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Imetelstat Sodium in Treating Young Patients With Refractory or Recurrent Solid Tumors or Lymphoma

Phase 1
Completed
Conditions
Brain and Central Nervous System Tumors
Lymphoma
Lymphoproliferative Disorder
Small Intestine Cancer
Unspecified Childhood Solid Tumor, Protocol Specific
Interventions
Other: laboratory biomarker analysis
Other: pharmacological study
Registration Number
NCT01273090
Lead Sponsor
Children's Oncology Group
Brief Summary

RATIONALE: Imetelstat sodium may stop the growth of tumor cells by blocking some of the enzymes needed for cell growth.

PURPOSE: This phase I clinical trial is studying the side effects and best dose of imetelstat sodium in treating young patients with refractory or recurrent solid tumors or lymphoma.

Detailed Description

OBJECTIVES:

Primary

* To estimate the maximum-tolerated dose (MTD) and/or recommended phase II dose of imetelstat sodium in children with refractory or recurrent solid tumors or lymphoma.

* To define and describe the toxicities of imetelstat sodium.

* To characterize the pharmacokinetics of imetelstat sodium in children with refractory or recurrent solid tumors or lymphoma.

Secondary

* To determine, in a preliminary manner, the antitumor effects of imetelstat sodium in children with refractory or recurrent solid tumors or lymphoma. (exploratory)

* To provide preliminary assessment of the biological activity of imetelstat sodium in children with recurrent or refractory malignancies by assessing telomerase activity, telomere length, hTERT protein, hTERT mRNA, and hTR levels in patient peripheral blood mononuclear cells (PBMNC) samples pretreatment and on treatment. (Exploratory)

* To assess telomerase activity, hTERT expression, telomere length, hTERT protein, hTERT mRNA, and hTR levels in patients' pretreatment tumor samples. (Exploratory)

OUTLINE: This is a multicenter, dose-escalation study.

Patients receive imetelstat sodium IV over 2 hours on days 1 and 8. Treatment repeats every 21 days for up to 18 courses in the absence of disease progression or unacceptable toxicity.

Patients undergo blood sample collection at baseline and periodically during study for pharmacokinetic and correlative studies. Tumor tissue samples from diagnosis and/or subsequent tumor resections or biopsies may also be collected for correlative studies.

After completion of study therapy, patients are followed up for 30 days.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
34
Inclusion Criteria

Not provided

Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
Treatmentimetelstat sodium-
Treatmentlaboratory biomarker analysis-
Treatmentpharmacological study-
Primary Outcome Measures
NameTimeMethod
Maximum-tolerated dose and/or recommended phase II dose of imetelstat sodium in children with refractory or recurrent solid tumors or lymphoma21 Days
Toxicities of imetelstat sodiumUp to 30 days post-treatment
Secondary Outcome Measures
NameTimeMethod

Trial Locations

Locations (23)

UAB Comprehensive Cancer Center

🇺🇸

Birmingham, Alabama, United States

Children's Hospital of Orange County

🇺🇸

Orange, California, United States

UCSF Helen Diller Family Comprehensive Cancer Center

🇺🇸

San Francisco, California, United States

Children's National Medical Center

🇺🇸

Washington, District of Columbia, United States

AFLAC Cancer Center and Blood Disorders Service of Children's Healthcare of Atlanta - Egleston Campus

🇺🇸

Atlanta, Georgia, United States

Children's Memorial Hospital - Chicago

🇺🇸

Chicago, Illinois, United States

Riley's Children Cancer Center at Riley Hospital for Children

🇺🇸

Indianapolis, Indiana, United States

Warren Grant Magnuson Clinical Center - NCI Clinical Trials Referral Office

🇺🇸

Bethesda, Maryland, United States

Dana-Farber/Harvard Cancer Center at Dana-Farber Cancer Institute

🇺🇸

Boston, Massachusetts, United States

C.S. Mott Children's Hospital at University of Michigan Medical Center

🇺🇸

Ann Arbor, Michigan, United States

Scroll for more (13 remaining)
UAB Comprehensive Cancer Center
🇺🇸Birmingham, Alabama, United States

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