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Vaccine Therapy and Sargramostim in Treating Patients With Stage IV Malignant Melanoma

Not Applicable
Completed
Conditions
Recurrent Melanoma
Stage IV Melanoma
Interventions
Biological: tyrosinase peptide
Biological: gp100 antigen
Biological: incomplete Freund's adjuvant
Other: laboratory biomarker analysis
Biological: sargramostim
Registration Number
NCT00006243
Lead Sponsor
National Cancer Institute (NCI)
Brief Summary

This randomized pilot clinical trial studies vaccine therapy and sargramostim in treating patients with stage IV malignant melanoma. Vaccines made from melanoma peptides or antigens may help the body build an effective immune response to kill tumor cells. Colony-stimulating factors, such as sargramostim, increase the number of white blood cells and platelets found in bone marrow or peripheral blood. Giving vaccine therapy together with sargramostim may be an effective treatment for malignant melanoma

Detailed Description

PRIMARY OBJECTIVES:

I. Determine the immunological effects of immunization protocols utilizing MART-1:27-35 (MART-1:27-35 peptide vaccine), tyrosinase (tyrosinase peptide) or gp-100 (gp100 antigen) peptides suspended in incomplete Freund's adjuvant (IFA) in the presence of two different concentrations of sargramostim (GM-CSF).

II. Define the safety and toxicity profile of an immunization protocol utilizing varying concentrations of MART-1:27-35, tyrosinase and gp-100 peptides suspended in IFA in the presence of two different concentrations of GM-CSF.

III. Collect preliminary data on therapeutic efficacy as it relates to parameters of immune function in patients with stage IV malignant melanoma.

OUTLINE: Patients are randomized to 1 of 3 treatment arms.

ARM I: Patients receive tyrosinase peptide, MART-1:27-35 peptide vaccine, and gp100 antigen admixed in incomplete Freund's adjuvant subcutaneously (SC) on day 1 of weeks 0, 3, 6, 9, 12, and 24.

ARM II: Patients receive tyrosinase peptide, MART-1:27-35 peptide vaccine, and gp100 antigen admixed in incomplete Freund's adjuvant SC and lower-dose sargramostim SC on day 1 of weeks 0, 3, 6, 9, 12, and 24.

ARM III: Patients receive tyrosinase peptide, MART-1:27-35 peptide vaccine, and gp100 antigen admixed in incomplete Freund's adjuvant SC and higher-dose sargramostim SC on day 1 of weeks 0, 3, 6, 9, 12, and 24.

In all arms, treatment may repeat every 3 months for up to 18 months in the absence of disease progression or unacceptable toxicity.

After completion of study treatment, patients are followed up every 3 months for up to 3 years.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
30
Inclusion Criteria
  • Human leukocyte antigen (HLA)-A2 positive
  • Histologic proof of stage IV malignant melanoma with measurable disease
  • Absolute neutrophil count (ANC) >= 1500
  • Platelets (PLT) >= 100,000
  • Alkaline phosphatase (Alk phos) =< 3 x upper limit of normal (ULN)
  • Aspartate aminotransferase (AST) =< 3 x ULN
  • Creatinine (Creat) =< 1.5 x ULN
  • Hemoglobin (Hgb) > 9.0
  • Ability to provide informed consent
  • Willingness to return to a Mayo Clinic institution for follow-up
  • Life expectancy >= 12 weeks
  • Eastern Cooperative Oncology Group (ECOG) performance status 0, 1 or 2
Exclusion Criteria
  • Uncontrolled or current infection

  • Prior immunization with differentiation antigen peptides

  • Known standard therapy for the patient's disease that is potentially curative or proven capable of extending life expectancy

  • Any of the following prior therapies:

    • Chemotherapy =< 4 weeks
    • Mitomycin C/nitrosoureas =< 6 weeks
    • Immunotherapy =<4 weeks
    • Biologic therapy =< 4 weeks
    • Radiation therapy =< 4 weeks
    • Radiation to > 25% of bone marrow
  • Failure to fully recover from effects of prior chemotherapy regardless of interval since last treatment

  • New York Heart Association classification III or IV

  • Seizure disorder

  • Any of the following:

    • Pregnant women
    • Nursing women
    • Women of childbearing potential or their sexual partners who are unwilling to employ adequate contraception (condoms, diaphragm, birth control pills, injections, intrauterine device [IUD], surgical sterilization, subcutaneous implants, or abstinence, etc.)
  • Other concurrent chemotherapy, immunotherapy, or radiotherapy

  • Active psychiatric disorder requiring medications (anti-psychotics)

  • Known central nervous system metastases or carcinomatous meningitis

  • History of other malignancy in last 5 years with the exception of basal cell or squamous cell carcinoma of the skin treated with local resection only (it is impossible to predict the effect of study treatment on other, potentially dormant malignant diseases)

  • Known immune deficiency (patients with known immune deficiencies will likely not be able to mount an immune response to the study vaccine)

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Arm I (vaccine therapy)tyrosinase peptidePatients receive tyrosinase peptide, MART-1:27-35 peptide vaccine, and gp100 antigen admixed in incomplete Freund's adjuvant SC on day 1 of weeks 0, 3, 6, 9, 12, and 24.
Arm I (vaccine therapy)gp100 antigenPatients receive tyrosinase peptide, MART-1:27-35 peptide vaccine, and gp100 antigen admixed in incomplete Freund's adjuvant SC on day 1 of weeks 0, 3, 6, 9, 12, and 24.
Arm I (vaccine therapy)incomplete Freund's adjuvantPatients receive tyrosinase peptide, MART-1:27-35 peptide vaccine, and gp100 antigen admixed in incomplete Freund's adjuvant SC on day 1 of weeks 0, 3, 6, 9, 12, and 24.
Arm I (vaccine therapy)laboratory biomarker analysisPatients receive tyrosinase peptide, MART-1:27-35 peptide vaccine, and gp100 antigen admixed in incomplete Freund's adjuvant SC on day 1 of weeks 0, 3, 6, 9, 12, and 24.
Arm II (vaccine therapy and lower-dose sargramostim)tyrosinase peptidePatients receive tyrosinase peptide, MART-1:27-35 peptide vaccine, and gp100 antigen admixed in incomplete Freund's adjuvant SC and lower-dose sargramostim SC on day 1 of weeks 0, 3, 6, 9, 12, and 24.
Arm II (vaccine therapy and lower-dose sargramostim)gp100 antigenPatients receive tyrosinase peptide, MART-1:27-35 peptide vaccine, and gp100 antigen admixed in incomplete Freund's adjuvant SC and lower-dose sargramostim SC on day 1 of weeks 0, 3, 6, 9, 12, and 24.
Arm II (vaccine therapy and lower-dose sargramostim)incomplete Freund's adjuvantPatients receive tyrosinase peptide, MART-1:27-35 peptide vaccine, and gp100 antigen admixed in incomplete Freund's adjuvant SC and lower-dose sargramostim SC on day 1 of weeks 0, 3, 6, 9, 12, and 24.
Arm II (vaccine therapy and lower-dose sargramostim)sargramostimPatients receive tyrosinase peptide, MART-1:27-35 peptide vaccine, and gp100 antigen admixed in incomplete Freund's adjuvant SC and lower-dose sargramostim SC on day 1 of weeks 0, 3, 6, 9, 12, and 24.
Arm II (vaccine therapy and lower-dose sargramostim)laboratory biomarker analysisPatients receive tyrosinase peptide, MART-1:27-35 peptide vaccine, and gp100 antigen admixed in incomplete Freund's adjuvant SC and lower-dose sargramostim SC on day 1 of weeks 0, 3, 6, 9, 12, and 24.
Arm III (vaccine therapy and higher-dose sargramostim)tyrosinase peptidePatients receive tyrosinase peptide, MART-1:27-35 peptide vaccine, and gp100 antigen admixed in incomplete Freund's adjuvant SC and higher-dose sargramostim SC on day 1 of weeks 0, 3, 6, 9, 12, and 24.
Arm III (vaccine therapy and higher-dose sargramostim)gp100 antigenPatients receive tyrosinase peptide, MART-1:27-35 peptide vaccine, and gp100 antigen admixed in incomplete Freund's adjuvant SC and higher-dose sargramostim SC on day 1 of weeks 0, 3, 6, 9, 12, and 24.
Arm III (vaccine therapy and higher-dose sargramostim)incomplete Freund's adjuvantPatients receive tyrosinase peptide, MART-1:27-35 peptide vaccine, and gp100 antigen admixed in incomplete Freund's adjuvant SC and higher-dose sargramostim SC on day 1 of weeks 0, 3, 6, 9, 12, and 24.
Arm III (vaccine therapy and higher-dose sargramostim)sargramostimPatients receive tyrosinase peptide, MART-1:27-35 peptide vaccine, and gp100 antigen admixed in incomplete Freund's adjuvant SC and higher-dose sargramostim SC on day 1 of weeks 0, 3, 6, 9, 12, and 24.
Arm III (vaccine therapy and higher-dose sargramostim)laboratory biomarker analysisPatients receive tyrosinase peptide, MART-1:27-35 peptide vaccine, and gp100 antigen admixed in incomplete Freund's adjuvant SC and higher-dose sargramostim SC on day 1 of weeks 0, 3, 6, 9, 12, and 24.
Primary Outcome Measures
NameTimeMethod
Changes in tumor antigen peptide specific immune responsesBaseline and 24 weeks

Plots of the percent changes in these factors from their pretreatment levels against time will be constructed.

Secondary Outcome Measures
NameTimeMethod
Number and severity of hematologic and non-hematologic toxicities observed using the Common Toxicity Criteria (CTC) version 2.0Up to 3 years
Proportion of objective responses (complete response [CR] and partial response [PR]) observedUp to 3 years

Trial Locations

Locations (1)

Mayo Clinic

🇺🇸

Rochester, Minnesota, United States

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