mecosta County Medical Center

🇺🇸

Big Rapids, Michigan, United States

Green Bay Oncology, Limited - Escanaba

🇺🇸

Escanaba, Michigan, United States

Butterworth Hospital at Spectrum Health

🇺🇸

Grand Rapids, Michigan, United States

CCOP - Grand Rapids

🇺🇸

Grand Rapids, Michigan, United States

Lacks Cancer Center at Saint Mary's Health Care

🇺🇸

Grand Rapids, Michigan, United States

Dickinson County Healthcare System

🇺🇸

Iron Mountain, Michigan, United States

Mercy General Health Partners

🇺🇸

Muskegon, Michigan, United States

Michiana Hematology Oncology PC - Niles

🇺🇸

Niles, Michigan, United States

Lakeland Regional Cancer Care Center - St. Joseph

🇺🇸

Saint Joseph, Michigan, United States

Lakeside Cancer Specialists, PLLC

🇺🇸

Saint Joseph, Michigan, United States

Munson Medical Center

🇺🇸

Traverse City, Michigan, United States

Metro Health Hospital

🇺🇸

Wyoming, Michigan, United States

Fairview Southdale Hospital

🇺🇸

Edina, Minnesota, United States

CCOP - Metro-Minnesota

🇺🇸

Saint Louis Park, Minnesota, United States

Mayo Clinic Cancer Center

🇺🇸

Rochester, Minnesota, United States

Ridgeview Medical Center

🇺🇸

Waconia, Minnesota, United States

Lakeview Hospital

🇺🇸

Stillwater, Minnesota, United States

United Hospital

🇺🇸

Saint Paul, Minnesota, United States

Willmar Cancer Center at Rice Memorial Hospital

🇺🇸

Willmar, Minnesota, United States

Minnesota Oncology Hematology, PA - Woodbury

🇺🇸

Woodbury, Minnesota, United States

Hematology-Oncology Centers of the Northern Rockies - Billings

🇺🇸

Billings, Montana, United States

Sletten Cancer Institute at Benefis Healthcare

🇺🇸

Great Falls, Montana, United States

Montana Cancer Center at St. Patrick Hospital and Health Sciences Center

🇺🇸

Missoula, Montana, United States

Green Bay Oncology, Limited - Oconto Falls

🇺🇸

Oconto Falls, Wisconsin, United States

St. Vincent Hospital Regional Cancer Center

🇺🇸

Green Bay, Wisconsin, United States

St. Nicholas Hospital

🇺🇸

Sheboygan, Wisconsin, United States

Medcenter One Hospital Cancer Care Center

🇺🇸

Bismarck, North Dakota, United States

Michiana Hematology-Oncology, PC - Elkhart

🇺🇸

Elkhart, Indiana, United States

Duluth Clinic Cancer Center - Duluth

🇺🇸

Duluth, Minnesota, United States

Green Bay Oncology, Limited at St. Vincent Hospital Regional Cancer Center

🇺🇸

Green Bay, Wisconsin, United States

© Copyright 2025. All Rights Reserved by MedPath