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Penumbral Rescue by Normobaric O2 Administration in Patients With Ischemic Stroke and Target Mismatch ProFile

Phase 2
Terminated
Conditions
Acute Ischemic Stroke
Interventions
Other: Standard of care
Registration Number
NCT03500939
Lead Sponsor
University Hospital Tuebingen
Brief Summary

The main objective of the PROOF trial is to investigate efficacy and safety of normobaric hyperoxygenation (NBHO) as a neuroprotective treatment in patients with acute ischemic stroke due to large vessel occlusion likely to receive endovascular mechanical thrombectomy (TBY) in a randomized controlled clinical phase IIb trial.

Detailed Description

http://www.proof-trial.eu/

European Union's Horizon 2020 research and innovation programme grant 733379 (2016): Euro 5.8 Mio

Recruitment & Eligibility

Status
TERMINATED
Sex
All
Target Recruitment
223
Inclusion Criteria

Not provided

Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Normobaric hyperoxygenation + standard of careMedical oxygenNormobaric hyperoxygenation (NBHO), i.e. inhalation of 100% oxygen at high flow (≥ 40 L/min) via a sealed non-rebreather face-mask with reservoir, or in case of intubation/ventilation for (study-independent) TBY, ventilation with an inspiratory oxygen fraction (FiO2) of 1.0. NBHO is started within 3 hours of stroke symptom onset (witnessed or last seen well) and within 20 minutes after end of baseline brain imaging and applied until the end of TBY procedure (defined by removal of guide catheter from sheath) or, in case TBY is not attempted, 4 hours after start of study treatment.
Normobaric hyperoxygenation + standard of careStandard of careNormobaric hyperoxygenation (NBHO), i.e. inhalation of 100% oxygen at high flow (≥ 40 L/min) via a sealed non-rebreather face-mask with reservoir, or in case of intubation/ventilation for (study-independent) TBY, ventilation with an inspiratory oxygen fraction (FiO2) of 1.0. NBHO is started within 3 hours of stroke symptom onset (witnessed or last seen well) and within 20 minutes after end of baseline brain imaging and applied until the end of TBY procedure (defined by removal of guide catheter from sheath) or, in case TBY is not attempted, 4 hours after start of study treatment.
standard of care aloneStandard of carestandard of care alone; oxygen supplementation if SpO2 ≤ 94% at 2 to 4 L/min via nasal cannula according to guidelines of the European Stroke Organisation (ESO), or in case of TBY-related intubation/ventilation, ventilation with an initial FiO2 of 0.3 to be gradually increased if SpO2 ≤ 94%.
Primary Outcome Measures
NameTimeMethod
ischemic core growth from baseline to 24 hoursfrom baseline to 24 (22 to 36) hours

difference in ischemic core volume (in mL) from baseline to 24 hours; intention-to-treat (ITT) analysis

Secondary Outcome Measures
NameTimeMethod
all-cause death5 ± 2 days, 90 ± 10 days after randomization

clinical safety endpoint; to be assessed at visit 6 (V6, day 5), and V7 (day 90)

National Institutes of Health Stroke Scale score (NIHSS)20 ± 10 minutes, 4 hours ± 15 minutes, 24 ± 6 hours, 5 ± 2 days, 90 ± 10 days after randomization

secondary clinical efficacy endpoint; NIHSS to be assessed at visit 2 (V2, 20 minutes), V4 (end of study treatment), V5 (24 hours), V6 (day 5), and V7 (day 90); the NIHSS is a stroke severity score composed of 11 items (range from 0 to 41, higher values indicate more severe deficits)

Montgomery-Åsberg Depression Rating Scale (MADRS)90 ± 10 days after randomization

secondary clinical efficacy endpoint; MADRS to be assessed at visit 7 (day 90); the MADRS is a 10-item depression rating test that uses a 0 to 6 severity scale (higher scores indicate increasing depressive symptoms)

penumbral salvage from baseline to 24 hoursfrom baseline to 24 (22 to 36) hours

secondary imaging efficacy endpoint

modified Rankin Scale score (mRS)5 ± 2 days, 90 ± 10 days after randomization

secondary clinical efficacy endpoint; mRS to be assessed at visit 6 (V6, day 5), and V7 (day 90); the mRs is an ordinal disability score of 7 categories (0 = no symptoms to 5 = severe disability, and 6 = death)

symptomatic intracranial hemorrhage5 ± 2 days after randomization or discharge

clinical safety endpoint; per ECASS III definition and per Heidelberg bleeding classification

vital signs90 ± 10 days after randomization

clinical safety endpoint; systolic and diastolic blood pressure, heart and respiratory rate, peripheral capillary oxygen saturation (SpO2)

concomitant invasive procedures90 ± 10 days after randomization

clinical safety endpoint; e.g. intravenous/intra-arterial thrombolysis, thrombectomy, stenting, carotid surgery, decompressive hemicraniectomy, cardioversion, patent foramen ovale (PFO) closure

relative changes in ischemic core volume (in %) from baseline to 24 hoursfrom baseline to 24 (22 to 36) hours

secondary imaging efficacy endpoint

survival5 ± 2 days, 90 ± 10 days after randomization

secondary clinical efficacy endpoint; survival to be assessed at visit 6 (V6, day 5), and V7 (day 90)

Montreal Cognitive Assessment (MoCA)90 ± 10 days after randomization

secondary clinical efficacy endpoint; MoCA to be assessed at visit 7 (day 90)

length of ICU stay5 ± 2 days, 90 ± 10 days after randomization

secondary clinical efficacy endpoint; length of ICU stay to be assessed at visit 6 (V6, day 5), and V7 (day 90); ICU is defined as a ward with capacity for mechanical ventilation and/or continuous monitoring of vital parameters (including stroke units)

duration of ventilation5 ± 2 days, 90 ± 10 days after randomization

secondary clinical efficacy endpoint; duration of ventilation to be assessed at visit 6 (V6, day 5), and V7 (day 90)

change in National Institutes of Health Stroke Scale (NIHSS) score from baseline to 24 hoursfrom baseline to 24 ± 6 hours

key secondary endpoint; the NIHSS is a stroke severity score that is composed of 11 items; range from 0 to 41, higher values indicate more severe deficits

Barthel Index (BI)5 ± 2 days, 90 ± 10 days after randomization

secondary clinical efficacy endpoint; BI to be assessed at visit 6 (V6, day 5), and V7 (day 90)

Stroke Impact Scale 16 (SIS-16)90 ± 10 days after randomization

secondary clinical efficacy endpoint; SIS-16 to be assessed at visit 7 (day 90); the SIS-16 is a 16-item physical dimension instrument for measuring the physical aspects of stroke recovery (items are rated on a 1 to 5 scale; 5 = not difficult at all, 1 = could not do at all)

EuroQoL Questionnaire (EQ-5D-5L)90 ± 10 days after randomization

secondary clinical efficacy endpoint; EQ-5D-5L to be assessed at visit 7 (day 90)

partial pressure of oxygen in the arterial blood (PaO2)90 ± 30 minutes, 24 ± 6 hours after randomization

secondary clinical efficacy endpoint; PaO2 to be assessed at visit 3 (90 minutes after start of study treatment), and V5 (24 hours)

length of hospital stay5 ± 2 days, 90 ± 10 days after randomization

secondary clinical efficacy endpoint; length of hospital stay to be assessed at visit 6 (V6, day 5), and V7 (day 90)

TICI (Thrombolysis in Cerebral Infarction perfusion scale grade)4 hours ± 15 minutes

secondary imaging efficacy endpoint; in patients who underwent mechanical thrombectomy (TBY)

new microbleeds on 24-hour follow-up MRI (vs. baseline T2*weighted MRI)24 (22 to 36) hours

imaging safety endpoints; only possible in patients who had MRI at baseline as well as at 24 hours

peri-interventional occurrence of vasospasms4 hours ± 15 minutes

imaging safety endpoints; in patients who underwent mechanical thrombectomy (TBY)

ischemic lesions in new territories on 24-hour follow-up imaging24 (22 to 36) hours

imaging safety endpoints

stroke related death5 ± 2 days, 90 ± 10 days after randomization

clinical safety endpoint; to be assessed at visit 6 (V6, day 5), and V7 (day 90)

12-lead electrocardiogram (ECG)24 ± 6 hours after randomization

clinical safety endpoint

safety laboratory5 ± 2 days after randomization or discharge

clinical safety endpoint; blood count, clinical chemistry, coagulation

absolute and relative ischemic core change from baseline to 24 hours using cerebral blood flow (CBF) < 30% for ischemic core estimation at baseline in all patientsfrom baseline to 24 (22 to 36) hours

secondary imaging efficacy endpoint; independent of imaging modality

revascularization on 24-hour follow-up imaging24 (22 to 36) hours

secondary imaging efficacy endpoint

any intracranial hemorrhage on 24-hour follow-up imaging24 (22 to 36) hours

imaging safety endpoints

Trial Locations

Locations (22)

KU Leuven

🇧🇪

Leuven, Belgium

UZ Gent

🇧🇪

Gent, Belgium

CHU de Grenoble

🇫🇷

Grendelbruch, France

CHU de Nice

🇫🇷

Nice, France

Universitätsklinikum Gießen

🇩🇪

Gießen, Germany

CHU de Liège

🇧🇪

Liernu, Belgium

Helsinki University Hospital

🇫🇮

Helsinki, Finland

CHU de Nancy

🇫🇷

Nancy, France

Fondation Ophtalmologique Adolphe de Rothschild

🇫🇷

Paris, France

Universitätsklinikum Schleswig-Holstein

🇩🇪

Kiel, Germany

Universitätsklinikum Essen

🇩🇪

Essen, Germany

Ludwig-Maximilians-Universität München

🇩🇪

München, Germany

Centre Hospitalier Saint Anne de Paris

🇫🇷

Paris, France

Universitätsklinikum Eppendorf

🇩🇪

Hamburg, Germany

Universitätsklinikum Heidelberg

🇩🇪

Heidelberg, Germany

St. Lukas Klinik

🇩🇪

Solingen, Germany

Fundacio Hospital Universitari Vall D'Hebron

🇪🇸

Barcelona, Spain

Hospital Universitari de Bellvitge

🇪🇸

Barcelona, Spain

HCU Valladolid

🇪🇸

Valladolid, Spain

AZ Groeninge Kortrijk

🇧🇪

Kortrijk, Belgium

Universitätsklinikum Ulm

🇩🇪

Ulm, Germany

University Hospital Tuebingen

🇩🇪

Tuebingen, Germany

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