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Treatment With hOKT3gamma1(Ala-Ala) in T1DM

Phase 2
Terminated
Conditions
Diabetes Mellitus, Type 1
Interventions
Registration Number
NCT00806572
Lead Sponsor
National Institute of Allergy and Infectious Diseases (NIAID)
Brief Summary

This is a phase II study to examine the clinical and immunological effects of humanized FcR non-binding anti-CD3 mAb in participants with Type 1 diabetes mellitus (T1DM), and to develop this therapy to prevent the immune destruction leading to β cell loss.

Detailed Description

This is a 2-arm, open-label phase II trial involving 0 or 3 cycles of treatment 6 months apart with hOKT3γ1 (Ala-Ala), over the first year of disease in participants with new onset T1DM. Each cycle consists of 12 daily doses of hOKT3γ1 (Ala-Ala).

Participants will be randomized in a ratio of 2:1 to either the experimental arm or the control arm and will be stratified by study site.

To be eligible, participants must be: male or female between 7-30 years of age, diagnosed with T1DM within the past 6 weeks, have a body weight ≥26 kg at the time of enrollment and have detectable anti-GAD, anti-ICA512/IA-2, or insulin autoantibodies (if the participant has been on insulin ≤10 days).

Participants randomized to the experimental group will start the first cycle of hOKT3γ1 (Ala-Ala) within 4-8 weeks of T1DM diagnosis. Each participant randomized to the experimental group will receive 3 cycles of drug treatment, separated by 6 months each. Each cycle consists of 12 days of drug treatment.

Both groups will undergo the Mixed Meal Stimulated C-Peptide Test and receive blood draws for mechanistic studies on the same schedule.

Recruitment & Eligibility

Status
TERMINATED
Sex
All
Target Recruitment
10
Inclusion Criteria
  • diagnosed with T1DM within the past 6 weeks
  • have a body weight ≥26 kg at the time of enrollment
  • have detectable anti-GAD, anti-ICA512/IA-2, or insulin autoantibodies (if the participant has been on insulin ≤10 days).
Exclusion Criteria
  • Pregnant or lactating females;
  • Prior OKT3 treatment;
  • Known hypersensitivity to murine products;
  • Uncompensated heart failure or fluid overload, recent myocardial infarction;
  • History of epilepsy, cancer, active infection, atopic disease, active Grave's disease, cystic fibrosis, sickle cell anemia, neuropathy, peripheral vascular disease, cerebrovascular disease, any concurrent autoimmune diseases, asthma;
  • Any medical condition that in the opinion of the investigator will interfere with safe completion of the trial;
  • Inability to give informed consent;
  • Prior participation in a clinical trial that could potentially affect diabetes or immunologic status;
  • Participation in a clinical trial within the last 6 weeks;
  • HIV positive;
  • Positive for Hepatitis B surface antigen or Anti-Hepatitis C antibody;
  • Seropositivity for Toxoplasmosis (IgG);
  • Lymphopenia (<1000 lymphocytes/microliter);
  • Thrombocytopenia (<150,000/mm3 platelets);
  • Anemia (Hgb < 10g/dL);
  • Vaccination with a live virus within the past 6 weeks;
  • Positive PPD skin test;
  • Any infectious mononucleosis-like illness within the 3 months prior to enrollment;
  • Serologic evidence of acute infection with EBV or CMV based on tests listed and as defined by the protocol.

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
TreatmenthOKT3gamma1(Ala-Ala)-
Primary Outcome Measures
NameTimeMethod
4-hour C-peptide AUC24 months
Secondary Outcome Measures
NameTimeMethod
Insulin usagethroughout study

Trial Locations

Locations (3)

University of California San Francisco

🇺🇸

San Francisco, California, United States

Benaroya Research Institute

🇺🇸

Seattle, Washington, United States

Naomie Berrie Diabetes Center, Columbia University

🇺🇸

New York, New York, United States

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